检索结果 - Pierre Martinucci
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Adenine base editor–mediated correction of the common and severe IVS1-110 (G>A) β-thalassemia mutation 由 Giulia Hardouin, Panagiotis Antoniou, Pierre Martinucci, Tristan Félix, Sandra Manceau, Laure Joseph, Cécile Masson, Samantha Scaramuzza, Giuliana Ferrari, Marina Cavazzana, Annarita Miccio
出版 2022Artigo -
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Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expression 由 Panagiotis Antoniou, Giulia Hardouin, Pierre Martinucci, Giacomo Frati, Tristan Félix, Anne Chalumeau, Letizia Fontana, Jeanne Martin, Cécile Masson, Mégane Brusson, Giulia Maule, Marion Rosello, Carine Giovannangeli, Vincent Abramowski, Jean‐Pierre de Villartay, Jean‐Paul Concordet, Filippo Del Bene, Wassim El Nemer, Mario Amendola, Marina Cavazzana, Anna Cereseto, Oriana Romano, Annarita Miccio
出版 2022Artigo