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Achromatopsia 由 Meredith H. Remmer, Neelesh Rastogi, Milan P. Ranka, Emily Ceisler

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Production of lentiviral vectors 由 Otto-Wilhelm Merten, Matthias Hebben, Chiara Bovolenta

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Adenovirus Strategies for Tissue-Specific Targeting 由 Matthew S. Beatty, David T. Curiel

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Development of Patient-specific AAV Vectors After Neutralizing Antibody Selection for Enhanced Muscle Gene Transfer 由 Chengwen Li, Shuqing Wu, Blake H. Albright, Matthew Hirsch, Wuping Li, Yu-Shan Tseng, Mavis Agbandje‐McKenna, Scott McPhee, Aravind Asokan, R. Jude Samulski

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Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1 由 Fabien Touzot, Despina Moshous, Rita Creidy, Bénédicte Neven, Pierre Frange, Guilhem Cros, Laure Caccavelli, Johanna Blondeau, Alessandra Magnani, Jean-Marc Luby, Brigitte Ternaux, Capucine Pïcard, Stéphane Blanche, Alain Fischer, Salima Hacein‐Bey‐Abina, Marina Cavazzana

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Fusions of Elastin-Like Polypeptides to Pharmaceutical Proteins 由 Wafa Hassouneh, Sarah R. MacEwan, Ashutosh Chilkoti

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PEO–PPO–PEO micelles as effective rAAV-mediated gene delivery systems to target human mesenchymal stem cells without altering their differentiation potency 由 Ana Rey‐Rico, Jagadeesh K. Venkatesan, Janina Frisch, M. Isabel Rial-Hermida, Gertrud Schmitt, Ángel Concheiro, Henning Madry, Carmen Alvarez‐Lorenzo, Magali Cucchiarini

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Gene Therapy Restores Hair Cell Stereocilia Morphology in Inner Ears of Deaf Whirler Mice 由 Wade W. Chien, Kevin Isgrig, Soumen Roy, Inna A. Belyantseva, Meghan C. Drummond, Lindsey May, Tracy S. Fitzgerald, Thomas B. Friedman, Lisa L. Cunningham

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Optogenetic Control of Cardiomyocytes via Viral Delivery 由 Christina M. Ambrosi, Emilia Entcheva

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Lentiviral-mediated gene transfer into human lymphocytes: role of HIV-1 accessory proteins 由 Dhanalakshmi Chinnasamy, Nachimuthu Chinnasamy, Melissa J. Enriquez, Makoto Otsu, Richard A. Morgan, Fabio Candotti

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A Coagulation Factor IX-Deficient Mouse Model for Human Hemophilia B 由 Hui-Feng Lin, Nobuyo Maeda, Oliver Smithies, David L. Straight, Darrel W. Stafford

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mRNA: Fulfilling the Promise of Gene Therapy 由 Drew Weissman, Katalin Karikó

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Fibronectin improves transduction of reconstituting hematopoietic stem cells by retroviral vectors: evidence of direct viral binding to chymotryptic carboxy-terminal fragments 由 Tassilo Moritz, Parmesh Dutt, Xiang Xiao, Dirk Carstanjen, Terry A. Vik, Helmut Hanenberg, DA Williams

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Modeling human lymphoid precursor cell gene therapy in the SCID-hu mouse 由 RK Akkina, Joseph D. Rosenblatt, Andrew G. Campbell, IS Chen, JA Zack

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Skipping the co-expression problem: the new 2A "CHYSEL" technology. 由 Pablo de Felipe

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The Challenge for Gene Therapy: Innate Immune Response to Adenoviruses 由 Bart Thaçi, Ilya V. Ulasov, Derek A. Wainwright, Maciej S. Lesniak

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Post-transcriptional restriction of human adenovirus expression in monkey cells 由 L J Eron

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In vivo genome editing of the albumin locus as a platform for protein replacement therapy 由 Rajiv P. Sharma, Xavier M. Anguela, Yannick Doyon, Thomas Wechsler, Russell C. DeKelver, Scott Sproul, David E. Paschon, Jeffrey C. Miller, Robert J. Davidson, David A. Shivak, Shangzhen Zhou, Julianne Rieders, Philip D. Gregory, Michael C. Holmes, Edward J. Rebar, Katherine A. High

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Inhibition of Human Immunodeficiency Virus-1 (HIV-1) Replication After Transduction of Granulocyte Colony-Stimulating Factor–Mobilized CD34+ Cells From HIV-1–Infected Donors Using... 由 Gerhard Bauer, Penelope Valdez, Karen Kearns, Ingrid Bahner, Sui Fang Wen, John A. Zaia, Donald B. Kohn

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A preliminary <i>in vitro</i> study into the use of IL‐1Ra gene therapy for the inhibition of intervertebral disc degeneration 由 Christine L. Le Maitre, Anthony J. Freemont, Judith A. Hoyland

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