Søgeresultater - Dwight D. Koeberl

Refine Results
  1. 1
    Gene therapy for glycogen storage diseases

    Gene therapy for glycogen storage diseases af Priya S. Kishnani, Baodong Sun, Dwight D. Koeberl

    Udgivet 2019
    Få fuldtekst Få fuldtekst
    Revisão
    Føj til favoritter
    Saved in:
  2. 2
    Glycogen storage disease types I and II: Treatment updates

    Glycogen storage disease types I and II: Treatment updates af Dwight D. Koeberl, Priya S. Kishnani, Yan‐Chu Chen

    Udgivet 2007
    Få fuldtekst
    Revisão
    Føj til favoritter
    Saved in:
  3. 3
    The Role of Hepatocyte Hemojuvelin in the Regulation of Bone Morphogenic Protein-6 and Hepcidin Expression in Vivo

    The Role of Hepatocyte Hemojuvelin in the Regulation of Bone Morphogenic Protein-6 and Hepcidin Expression in Vivo af An‐Sheng Zhang, Junwei Gao, Dwight D. Koeberl, Caroline Enns

    Udgivet 2010
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  4. 4
    Fasting alleviates metabolic alterations in mice with propionyl-CoA carboxylase deficiency due to Pcca mutation

    Fasting alleviates metabolic alterations in mice with propionyl-CoA carboxylase deficiency due to Pcca mutation af Wentao He, Hannah Marchuk, Dwight D. Koeberl, Takhar Kasumov, Xiaoxin Chen, Guofang Zhang

    Udgivet 2024
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  5. 5
    Enhanced Response to Enzyme Replacement Therapy in Pompe Disease after the Induction of Immune Tolerance

    Enhanced Response to Enzyme Replacement Therapy in Pompe Disease after the Induction of Immune Tolerance af Baodong Sun, Andrew Bird, Sarah P. Young, Priya S. Kishnani, Yuqi Chen, Dwight D. Koeberl

    Udgivet 2007
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  6. 6
    Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoter

    Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoter af Baodong Sun, Haoyue Zhang, Luis M. Franco, T. T. Brown, Andrew Bird, Ayn Schneider, Dwight D. Koeberl

    Udgivet 2005
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  7. 7
    Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors

    Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors af Dwight D. Koeberl, Ian E. Alexander, Christine L. Halbert, David W. Russell, A. Dusty Miller

    Udgivet 1997
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  8. 8
    Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction

    Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction af Sang-oh Han, Giuseppe Ronzitti, Benjamin Arnson, Christian Leborgne, Songtao Li, Federico Mingozzi, Dwight D. Koeberl

    Udgivet 2017
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  9. 9
    Efficacy of an Adeno-associated Virus 8-Pseudotyped Vector in Glycogen Storage Disease Type II

    Efficacy of an Adeno-associated Virus 8-Pseudotyped Vector in Glycogen Storage Disease Type II af Baodong Sun, Haoyue Zhang, Luis M. Franco, Sarah P. Young, Ayn Schneider, Andrew Bird, Andrea Amalfitano, Y.-T. Chen, Dwight D. Koeberl

    Udgivet 2004
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  10. 10
    Hepatocyte-targeted HFE and TFR2 control hepcidin expression in mice

    Hepatocyte-targeted HFE and TFR2 control hepcidin expression in mice af Junwei Gao, Juxing Chen, Ivana De Domenico, David M. Koeller, Cary O. Harding, Robert E. Fleming, Dwight D. Koeberl, Caroline Enns

    Udgivet 2010
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  11. 11
    Enhanced efficacy of enzyme replacement therapy in Pompe disease through mannose-6-phosphate receptor expression in skeletal muscle

    Enhanced efficacy of enzyme replacement therapy in Pompe disease through mannose-6-phosphate receptor expression in skeletal muscle af Dwight D. Koeberl, Xiaoyan Luo, Baodong Sun, Alison McVie‐Wylie, Jian Dai, Songtao Li, Suhrad G. Banugaria, Y.-T. Chen, Deeksha Bali

    Udgivet 2011
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  12. 12
    Immunodominant Liver-Specific Expression Suppresses Transgene-Directed Immune Responses in Murine Pompe Disease

    Immunodominant Liver-Specific Expression Suppresses Transgene-Directed Immune Responses in Murine Pompe Disease af Ping Zhang, Baodong Sun, Takuya Osada, Ramona M. Rodriguiz, Xiao Yang, Xiaoyan Luo, Alex R. Kemper, Timothy M. Clay, Dwight D. Koeberl

    Udgivet 2012
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  13. 13
    A Liver-Specific Thyromimetic, VK2809, Decreases Hepatosteatosis in Glycogen Storage Disease Type Ia

    A Liver-Specific Thyromimetic, VK2809, Decreases Hepatosteatosis in Glycogen Storage Disease Type Ia af Jin Zhou, Lauren R. Waskowicz, Andrea Lim, Xiao-Hui Liao, Brian Lian, Hiroko Masamune, Samuel Refetoff, Brian Tran, Dwight D. Koeberl, Paul M. Yen

    Udgivet 2019
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  14. 14
    Evasion of Immune Responses to Introduced Human Acid α-Glucosidase by Liver-Restricted Expression in Glycogen Storage Disease Type II

    Evasion of Immune Responses to Introduced Human Acid α-Glucosidase by Liver-Restricted Expression in Glycogen Storage Disease Type II af Luis M. Franco, Baodong Sun, Xiaoyi Yang, Andrew Bird, Haoyue Zhang, Ayn Schneider, T. T. Brown, Sarah P. Young, Timothy M. Clay, Andrea Amalfitano, Y.T. Chen, Dwight D. Koeberl

    Udgivet 2005
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  15. 15
    Hepatic mitochondrial dysfunction is a feature of Glycogen Storage Disease Type Ia (GSDIa)

    Hepatic mitochondrial dysfunction is a feature of Glycogen Storage Disease Type Ia (GSDIa) af Benjamin L. Farah, Rohit A. Sinha, Yajun Wu, Brijesh Kumar Singh, Andrea Lim, Masahiro Hirayama, Dustin J. Landau, Boon‐Huat Bay, Dwight D. Koeberl, Paul M. Yen

    Udgivet 2017
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  16. 16
    Interim analyses of a first-in-human phase 1/2 mRNA trial for propionic acidaemia

    Interim analyses of a first-in-human phase 1/2 mRNA trial for propionic acidaemia af Dwight D. Koeberl, Andreas Schulze, Neal Sondheimer, Gerald S. Lipshutz, Tarekegn Geberhiwot, Lerong Li, Rajnish Saini, Junxiang Luo, Vanja Sikirica, Ling Jin, M. Liang, Mary Leuchars, Stephanie Grünewald

    Udgivet 2024
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  17. 17
    Immunomodulatory Gene Therapy Prevents Antibody Formation and Lethal Hypersensitivity Reactions in Murine Pompe Disease

    Immunomodulatory Gene Therapy Prevents Antibody Formation and Lethal Hypersensitivity Reactions in Murine Pompe Disease af Baodong Sun, Michael D. Kulis, Sarah P. Young, Amy Hobeika, Songtao Li, Andrew Bird, Haoyue Zhang, Y Li, Timothy M. Clay, Wesley Burks, Priya S. Kishnani, Dwight D. Koeberl

    Udgivet 2009
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  18. 18
    Correction of Multiple Striated Muscles in Murine Pompe Disease Through Adeno-associated Virus–mediated Gene Therapy

    Correction of Multiple Striated Muscles in Murine Pompe Disease Through Adeno-associated Virus–mediated Gene Therapy af Baodong Sun, Sarah P. Young, Ping Li, Chunhui Di, T. T. Brown, Maja Z. Salva, Songtao Li, Andrew Bird, Zhen Yan, Richard L. Auten, Stephen D. Hauschka, Dwight D. Koeberl

    Udgivet 2008
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  19. 19
    Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants

    Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants af Priya S. Kishnani, Paula Goldenberg, Stephanie DeArmey, James H. Heller, Danny Benjamin, Sarah P. Young, Deeksha Bali, Sue Ann Smith, Jennifer S. Li, Hanna Mandel, Dwight D. Koeberl, Amy S. Rosenberg, Y-T Chen

    Udgivet 2009
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  20. 20
    Chromosomal and genetic alterations in human hepatocellular adenomas associated with type Ia glycogen storage disease

    Chromosomal and genetic alterations in human hepatocellular adenomas associated with type Ia glycogen storage disease af Priya S. Kishnani, Tzu‐Po Chuang, Deeksha Bali, Dwight D. Koeberl, Stephanie Austin, David A. Weinstein, Elaine Murphy, Ying‐Ting Chen, Keri Boyette, Chu‐Hao Liu, Yuan-Tsong Chen, Ling‐Hui Li

    Udgivet 2009
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:

Søgeredskaber: