Search Results - Colleen Dansereau
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Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy by Florian Eichler, Christine Duncan, Patricia L. Musolino, Paul J. Orchard, Satiro De Oliveira, Adrian J. Thrasher, Myriam Armant, Colleen Dansereau, Troy C. Lund, Weston P. Miller, Gerald V. Raymond, Raman Sankar, Ami J. Shah, Caroline Sevin, H. Bobby Gaspar, Paul Gissen, Hernán Amartino, Drago Bratkovic, Nicholas Smith, Asif Paker, Esther Shamir, Tara O’Meara, David Davidson, Patrick Aubourg, David A. Williams
Published 2017Artigo -
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Post-Transcriptional Genetic Silencing of<i>BCL11A</i>to Treat Sickle Cell Disease by Erica B. Esrick, Leslie E. Lehmann, Alessandra Biffi, Maureen Achebe, Christian Brendel, Marioara F. Ciuculescu, Heather Daley, Brenda L. MacKinnon, Emily A. Morris, Amy Federico, Daniela Abriss, Kari Boardman, Radia Khelladi, Kit L. Shaw, Hélène Negre, Olivier Nègre, Sarah Nikiforow, Jerome Ritz, Sung‐Yun Pai, Wendy B. London, Colleen Dansereau, Matthew M. Heeney, Myriam Armant, John P. Manis, David A. Williams
Published 2020Artigo