Targeted Correction and Restored Function of the CFTR Gene in Cystic Fibrosis Induced Pluripotent Stem Cells

Targeted Correction and Restored Function of the CFTR Gene in Cystic Fibrosis Induced Pluripotent Stem Cells

Recently developed reprogramming and genome editing technologies make possible the derivation of corrected patient-specific pluripotent stem cell sources—potentially useful for the development of new therapeutic approaches. Starting with skin fibroblasts from patients diagnosed with cystic fibrosis,...

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Main Authors: Crane, Ana M., Kramer, Philipp, Bui, Jacquelin H., Chung, Wook Joon, Li, Xuan Shirley, Gonzalez-Garay, Manuel L., Hawkins, Finn, Liao, Wei, Mora, Daniela, Choi, Sangbum, Wang, Jianbin, Sun, Helena C., Paschon, David E., Guschin, Dmitry Y., Gregory, Philip D., Kotton, Darrell N., Holmes, Michael C., Sorscher, Eric J., Davis, Brian R.
Format: Text
Language:English
Published: Elsevier 2015
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Online Access:https://pmc.ncbi.nlm.nih.gov/articles/PMC4400651/
https://pubmed.ncbi.nlm.nih.gov/25772471
http://dx.doi.org/10.1016/j.stemcr.2015.02.005
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https://pmc.ncbi.nlm.nih.gov/articles/PMC4400651/
https://pubmed.ncbi.nlm.nih.gov/25772471
http://dx.doi.org/10.1016/j.stemcr.2015.02.005

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