Torthaí cuardaigh - Xiupeng Chen

Improved gene therapy for spinal muscular atrophy in mice using codon-optimized hSMN1 transgene and hSMN1 gene-derived promotor de réir Qing Xie, Xiupeng Chen, Hong Ma, Yunxiang Zhu, Yijie Ma, Leila Jalinous, Gerald F. Cox, F. Lloyd Weaver, Jun Yang, Zachary Kennedy, Alisha M. Gruntman, Ailing Du, Qin Su, Ran He, Phillip W.L. Tai, Guangping Gao, Jun Xie