檢索結果 - Winston X. Yan
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Consensus Guidelines for the Design and <i>In Vitro</i> Preclinical Efficacy Testing N-of-1 Exon Skipping Antisense Oligonucleotides 由 Annemieke Aartsma‐Rus, Alejandro Garanto, Willeke M. C. van Roon‐Mom, Erin M. McConnell, Victoria Suslovitch, Winston X. Yan, Jonathan K. Watts, Timothy W. Yu
出版 2022Artigo -
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BLISS is a versatile and quantitative method for genome-wide profiling of DNA double-strand breaks 由 Winston X. Yan, Reza Mirzazadeh, Silvano Garnerone, David Scott, Martin Schneider, Tomasz Kallas, Joaquín Custodio, Erik Wernersson, Yinqing Li, Linyi Gao, Yana Federova, Bernd Zetsche, Feng Zhang, Magda Bienko, Nicola Crosetto
出版 2017Artigo -
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In vivo gene editing in dystrophic mouse muscle and muscle stem cells 由 Mohammadsharif Tabebordbar, Kexian Zhu, Jason Cheng, Wei Leong Chew, Jeffrey J. Widrick, Winston X. Yan, Claire Maesner, Elizabeth Y. Wu, Ru Xiao, F. Ann Ran, Le Cong, Feng Zhang, Luk H. Vandenberghe, George M. Church, Amy J. Wagers
出版 2016Artigo -
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In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy 由 Christopher E. Nelson, Chady H. Hakim, David G. Ousterout, Pratiksha I. Thakore, Eirik A. Moreb, Ruth M. Castellanos Rivera, Sarina Madhavan, Xiufang Pan, F. Ann Ran, Winston X. Yan, Aravind Asokan, Feng Zhang, Dongsheng Duan, Charles A. Gersbach
出版 2016Artigo -
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The miniature CRISPR-Cas12m effector binds DNA to block transcription 由 Wen Y. Wu, Prarthana Mohanraju, Chunyu Liao, Belén Adiego-Pérez, Sjoerd C.A. Creutzburg, Kira S. Makarova, Karlijn Keessen, Timon A. Lindeboom, Tahseen S. Khan, Stijn H. P. Prinsen, Rob Joosten, Winston X. Yan, Anzhela Migur, Charlie Laffeber, David Scott, Joyce H.G. Lebbink, Eugene V. Koonin, Chase L. Beisel, John van der Oost
出版 2022Artigo -
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Engineered Cas12i2 is a versatile high-efficiency platform for therapeutic genome editing 由 Colin McGaw, Anthony J. Garrity, Gabrielle Munoz, Jeffrey R. Haswell, Sejuti Sengupta, Elise Keston-Smith, Pratyusha Hunnewell, Alexa Ornstein, Mishti Bose, Quinton N. Wessells, Noah Jakimo, Paul Yan, Huaibin Zhang, Lauren E. Alfonse, Roy Ziblat, Jason Carte, Weicheng Lu, Derek Cerchione, Brendan J. Hilbert, Shanmugapriya Sothiselvam, Winston X. Yan, David R. Cheng, David Scott, Tia DiTommaso, Shaorong Chong
出版 2022Artigo -
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Evolutionary classification of CRISPR–Cas systems: a burst of class 2 and derived variants 由 Kira S. Makarova, Yuri I. Wolf, Jaime Iranzo, Sergey Shmakov, Omer S. Alkhnbashi, Stan J. J. Brouns, Emmanuelle Charpentier, David R. Cheng, Daniel H. Haft, Philippe Horvath, Sylvain Moineau, Francisco J. M. Mojica, David Scott, Shiraz A. Shah, Virginijus Šikšnys, Michael P. Terns, Česlovas Venclovas, Malcolm F. White, Alexander F. Yakunin, Winston X. Yan, Feng Zhang, Roger A. Garrett, Rolf Backofen, John van der Oost, Rodolphe Barrangou, Eugene V. Koonin
出版 2019Revisão
相關主題
Biology
Gene
Genetics
CRISPR
Computational biology
Genome editing
Cas9
Computer science
Genome
Cell biology
DNA
Guide RNA
Artificial intelligence
Effector
RNA
Nuclease
Neuroscience
Acoustics
Bacteria
Class (philosophy)
Duchenne muscular dystrophy
EEG-fMRI
Electroencephalography
Evolutionary biology
Exon
Genome engineering
Medicine
Molecular biology
Muscular dystrophy
Physics