Výsledky vyhledávání - Vanessa R. Strings
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PABPN1 gene therapy for oculopharyngeal muscular dystrophy Autor Alberto Malerba, Pierre Klein, Houria Bachtarzi, Susan Jarmin, Gonzalo Córdova, Arnaud Ferry, Vanessa R. Strings, Micaela Polay Espinoza, Kamel Mamchaoui, Sergiu C. Blumen, Jean Lacau St Guily, Vincent Mouly, Michael W. Graham, Gillian Butler‐Browne, David Suhy, Capucine Trollet, George Dickson
Vydáno 2017Artigo
Vyhledávací nástroje:
Související témata
Biology
Gene
Genetics
Allele
Bioinformatics
Cancer research
Computational biology
Gene expression
Gene knockdown
Genetic enhancement
Internal medicine
Medicine
Muscle weakness
Muscular dystrophy
Non-coding RNA
Nucleic acid structure
Oculopharyngeal muscular dystrophy
Open reading frame
Peptide sequence
Picornavirus
Poliovirus
RNA
RNA editing
RNA interference
RNA silencing
RNA-dependent RNA polymerase
RNA-induced transcriptional silencing
Small nuclear RNA
Transcriptome
Trinucleotide repeat expansion