Výsledky vyhledávání - Valentina Vavassori
- Zobrazuji výsledky 1 - 7 z 7
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Lipid nanoparticles allow efficient and harmless ex vivo gene editing of human hematopoietic cells Autor Valentina Vavassori, Samuele Ferrari, Stefano Beretta, Claudia Asperti, Luisa Albano, Andrea Annoni, Chiara Gaddoni, Angelica Varesi, Monica Soldi, Alessandro Cuomo, Tiziana Bonaldi, Marina Radrizzani, Ivan Merelli, Luigi Naldini
Vydáno 2023Artigo -
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Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking Autor Samuele Ferrari, Aurélien Jacob, Stefano Beretta, Giulia Unali, Luisa Albano, Valentina Vavassori, Davide Cittaro, Dejan Lazarević, Chiara Brombin, Federica Cugnata, Anna Kajaste‐Rudnitski, Ivan Merelli, Pietro Genovese, Luigi Naldini
Vydáno 2020Artigo -
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Precise Gene Editing Preserves Hematopoietic Stem Cell Function following Transient p53-Mediated DNA Damage Response Autor Giulia Schiroli, Anastasia Conti, Samuele Ferrari, Lucrezia della Volpe, Aurélien Jacob, Luisa Albano, Stefano Beretta, Andrea Calabria, Valentina Vavassori, Patrizia Gasparini, Eralda Salataj, Delphine Ndiaye‐Lobry, Chiara Brombin, Julie Chaumeil, Eugenio Montini, Ivan Merelli, Pietro Genovese, Luigi Naldini, Raffaella Di Micco
Vydáno 2019Artigo -
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Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome Autor Valentina Vavassori, E. Mercuri, Genni Enza Marcovecchio, Maria Carmina Castiello, Giulia Schiroli, Luisa Albano, Carrie M. Margulies, Frank A. Buquicchio, Elena Fontana, Stefano Beretta, Ivan Merelli, Andrea Cappelleri, Paola M. V. Rancoita, Vassilios Lougaris, Alessandro Plebani, Maria Kanariou, Arjan C. Lankester, Francesca Ferrua, Eugenio Scanziani, Cecilia Cotta‐Ramusino, Anna Villa, Luigi Naldini, Pietro Genovese
Vydáno 2021Artigo -
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Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells Autor Samuele Ferrari, Aurélien Jacob, Daniela Cesana, Marianne Laugel, Stefano Beretta, Angelica Varesi, Giulia Unali, Anastasia Conti, Daniele Canarutto, Luisa Albano, Andrea Calabria, Valentina Vavassori, Carlo Cipriani, Maria Carmina Castiello, Simona Esposito, Chiara Brombin, Federica Cugnata, Oumeya Adjali, Eduard Ayuso, Ivan Merelli, Anna Villa, Raffaella Di Micco, Anna Kajaste‐Rudnitski, Eugenio Montini, Magalie Penaud‐Budloo, Luigi Naldini
Vydáno 2022Artigo -
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Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency Autor Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso‐Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M. Holland, Jenna Bergerson, Suk See De Ravin, Harry L. Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M. Crooks, Luigi D. Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Vydáno 2024Artigo
Vyhledávací nástroje:
Související témata
Biology
Gene
Genetics
Genome editing
Haematopoiesis
Stem cell
CRISPR
Cell biology
Genetic enhancement
Progenitor cell
Cancer research
Computational biology
Gene delivery
Cas9
DNA
DNA damage
Hematopoietic stem cell
Biochemistry
Cell cycle
Electroporation
Ex vivo
Exon
Gene knockin
Genome
Hematopoietic stem cell transplantation
Homology directed repair
Immunology
In vivo
Medicine
Messenger RNA