检索结果 - Shestruma Parajuli
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Unexpected Death of a Duchenne Muscular Dystrophy Patient in an N-of-1 Trial of rAAV9-delivered CRISPR-transactivator 由 Angela Lek, Brenda Wong, Allison M. Keeler, Meghan Blackwood, Kaiyue Ma, Shushu Huang, Katelyn Sylvia, Ana Rita Batista, Rebecca Artinian, Danielle Kokoski, Shestruma Parajuli, Juan Putra, Chrystalle Katte Carreon, Hart G.W. Lidov, Keryn G. Woodman, Sander Pajusalu, Janelle M. Spinazzola, T. F. Gallagher, Joan M. LaRovere, Diane Baulderson, Lauren Page Black, Keith A. Sutton, Richard Horgan, Monkol Lek, Terence R. Flotte
出版 2023Pré-impressão -
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Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne’s Muscular Dystrophy 由 Angela Lek, Brenda Wong, Allison M. Keeler, Meghan Blackwood, Kaiyue Ma, Shushu Huang, Katelyn Sylvia, Ana Rita Batista, Rebecca Artinian, Danielle Kokoski, Shestruma Parajuli, Juan Putra, Chrystalle Katte Carreon, Hart G.W. Lidov, Keryn G. Woodman, Sander Pajusalu, Janelle M. Spinazzola, T. F. Gallagher, Joan M. LaRovere, Diane Balderson, Lauren Page Black, Keith A. Sutton, Richard Horgan, Monkol Lek, Terence R. Flotte
出版 2023Artigo