Search Results - Samuele Ferrari
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Genetic engineering meets hematopoietic stem cell biology for next-generation gene therapy by Samuele Ferrari, Erika Valeri, Anastasia Conti, Serena Scala, Annamaria Aprile, Raffaella Di Micco, Anna Kajaste‐Rudnitski, Eugenio Montini, Giuliana Ferrari, Alessandro Aiuti, Luigi Naldini
Published 2023Revisão -
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Lipid nanoparticles allow efficient and harmless ex vivo gene editing of human hematopoietic cells by Valentina Vavassori, Samuele Ferrari, Stefano Beretta, Claudia Asperti, Luisa Albano, Andrea Annoni, Chiara Gaddoni, Angelica Varesi, Monica Soldi, Alessandro Cuomo, Tiziana Bonaldi, Marina Radrizzani, Ivan Merelli, Luigi Naldini
Published 2023Artigo -
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Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking by Samuele Ferrari, Aurélien Jacob, Stefano Beretta, Giulia Unali, Luisa Albano, Valentina Vavassori, Davide Cittaro, Dejan Lazarević, Chiara Brombin, Federica Cugnata, Anna Kajaste‐Rudnitski, Ivan Merelli, Pietro Genovese, Luigi Naldini
Published 2020Artigo -
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Genotoxic effects of base and prime editing in human hematopoietic stem cells by Martina Fiumara, Samuele Ferrari, Attya Omer, Stefano Beretta, Luisa Albano, Daniele Canarutto, Angelica Varesi, Chiara Gaddoni, Chiara Brombin, Federica Cugnata, Erika Zonari, Matteo Maria Naldini, Matteo Barcella, Bernhard Gentner, Ivan Merelli, Luigi Naldini
Published 2023Artigo -
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Precise Gene Editing Preserves Hematopoietic Stem Cell Function following Transient p53-Mediated DNA Damage Response by Giulia Schiroli, Anastasia Conti, Samuele Ferrari, Lucrezia della Volpe, Aurélien Jacob, Luisa Albano, Stefano Beretta, Andrea Calabria, Valentina Vavassori, Patrizia Gasparini, Eralda Salataj, Delphine Ndiaye‐Lobry, Chiara Brombin, Julie Chaumeil, Eugenio Montini, Ivan Merelli, Pietro Genovese, Luigi Naldini, Raffaella Di Micco
Published 2019Artigo -
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Diaphragm ultrasound evaluation during weaning from mechanical ventilation in COVID-19 patients: a pragmatic, cross-section, multicenter study by Luigi Vetrugno, Daniele Orso, Francesco Corradi, Gianluca Zani, Savino Spadaro, Francesco Meroi, Natascia D’Andrea, Tiziana Bove, Gianmaria Cammarota, Edoardo De Robertis, Samuele Ferrari, Marcello Guarnieri, Margherita Ajuti, Maurizio Fusari, Domenico Luca Grieco, Cristian Deana, Enrico Boero, Federico Franchi, Sabino Scolletta, Salvatore Maurizio Maggiore, Francesco Forfori
Published 2022Artigo -
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A p38 MAPK-ROS axis fuels proliferation stress and DNA damage during CRISPR-Cas9 gene editing in hematopoietic stem and progenitor cells by Lucrezia della Volpe, Federico Midena, Roberta Vacca, Teresa Tavella, Laura Alessandrini, Giacomo Farina, Chiara Brandas, Elena Lo Furno, Kety Giannetti, Edoardo Carsana, Matteo Maria Naldini, Matteo Barcella, Samuele Ferrari, Stefano Beretta, Antonella Santoro, Simona Porcellini, Angelica Varesi, Diego Gilioli, Anastasia Conti, Ivan Merelli, Bernhard Gentner, Anna Villa, Luigi Naldini, Raffaella Di Micco
Published 2024Artigo -
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Choice of template delivery mitigates the genotoxic risk and adverse impact of editing in human hematopoietic stem cells by Samuele Ferrari, Aurélien Jacob, Daniela Cesana, Marianne Laugel, Stefano Beretta, Angelica Varesi, Giulia Unali, Anastasia Conti, Daniele Canarutto, Luisa Albano, Andrea Calabria, Valentina Vavassori, Carlo Cipriani, Maria Carmina Castiello, Simona Esposito, Chiara Brombin, Federica Cugnata, Oumeya Adjali, Eduard Ayuso, Ivan Merelli, Anna Villa, Raffaella Di Micco, Anna Kajaste‐Rudnitski, Eugenio Montini, Magalie Penaud‐Budloo, Luigi Naldini
Published 2022Artigo -
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Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency by Maria Carmina Castiello, Chiara Brandas, Samuele Ferrari, Simona Porcellini, Nicolò Sacchetti, Daniele Canarutto, Elena Draghici, Ivan Merelli, Matteo Barcella, Gabriele Pelosi, Valentina Vavassori, Angelica Varesi, Aurélien Jacob, Serena Scala, Luca Basso‐Ricci, Marianna Paulis, Dario Strina, Martina Di Verniere, Lucia Sergi Sergi, Marta Serafini, Steven M. Holland, Jenna Bergerson, Suk See De Ravin, Harry L. Malech, Francesca Pala, Marita Bosticardo, Chiara Brombin, Federica Cugnata, Enrica Calzoni, Gay M. Crooks, Luigi D. Notarangelo, Pietro Genovese, Luigi Naldini, Anna Villa
Published 2024Artigo -
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Mechanisms of hematopoietic clonal dominance in VEXAS syndrome by Raffaella Molteni, Martina Fiumara, Corrado Campochiaro, Roberta Alfieri, Guido Pacini, Elisa Licari, Alessandro Tomelleri, Elisa Diral, Angelica Varesi, Alessandra Weber, Pamela Quaranta, Luisa Albano, Chiara Gaddoni, Luca Basso‐Ricci, Davide Stefanoni, Laura Alessandrini, S. Degl’Innocenti, Francesca Sanvito, Gregorio Maria Bergonzi, Andrea Annoni, Maddalena Panigada, Eleonora Cantoni, Daniele Canarutto, Stephanie Z. Xie, Angelo D’Alessandro, Raffaella Di Micco, Alessandro Aiuti, Fabio Ciceri, Giacomo De Luca, Lorenzo Dagna, Marco Matucci‐Cerinic, Ivan Merelli, Simone Cenci, Serena Scala, Giulio Cavalli, Luigi Naldini, Samuele Ferrari
Published 2025Artigo
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Biology
Genetics
Haematopoiesis
Stem cell
Gene
Genome editing
CRISPR
Cell biology
Progenitor cell
Genetic enhancement
Computational biology
Cancer research
DNA
DNA damage
Gene delivery
Cas9
Hematopoietic stem cell
Medicine
2019-20 coronavirus outbreak
Acoustics
Base (topology)
Biochemistry
Bioinformatics
Cell cycle
Combinatorics
Computer science
Coronavirus disease 2019 (COVID-19)
Diaphragm (acoustics)
Disease
Dominance (genetics)