Canlyniadau Chwilio - Ronald K. Scheule
- Dangos 1 - 16 canlyniadau o 16
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Role of viral hemagglutinin glycosylation in anti-influenza activities of recombinant surfactant protein D gan Kevan L. Hartshorn, Richard J. Webby, Mitchell R. White, Tesfaldet Tecle, Clark Q. Pan, Susan Boucher, Rodney J. Moreland, Erika C. Crouch, Ronald K. Scheule
Cyhoeddwyd 2008Artigo -
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Stoichiometry of recombinant cystic fibrosis transmembrane conductance regulator in epithelial cells and its functional reconstitution into cells in vitro. gan John Marshall, Shaona L. Fang, Lynda S. Ostedgaard, Catherine R. O’Riordan, Dawn T. Ferrara, Jane F. Amara, H. Hoppe, Ronald K. Scheule, Michael J. Welsh, Alan E. Smith
Cyhoeddwyd 1994Artigo -
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Antisense Oligonucleotide-mediated Suppression of Muscle Glycogen Synthase 1 Synthesis as an Approach for Substrate Reduction Therapy of Pompe Disease gan Nicholas P. Clayton, Carol A. Nelson, Timothy Weeden, Kristin M. Taylor, Rodney J. Moreland, Ronald K. Scheule, Lucy Phillips, Andrew J. Leger, Seng H. Cheng, Bruce M. Wentworth
Cyhoeddwyd 2014Artigo -
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Efficacy of Enzyme and Substrate Reduction Therapy with a Novel Antagonist of Glucosylceramide Synthase for Fabry Disease gan Karen M. Ashe, Eva Budman, Dinesh S. Bangari, Craig Siegel, Jennifer B. Nietupski, Bing Wang, Robert J. Desnick, Ronald K. Scheule, John P. Leonard, Seng H. Cheng, John Marshall
Cyhoeddwyd 2015Artigo -
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Substrate Reduction Augments the Efficacy of Enzyme Therapy in a Mouse Model of Fabry Disease gan John Marshall, Karen M. Ashe, Dinesh S. Bangari, KerryAnne McEachern, Wei-Lien Chuang, Joshua Pacheco, Diane Copeland, Robert J. Desnick, James A. Shayman, Ronald K. Scheule, Seng H. Cheng
Cyhoeddwyd 2010Artigo -
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Systemic Administration of AAV8-α-galactosidase A Induces Humoral Tolerance in Nonhuman Primates Despite Low Hepatic Expression gan Jennifer B. Nietupski, Gregory D Hurlbut, Robin J. Ziegler, Qiuming Chu, Bradley L. Hodges, Karen M. Ashe, Mark P. Bree, Seng H. Cheng, Richard J. Gregory, John Marshall, Ronald K. Scheule
Cyhoeddwyd 2011Artigo -
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Systemic Delivery of a Glucosylceramide Synthase Inhibitor Reduces CNS Substrates and Increases Lifespan in a Mouse Model of Type 2 Gaucher Disease gan Mario A. Cabrera-Salazar, Matthew DeRiso, Scott D. Bercury, Lingyun Li, John T. Lydon, William Weber, Nilesh Pande, Mandy Cromwell, Diane Copeland, John P. Leonard, Seng H. Cheng, Ronald K. Scheule
Cyhoeddwyd 2012Artigo -
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Preexisting Immunity and Low Expression in Primates Highlight Translational Challenges for Liver-directed AAV8-mediated Gene Therapy gan Gregory D Hurlbut, Robin J. Ziegler, Jennifer B. Nietupski, Joseph W. Foley, Lisa Woodworth, Elizabeth Meyers, Scott D. Bercury, Nilesh Pande, David W. Souza, Mark P. Bree, Michael Lukason, John Marshall, Seng H. Cheng, Ronald K. Scheule
Cyhoeddwyd 2010Artigo -
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Timing of Therapeutic Intervention Determines Functional and Survival Outcomes in a Mouse Model of Late Infantile Batten Disease gan Mario A. Cabrera-Salazar, Eric M. Roskelley, Jie Bu, Bradley L. Hodges, Nelson S. Yew, James C. Dodge, Lamya S. Shihabuddin, István Sohár, David E. Sleat, Ronald K. Scheule, Beverly L. Davidson, Seng H. Cheng, Peter Lobel, Marco A. Passini
Cyhoeddwyd 2007Artigo -
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Iminosugar-Based Inhibitors of Glucosylceramide Synthase Increase Brain Glycosphingolipids and Survival in a Mouse Model of Sandhoff Disease gan Karen M. Ashe, Dinesh S. Bangari, Lingyun Li, Mario A. Cabrera-Salazar, Scott D. Bercury, Jennifer B. Nietupski, Christopher G. F. Cooper, Johannes M. F. G. Aerts, Edward R. Lee, Diane Copeland, Seng H. Cheng, Ronald K. Scheule, John Marshall
Cyhoeddwyd 2011Artigo -
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Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial gan Eric W.F.W. Alton, David K Armstrong, Deborah Ashby, Katie J Bayfield, Diana Bilton, Emily V Bloomfield, A. Christopher Boyd, June Brand, Ruaridh Buchan, Roberto Calcedo, Paula Carvelli, Mario Chan, Seng H. Cheng, David Collie, Steve Cunningham, Heather Davidson, Gwyneth Davies, Jane C. Davies, Lee A. Davies, Maria H Dewar, Ann Doherty, Jackie Donovan, Natalie S Dwyer, Hala I Elgmati, Rosanna F Featherstone, Jemyr Gavino, Sabrina Gea‐Sorlí, Duncan M. Geddes, James Sr Gibson, Deborah R. Gill, A P Greening, Uta Griesenbach, David M. Hansell, Katharine Harman, Tracy Higgins, Samantha L. Hodges, Stephen C. Hyde, Laura Hyndman, J. Alastair Innes, Joseph Jacob, Nancy E. Jones, Brian F Keogh, Maria P. Limberis, Paul Lloyd-Evans, Alan Maclean, Michelle C Manvell, Dominique McCormick, Michael McGovern, Gerry McLachlan, Cuixiang Meng, M Angeles Montero, Hazel Milligan, Laura Moyce, Gordon Murray, Andrew G. Nicholson, Tina Osadolor, Javier Parra-Leiton, David J. Porteous, Ian A. Pringle, Emma K Punch, Kamila M Pytel, Alexandra L. Quittner, Gina Rivellini, Clare Saunders, Ronald K. Scheule, Sarah Sheard, Nicholas J. Simmonds, Keith Smith, Stephen N. Smith, Najwa Soussi, Samia Soussi, Emma J Spearing, Barbara Stevenson, Stephanie Jones, Minna Turkkila, Rosa P Ureta, Michael D Waller, Marguerite Y Wasowicz, James M. Wilson, Paul Wolstenholme-Hogg
Cyhoeddwyd 2015Artigo
Offerynnau Chwilio:
Pynciau Perthynol
Biology
Biochemistry
Internal medicine
Medicine
Gene
Disease
Recombinant DNA
Chemistry
Enzyme replacement therapy
Gene expression
Genetics
Molecular biology
Pharmacology
Transfection
Transgene
Vector (molecular biology)
CpG site
DNA
DNA methylation
Enzyme
Genetic enhancement
Glycosphingolipid
Immunology
Lysosomal storage disease
Pathology
Receptor
Substrate reduction therapy
Virology
Alpha-galactosidase
Antibody