Resultats de la cerca - Mathilde Cohen-Tannoudji
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1
Gene Therapy for ALS—A Perspective per M Cappella, Chiara Ciotti, Mathilde Cohen-Tannoudji, Maria Grazia Biferi
Publicat 2019Revisão -
2
Systemic AAVrh10 provides higher transgene expression than AAV9 in the brain and the spinal cord of neonatal mice per Yannick Tanguy, Maria Grazia Biferi, Aurore Besse, Stéphanie Astord, Mathilde Cohen-Tannoudji, Thibaut Marais, Martine Barkats
Publicat 2015Artigo -
3
A New AAV10-U7-Mediated Gene Therapy Prolongs Survival and Restores Function in an ALS Mouse Model per Maria Grazia Biferi, Mathilde Cohen-Tannoudji, Ambra Cappelletto, Benoit Giroux, Marianne Roda, Stéphanie Astord, Thibaut Marais, Corinne Bos, Thomas Voit, Arnaud Ferry, Martine Barkats
Publicat 2017Artigo -
4
Cofilin-1 phosphorylation catalyzed by ERK1/2 alters cardiac actin dynamics in dilated cardiomyopathy caused by lamin A/C gene mutation per Maria Chatzifrangkeskou, David Yadin, Thibaut Marais, Solenne Chardonnet, Mathilde Cohen-Tannoudji, Nathalie Mougenot, Alain Schmitt, Silvia Crasto, Elisa Di Pasquale, Coline Macquart, Yannick Tanguy, Imen Jebeniani, Michel Pucéat, Blanca Morales Rodríguez, Wolfgang H. Goldmann, Matteo Dal Ferro, Maria Grazia Biferi, Petra Knaus, Gisèle Bonne, Howard J. Worman, Antoine Muchir
Publicat 2018Artigo -
5
Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase per Francesco Puzzo, Pasqualina Colella, Maria Grazia Biferi, Deeksha Bali, Nicole K. Paulk, Patrice Vidal, Fanny Collaud, Marcelo Simon‐Sola, Séverine Charles, Romain Hardet, Christian Leborgne, Amine Meliani, Mathilde Cohen-Tannoudji, Stéphanie Astord, Bernard Gjata, Pauline Sellier, Laetitia van Wittenberghe, Alban Vignaud, Florence Boisgérault, Martine Barkats, Pascal Laforêt, Mark A. Kay, Dwight D. Koeberl, Giuseppe Ronzitti, Federico Mingozzi
Publicat 2017Artigo
Eines de cerca:
Matèries relacionades
Biology
Medicine
Gene
Genetic enhancement
Genetics
Adeno-associated virus
Cell biology
Disease
Neuroscience
Pathology
Recombinant DNA
Vector (molecular biology)
Actin
Actin cytoskeleton
Amyotrophic lateral sclerosis
Biochemistry
Bioinformatics
Cancer research
Cardiomyopathy
Cell
Central nervous system
Cofilin
Computational biology
Cytoskeleton
Function (biology)
Heart failure
Internal medicine
LMNA
Lamin
Motor neuron