檢索結果 - Mathilde Cohen-Tannoudji
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Gene Therapy for ALS—A Perspective 由 M Cappella, Chiara Ciotti, Mathilde Cohen-Tannoudji, Maria Grazia Biferi
出版 2019Revisão -
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A New AAV10-U7-Mediated Gene Therapy Prolongs Survival and Restores Function in an ALS Mouse Model 由 Maria Grazia Biferi, Mathilde Cohen-Tannoudji, Ambra Cappelletto, Benoit Giroux, Marianne Roda, Stéphanie Astord, Thibaut Marais, Corinne Bos, Thomas Voit, Arnaud Ferry, Martine Barkats
出版 2017Artigo -
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Cofilin-1 phosphorylation catalyzed by ERK1/2 alters cardiac actin dynamics in dilated cardiomyopathy caused by lamin A/C gene mutation 由 Maria Chatzifrangkeskou, David Yadin, Thibaut Marais, Solenne Chardonnet, Mathilde Cohen-Tannoudji, Nathalie Mougenot, Alain Schmitt, Silvia Crasto, Elisa Di Pasquale, Coline Macquart, Yannick Tanguy, Imen Jebeniani, Michel Pucéat, Blanca Morales Rodríguez, Wolfgang H. Goldmann, Matteo Dal Ferro, Maria Grazia Biferi, Petra Knaus, Gisèle Bonne, Howard J. Worman, Antoine Muchir
出版 2018Artigo -
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Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase 由 Francesco Puzzo, Pasqualina Colella, Maria Grazia Biferi, Deeksha Bali, Nicole K. Paulk, Patrice Vidal, Fanny Collaud, Marcelo Simon‐Sola, Séverine Charles, Romain Hardet, Christian Leborgne, Amine Meliani, Mathilde Cohen-Tannoudji, Stéphanie Astord, Bernard Gjata, Pauline Sellier, Laetitia van Wittenberghe, Alban Vignaud, Florence Boisgérault, Martine Barkats, Pascal Laforêt, Mark A. Kay, Dwight D. Koeberl, Giuseppe Ronzitti, Federico Mingozzi
出版 2017Artigo
相關主題
Biology
Medicine
Gene
Genetic enhancement
Genetics
Adeno-associated virus
Cell biology
Disease
Neuroscience
Pathology
Recombinant DNA
Vector (molecular biology)
Actin
Actin cytoskeleton
Amyotrophic lateral sclerosis
Biochemistry
Bioinformatics
Cancer research
Cardiomyopathy
Cell
Central nervous system
Cofilin
Computational biology
Cytoskeleton
Function (biology)
Heart failure
Internal medicine
LMNA
Lamin
Motor neuron