Výsledky vyhledávání - Laurence Guianvarc’h
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Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome Autor Fanny Collaud, Giulia Bortolussi, Laurence Guianvarc’h, Sem J. Aronson, Thierry Bordet, P. Véron, Séverine Charles, Patrice Vidal, Marcelo Simon Sola, Stéphanie Rundwasser, Delphine G. Dufour, Florence Lacoste, Cyril Luc, Laetitia van Wittenberghe, Samia Martin, Christine Le Bec, Piter J. Bosma, Andrés F. Muro, Giuseppe Ronzitti, Matthias Hebben, Federico Mingozzi
Vydáno 2018Artigo -
2
Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders Autor Jihad El Andari, Edith Renaud-Gabardos, Warut Tulalamba, Jonas Weinmann, Louise Mangin, Quang Hong Pham, Susanne Hille, Antonette Bennett, Esther Attebi, Emanuele Bourges, Christian Leborgne, Nicolas Guerchet, Julia Fakhiri, Chiara Krämer, Ellen Wiedtke, Robert McKenna, Laurence Guianvarc’h, Magali Toueille, Giuseppe Ronzitti, Matthias Hebben, Federico Mingozzi, Thierry VandenDriessche, Mavis Agbandje‐McKenna, Oliver J. Müller, Marinee Chuah, Ana Buj‐Bello, Dirk Grimm
Vydáno 2022Artigo
Vyhledávací nástroje:
Související témata
Bioinformatics
Biology
Computational biology
Gene
Genetic enhancement
Genetics
Medicine
Recombinant DNA
Vector (molecular biology)
Viral vector
Virology
Adeno-associated virus
Anatomy
Biochemistry
Biodistribution
Capsid
Cell biology
Clinical trial
Duchenne muscular dystrophy
Dystrophin
Enzyme
Furin
Gene delivery
Genome
Genome editing
Immunology
In vivo
Internal medicine
Muscle disorder
Muscular dystrophy