Torthaí cuardaigh - Jin‐Hong Shin
- 1 - 16 toradh as 16 á dtaispeáint
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1
The evolution of heart gene delivery vectors de réir Nalinda B. Wasala, Jin‐Hong Shin, Dongsheng Duan
Foilsithe / Cruthaithe 2011Revisão -
2
AAV-microdystrophin Therapy Improves Cardiac Performance in Aged Female mdx Mice de réir Benjamín C. Bostick, Jin‐Hong Shin, Yongping Yue, Dongsheng Duan
Foilsithe / Cruthaithe 2011Artigo -
3
Genotyping<i>mdx</i>,<i>mdx3cv</i>, and<i>mdx4cv</i>mice by primer competition polymerase chain reaction de réir Jin‐Hong Shin, Chady H. Hakim, Keqing Zhang, Dongsheng Duan
Foilsithe / Cruthaithe 2010Artigo -
4
SERCA2a gene transfer improves electrocardiographic performance in aged mdx mice de réir Jin‐Hong Shin, Benjamín C. Bostick, Yongping Yue, Roger J. Hajjar, Dongsheng Duan
Foilsithe / Cruthaithe 2011Artigo -
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AAV micro-dystrophin gene therapy alleviates stress-induced cardiac death but not myocardial fibrosis in > 21-m-old mdx mice, an end-stage model of Duchenne muscular dystrophy c... de réir Benjamín C. Bostick, Jin‐Hong Shin, Yongping Yue, Nalinda B. Wasala, Yi Lai, Dongsheng Duan
Foilsithe / Cruthaithe 2012Artigo -
7
Transduction Efficiency and Immune Response Associated With the Administration of AAV8 Vector Into Dog Skeletal Muscle de réir Sachiko Ohshima, Jin‐Hong Shin, Katsutoshi Yuasa, Akiyo Nishiyama, Jun‐ichi Kira, Takashi Okada, Shin’ichi Takeda
Foilsithe / Cruthaithe 2008Artigo -
8
An intronic LINE-1 element insertion in the dystrophin gene aborts dystrophin expression and results in Duchenne-like muscular dystrophy in the corgi breed de réir B. F. Smith, Yongping Yue, Philip R. Woods, Joe N. Kornegay, Jin‐Hong Shin, Regina R Williams, Dongsheng Duan
Foilsithe / Cruthaithe 2010Artigo -
9
Microdystrophin Ameliorates Muscular Dystrophy in the Canine Model of Duchenne Muscular Dystrophy de réir Jin‐Hong Shin, Xiufang Pan, Chady H. Hakim, H. T. Yang, Yongping Yue, Keqing Zhang, Ronald L. Terjung, Dongsheng Duan
Foilsithe / Cruthaithe 2013Artigo -
10
Safe and bodywide muscle transduction in young adult Duchenne muscular dystrophy dogs with adeno-associated virus de réir Yongping Yue, Xiufang Pan, Chady H. Hakim, Kasun Kodippili, Keqing Zhang, Jin‐Hong Shin, H. T. Yang, Thomas McDonald, Dongsheng Duan
Foilsithe / Cruthaithe 2015Artigo -
11
Dual AAV Gene Therapy for Duchenne Muscular Dystrophy with a 7-kb <i>Mini-Dystrophin</i> Gene in the Canine Model de réir Kasun Kodippili, Chady H. Hakim, Xiufang Pan, H. T. Yang, Yongping Yue, Yadong Zhang, Jin‐Hong Shin, N. Nora Yang, Dongsheng Duan
Foilsithe / Cruthaithe 2017Artigo -
12
Adeno-Associated Virus Serotype 6 Capsid Tyrosine-to-Phenylalanine Mutations Improve Gene Transfer to Skeletal Muscle de réir Chunping Qiao, Wei Zhang, Zhenhua Yuan, Jin‐Hong Shin, Jianbin Li, Giridhara R. Jayandharan, Zhong Li, Arun Srivastava, Xiao Xiao, Dongsheng Duan
Foilsithe / Cruthaithe 2010Artigo -
13
Genetic Variants Associated with Episodic Ataxia in Korea de réir Kwang‐Dong Choi, Ji‐Soo Kim, Hyo‐Jung Kim, Ileok Jung, Seong‐Hae Jeong, Seung‐Han Lee, Dong Uk Kim, Sang-Ho Kim, Seo‐Young Choi, Jin‐Hong Shin, Dae‐Seong Kim, Kyung‐Pil Park, Hyang-Sook Kim, Jae‐Hwan Choi
Foilsithe / Cruthaithe 2017Artigo -
14
Myo‐Guide: A Machine Learning‐Based Web Application for Neuromuscular Disease Diagnosis With MRI de réir José Verdú-Díaz, C. Bolano-Díaz, A. Gonzalez-Chamorro, S Fitzsimmons, Jodi Warman‐Chardon, Goknur Selen Kocak, Debora Mucida‐Alvim, Ian C. P. Smith, John Vissing, Nanna Scharff Poulsen, Sushan Luo, Cristina Domínguez‐González, Laura Bermejo‐Guerrero, David Gómez‐Andrés, J. Sotoca, Anna Pichiecchio, Silvia Nicolosi, Mauro Monforte, Claudia Brogna, Eugenio Mercuri, Jorge A. Bevilacqua, Jorge Díaz‐Jara, Benjamín Pizarro‐Galleguillos, Peter Krkoška, Jorge Alonso‐Pérez, Montse Olivé, Erik H. Niks, Hermien E. Kan, James B Lilleker, Mark Roberts, Bianca Buchignani, Jin‐Hong Shin, Florence Esselin, Emmanuelle Le Bars, Anne Marie Childs, Edoardo Malfatti, Anna Sárközy, Luke Perry, Sniya Sudhakar, Edmar Zanoteli, Filipe Tupinamba Di Pace, Emma Matthews, Shahram Attarian, David Bendahan, Matteo Garibaldi, Laura Fionda, Alicia Alonso‐Jiménez, Robert Carlier, Ali Asghar Okhovat, Shahriar Nafissi, Atchayaram Nalini, Seena Vengalil, Kieren G. Hollingsworth, Chiara Marini‐Bettolo, Volker Straub, Giorgio Tasca, Jaume Bacardit, Jordi Díaz‐Manera
Foilsithe / Cruthaithe 2025Artigo -
15
Genotype–phenotype correlations in valosin-containing protein disease: a retrospective muticentre study de réir Marianela Schiava, Chiseko Ikenaga, Rocío N. Villar‐Quiles, Marta Caballero‐Ávila, Ana Töpf, Ichizo Nishino, Virginia Kimonis, Bjarne Udd, Benedikt Schoser, Edmar Zanoteli, Paulo Victor Sgobbi de Souza, Giorgio Tasca, Thomas Lloyd, Adolfo Lopez-de Munain, Carmen Paradas, Elena Pegoraro, Aleksandra Nadaj-Pakleza, Jan De Bleecker, Umesh A. Badrising, Alicia Alonso‐Jiménez, Anna Kostera‐Pruszczyk, Francesc X. Miralles, Jin‐Hong Shin, Jorge A. Bevilacqua, Montse Olivé, Matthias Vorgerd, Rudi Kley, Stefen Brady, Timothy L. Williams, Cristina Domínguez‐González, George K. Papadimas, Jodi Warman‐Chardon, Kristl G. Claeys, Marianne de Visser, Nuria Muelas, Pascal Laforêt, Edoardo Malfatti, Lindsay N. Alfano, Sruthi Nair, Georgios Manousakis, Hani Kushlaf, Matthew Harms, Christopher Nance, Alba Ramos‐Fransí, Carmelo Rodolico, Channa Hewamadduma, Hakan Çetin, Jorge García‐García, Endre Pál, Maria Elena Farrugia, Phillipa J. Lamont, Colin Quinn, Velina Nedkova-Hristova, Stojan Peric, Sushan Luo, Anders Oldfors, Kate Taylor, Stuart H. Ralston, Tanya Stojkovic, Conrad C. Weihl, Jordi Díaz‐Manera
Foilsithe / Cruthaithe 2022Artigo -
16
104-week efficacy and safety of cipaglucosidase alfa plus miglustat in adults with late-onset Pompe disease: a phase III open-label extension study (ATB200-07) de réir Benedikt Schoser, Priya S. Kishnani, Drago Bratkovic, Barry J. Byrne, Kristl G. Claeys, Jordi Díaz‐Manera, Pascal Laforêt, Mark Roberts, António Toscano, Ans T. van der Ploeg, Jeff Castelli, Mitchell Goldman, Fred Holdbrook, Sheela Sitaraman Das, Y. Wasfi, Tahseen Mozaffar, Ágnes Sebök, Alan Pestronk, Aleksandra Dominović-Kovačević, Anzalee Khan, Blaž Koritnik, Céline Tard, Christopher Lindberg, Colin Quinn, Crystal Eldridge, Cynthia Bodkin, David Reyes‐Leiva, Derralynn Hughes, Ela Stefanescu, Emmanuelle Salort‐Campana, Ernest Butler, Françoise Bouhour, Gee Kim, George K. Papadimas, Giancarlo Parenti, Halina Bartosik-Psujek, Hani Kushlaf, Akihiro Hashiguchi, Heather Lau, Hélio Pedro, Henning Andersen, Hernán Amartino, Hideaki Shiraishi, Hiroshi Kobayashi, Ivaylo Tarnev, Jaime Vengoechea, Jennifer Avelar, Jin‐Hong Shin, John Nevin, Jonathan Cauci, Jorge Alonso‐Pérez, József Janszky, Julie Berthy, Cornelia Kornblum, Kristina Gutschmidt, Mária Judit Molnár, Marie Wencel, Mark A. Tarnopolsky, Matthias Boentert, Michel Tchan, Miriam Freimer, Nicola Longo, Nicolas J. Abreu, Nuria Vidal-Fernandez, Olimpia Musumeci, Özlem Göker-Alpan, Patrick Deegan, Paula R. Clemens, Richard Roxburgh, Robert Henderson, Robert J. Hopkin, Sabrina Sacconi, Simona Fecarotta, Shahram Attarian, Stephan Wenninger, Stephanie DeArmey, Tarekegn Hiwot, Thomas Andrew Burrow, Tobias Ruck, Tomo Sawada, Vescei Laszlo, Wolfgang N. Löscher, Yin‐Hsiu Chien
Foilsithe / Cruthaithe 2024Artigo
Uirlisí cuardaigh:
Ábhair a bhaineann le hábhar
Biology
Gene
Genetics
Medicine
Duchenne muscular dystrophy
Dystrophin
Internal medicine
Genetic enhancement
Muscular dystrophy
Gene delivery
Recombinant DNA
Vector (molecular biology)
Adeno-associated virus
Biochemistry
Cardiology
Cardiomyopathy
Disease
Endocrinology
Heart failure
Transduction (biophysics)
Bioinformatics
Computational biology
Dilated cardiomyopathy
Gene transfer
Genotype
Molecular biology
Muscle disorder
Muscle weakness
Mutation
Pathology