Rezultaty - Jie Bu
- Rezultaty 1 - 13 Rezultaty od 13
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CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy od Marco A. Passini, Jie Bu, Eric M. Roskelley, Amy M. Richards, S. Pablo Sardi, Catherine R. O’Riordan, K. Klinger, Lamya S. Shihabuddin, Seng H. Cheng
Wydane 2010Artigo -
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AAV Vector-Mediated Correction of Brain Pathology in a Mouse Model of Niemann–Pick A Disease od Marco A. Passini, Shannon L. Macauley, Michael R. Huff, Tatyana V. Taksir, Jie Bu, I‐Huan Wu, Peter Piepenhagen, James C. Dodge, Lamya S. Shihabuddin, Catherine R. O’Riordan, Edward H. Schuchman, Gregory R. Stewart
Wydane 2005Artigo -
7
Augmenting CNS glucocerebrosidase activity as a therapeutic strategy for parkinsonism and other Gaucher-related synucleinopathies od S. Pablo Sardi, Jennifer Clarke, Catherine Viel, Monyrath Chan, Thomas J. Tamsett, Christopher M. Treleaven, Jie Bu, Lindsay Sweet, Marco A. Passini, James C. Dodge, Wen H. Yu, Richard L. Sidman, Seng H. Cheng, Lamya S. Shihabuddin
Wydane 2013Artigo -
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Gene transfer of human acid sphingomyelinase corrects neuropathology and motor deficits in a mouse model of Niemann-Pick type A disease od James C. Dodge, Jennifer Clarke, Antonius Song, Jie Bu, Wendy Yang, Tatyana V. Taksir, Denise Griffiths, Michael Zhao, Edward H. Schuchman, Seng H. Cheng, Catherine R. O’Riordan, Lamya S. Shihabuddin, Marco A. Passini, Gregory R. Stewart
Wydane 2005Artigo -
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Antisense Oligonucleotides Delivered to the Mouse CNS Ameliorate Symptoms of Severe Spinal Muscular Atrophy od Marco A. Passini, Jie Bu, Amy M. Richards, Cathrine Kinnecom, S. Pablo Sardi, Lisa M. Stanek, Yimin Hua, Frank Rigo, John Matson, Gene Hung, Edward M. Kaye, Lamya S. Shihabuddin, Adrian R. Krainer, C. Frank Bennett, Seng H. Cheng
Wydane 2011Artigo -
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Timing of Therapeutic Intervention Determines Functional and Survival Outcomes in a Mouse Model of Late Infantile Batten Disease od Mario A. Cabrera-Salazar, Eric M. Roskelley, Jie Bu, Bradley L. Hodges, Nelson S. Yew, James C. Dodge, Lamya S. Shihabuddin, István Sohár, David E. Sleat, Ronald K. Scheule, Beverly L. Davidson, Seng H. Cheng, Peter Lobel, Marco A. Passini
Wydane 2007Artigo -
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Combination brain and systemic injections of AAV provide maximal functional and survival benefits in the Niemann-Pick mouse od Marco A. Passini, Jie Bu, Jonathan A. Fidler, Robin J. Ziegler, Joseph W. Foley, James C. Dodge, Wendy W. Yang, Jennifer Clarke, Tatyana V. Taksir, Denise Griffiths, Michael Zhao, Catherine R. O’Riordan, Edward H. Schuchman, Lamya S. Shihabuddin, Seng H. Cheng
Wydane 2007Artigo -
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Intracranial Delivery of CLN2 Reduces Brain Pathology in a Mouse Model of Classical Late Infantile Neuronal Ceroid Lipofuscinosis od Marco A. Passini, James C. Dodge, Jie Bu, Wendy Yang, Qi Zhao, Dolan Sondhi, Neil R. Hackett, Stephen M. Kaminsky, Qinwen Mao, Lamya S. Shihabuddin, Seng H. Cheng, David E. Sleat, Gregory R. Stewart, Beverly L. Davidson, Peter Lobel, Ronald G. Crystal
Wydane 2006Artigo -
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AAV-mediated ARSA replacement for the treatment of Metachromatic Leukodystrophy od Sujith Ramachandran, Jeffery Ardinger, Jie Bu, M. Isabel Alcalá Ramos, Lilu Guo, Debabrata Ghosh, Mahmud Hossain, Shelley N. Chou, Chen Yao, Erik Wischof, Swathi Ayloo, Roger Trullo, Yongde Luo, Jessica M. Hogestyn, Daniel M DuBreuil, Emily Crosier, Johanna Adams, Amy M. Richards, Michael Tsabar, Giorgio Gaglia, Shelly Nass, Bindu Nambiar, Denise Woodcock, Catherine R. O’Riordan, Qi Tang, Bradford Elmer, Bailin Zhang, Martin Goulet, Christian Mueller
Wydane 2025Pré-impressão
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