Sökresultat - Ivan Labik
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Betibeglogene Autotemcel Gene Therapy for Non–β <sup>0</sup> /β <sup>0</sup> Genotype β-Thalassemia av Franco Locatelli, Alexis A. Thompson, Janet L. Kwiatkowski, John B. Porter, Adrian J. Thrasher, Suradej Hongeng, Martin G. Sauer, Isabelle Thuret, Ashutosh Lal, Mattia Algeri, Jennifer Schneiderman, Timothy S. Olson, Ben Carpenter, Persis Amrolia, Usanarat Anurathapan, Axel Schambach, Christian Chabannon, Manfred Schmidt, Ivan Labik, Heidi Elliot, Ruiting Guo, Mohammed Asmal, Richard A. Colvin, Mark C. Walters
Publicerad 2021Artigo -
2
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency av Donald B. Kohn, Claire Booth, Kit L. Shaw, Jinhua Xu‐Bayford, Elizabeth Garabedian, Valentina Trevisan, Denise A. Carbonaro-Sarracino, Kajal Soni, Dayna Terrazas, Katie Snell, Alan K. Ikeda, Diego León‐Rico, Theodore B. Moore, Karen Buckland, Ami J. Shah, Kimberly Gilmour, Satiro De Oliveira, Christine Rivat, Gay M. Crooks, Natalia Izotova, John Tse, Stuart Adams, Sally Shupien, Hilory Ricketts, Alejandra Davila, Chilenwa Uzowuru, Amalia Icreverzi, Provaboti Barman, Beatriz Campo Fernandez, Roger P. Hollis, Maritess Coronel, Allen Chi-Shing Yu, Krista Chun, Christian E. Casas, Ruixue Zhang, Serena Arduini, Frances Lynn, Mahesh Kudari, Andrea Spezzi, Marco Zahn, Rene Heimke, Ivan Labik, Roberta Parrott, Rebecca H. Buckley, Lilith Reeves, Kenneth Cornetta, Robert Sokolic, Michael S. Hershfield, Manfred Schmidt, Fabio Candotti, Harry L. Malech, Adrian J. Thrasher, H. Bobby Gaspar
Publicerad 2021Artigo
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Relaterade ämnen
Biology
Gene
Genetic enhancement
Genetics
Internal medicine
Medicine
AMP deaminase
Adenosine
Adenosine deaminase
Adenosine deaminase deficiency
Adverse effect
Beta thalassemia
Blood transfusion
Busulfan
Ex vivo
Gastroenterology
Hematopoietic stem cell transplantation
Hemoglobin
Immune system
Immunodeficiency
Immunology
In vivo
Pediatrics
Primary immunodeficiency
Severe combined immunodeficiency
Surgery
Thalassemia
Transfusion medicine
Transplantation
Virology