Søgeresultater - Francesca Ferrua

Refine Results
  1. 1
    Twenty-Five Years of Gene Therapy for ADA-SCID: From<i>Bubble Babies</i>to an Approved Drug

    Twenty-Five Years of Gene Therapy for ADA-SCID: From<i>Bubble Babies</i>to an Approved Drug af Francesca Ferrua, Alessandro Aiuti

    Udgivet 2017
    Få fuldtekst
    Revisão
    Føj til favoritter
    Saved in:
  2. 2
    Gene therapy for Wiskott-Aldrich syndrome: History, new vectors, future directions

    Gene therapy for Wiskott-Aldrich syndrome: History, new vectors, future directions af Francesca Ferrua, Francesco Marangoni, Alessandro Aiuti, Maria Grazia Roncarolo

    Udgivet 2020
    Få fuldtekst
    Editorial
    Føj til favoritter
    Saved in:
  3. 3
    Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety

    Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety af Maria Pia Cicalese, Francesca Ferrua, Laura Castagnaro, Katie Rolfe, Erika De Boever, Rickey R. Reinhardt, Jonathan Appleby, Maria Grazia Roncarolo, Alessandro Aiuti

    Udgivet 2018
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  4. 4
    B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome

    B-cell reconstitution after lentiviral vector–mediated gene therapy in patients with Wiskott-Aldrich syndrome af Maria Carmina Castiello, Samantha Scaramuzza, Francesca Pala, Francesca Ferrua, Paolo Uva, Immacolata Brigida, Lucia Piceni Sereni, Mirjam van der Burg, Giorgio Ottaviano, Michael H. Albert, Maria Grazia Roncarolo, Luigi Naldini, Alessandro Aiuti, Anna Villa, Marita Bosticardo

    Udgivet 2015
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  5. 5
    Thymic Epithelium Abnormalities in DiGeorge and Down Syndrome Patients Contribute to Dysregulation in T Cell Development

    Thymic Epithelium Abnormalities in DiGeorge and Down Syndrome Patients Contribute to Dysregulation in T Cell Development af Genni Enza Marcovecchio, Ileana Bortolomai, Francesca Ferrua, Elena Fontana, Luisa Imberti, Erika Conforti, Donato Amodio, Sonia Bergante, Giulia Macchiarulo, Veronica D’Oria, Francesca Conti, Silvia Di Cesare, Georgia Fousteri, Adriano Carotti, Alessandro Giamberti, Pietro Luigi Poliani, Luigi D. Notarangelo, Caterina Cancrini, Anna Villa, Marita Bosticardo

    Udgivet 2019
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  6. 6
    Gene Modification and Three-Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches

    Gene Modification and Three-Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches af Ileana Bortolomai, Monica Sandri, Elena Draghici, Elena Fontana, Elisabetta Campodoni, Genni Enza Marcovecchio, Francesca Ferrua, Laura Perani, Antonello E. Spinelli, Tamara Canu, Marco Catucci, Tiziano Di Tomaso, Lucia Sergi Sergi, Antonio Esposito, Angelo Lombardo, Luigi Naldini, Anna Tampieri, Georg A. Holländer, Anna Villa, Marita Bosticardo

    Udgivet 2019
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  7. 7
    In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution Phases

    In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution Phases af Luca Biasco, Danilo Pellin, Serena Scala, Francesca Dionisio, Luca Basso‐Ricci, Lorena Leonardelli, Samantha Scaramuzza, Cristina Baricordi, Francesca Ferrua, Maria Pia Cicalese, Stefania Giannelli, Victor Neduva, David J. Dow, Manfred Schmidt, Christof von Kalle, Maria Grazia Roncarolo, Fabio Ciceri, Paola Vicard, Ernst C. Wit, Clelia Di Serio, Luigi Naldini, Alessandro Aiuti

    Udgivet 2016
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  8. 8
    Outcome of BCG Vaccination in ADA-SCID Patients: A 12-Patient Series

    Outcome of BCG Vaccination in ADA-SCID Patients: A 12-Patient Series af Daniele Canarutto, Chiara Oltolini, Federica Barzaghi, Valeria Calbi, Maddalena Migliavacca, Francesca Tucci, Vera Gallo, Giulia Consiglieri, Francesca Ferrua, Salvatore Recupero, Maria Célia Cervi, Hamoud Al‐Mousa, Anna Pituch‐Noworolska, Chiara Tassan Din, Paolo Scarpellini, Paolo Silvani, Claudia Fossati, Miriam Casiraghi, Daniela María Cirillo, Antonella Castagna, Maria Ester Bernardo, Alessandro Aiuti, Maria Pia Cicalese

    Udgivet 2023
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  9. 9
    Lentiviral gene therapy corrects platelet phenotype and function in patients with Wiskott-Aldrich syndrome

    Lentiviral gene therapy corrects platelet phenotype and function in patients with Wiskott-Aldrich syndrome af Lucia Piceni Sereni, Maria Carmina Castiello, Dario Di Silvestre, Patrizia Della Valle, Chiara Brombin, Francesca Ferrua, Maria Pia Cicalese, L. Pozzi, Maddalena Migliavacca, Maria Ester Bernardo, Claudio Pignata, Roula Farah, Lucia Dora Notarangelo, Nufar Marcus, Lorella Cattaneo, Marco Spinelli, Stefania Giannelli, Marita Bosticardo, Koen van Rossem, Armando D’Angelo, Alessandro Aiuti, Pierluigi Mauri, Anna Villa

    Udgivet 2019
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  10. 10
    Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome

    Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome af Valentina Vavassori, E. Mercuri, Genni Enza Marcovecchio, Maria Carmina Castiello, Giulia Schiroli, Luisa Albano, Carrie M. Margulies, Frank A. Buquicchio, Elena Fontana, Stefano Beretta, Ivan Merelli, Andrea Cappelleri, Paola M. V. Rancoita, Vassilios Lougaris, Alessandro Plebani, Maria Kanariou, Arjan C. Lankester, Francesca Ferrua, Eugenio Scanziani, Cecilia Cotta‐Ramusino, Anna Villa, Luigi Naldini, Pietro Genovese

    Udgivet 2021
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  11. 11
    Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency

    Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency af Maria Pia Cicalese, Francesca Ferrua, Laura Castagnaro, Roberta Pajno, Federica Barzaghi, Stefania Giannelli, Francesca Dionisio, Immacolata Brigida, Marco Bonopane, Miriam Casiraghi, Antonella Tabucchi, Filippo Carlucci, Eyal Grunebaum, Mehdi Adeli, Robbert G. M. Bredius, Jennifer M. Puck, Polina Stepensky, İlhan Tezcan, Katie Rolfe, Erika De Boever, Rickey R. Reinhardt, Jonathan Appleby, Fabio Ciceri, Maria Grazia Roncarolo, Alessandro Aiuti

    Udgivet 2016
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  12. 12
    Alterations in the brain adenosine metabolism cause behavioral and neurological impairment in ADA-deficient mice and patients

    Alterations in the brain adenosine metabolism cause behavioral and neurological impairment in ADA-deficient mice and patients af Aisha V. Sauer, Raisa Jofra Hernández, Francesca Fumagalli, Veronica Bianchi, Pietro Luigi Poliani, Chiara Dallatomasina, Elisa Riboni, Letterio S. Politi, Antonella Tabucchi, Filippo Carlucci, Miriam Casiraghi, Nicola Carriglio, Manuela Cominelli, Carlo Alberto Forcellini, Federica Barzaghi, Francesca Ferrua, Fabio Minicucci, S. Medaglini, Letizia Leocani, Giancarlo la Marca, Lucia Dora Notarangelo, Chiara Azzari, Cristoforo Comi, Cristina Baldoli, Sabrina Canale, Maria Sessa, Patrizia D’Adamo, Alessandro Aiuti

    Udgivet 2017
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  13. 13
    Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis

    Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis af Pamela Quaranta, Luca Basso‐Ricci, Raisa Jofra Hernández, Guido Pacini, Matteo Maria Naldini, Matteo Barcella, Luca Seffin, Giulia Pais, Giulio Spinozzi, Fabrizio Benedicenti, Carlo Pietrasanta, Jin‐Gyu Cheong, Andrea Ronchi, Lorenza Pugni, Francesca Dionisio, Ilaria Monti, Stefania Giannelli, Silvia Darin, Federico Fraschetta, Graziano Barera, Francesca Ferrua, Valeria Calbi, Marco Ometti, Raffaella Di Micco, Fabio Mosca, Steven Z. Josefowicz, Eugenio Montini, Andrea Calabria, Maria Ester Bernardo, Maria Pia Cicalese, Bernhard Gentner, Ivan Merelli, Alessandro Aiuti, Serena Scala

    Udgivet 2024
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  14. 14
    Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

    Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study af Francesca Ferrua, Maria Pia Cicalese, Stefania Galimberti, Stefania Giannelli, Francesca Dionisio, Federica Barzaghi, Maddalena Migliavacca, Maria Ester Bernardo, Valeria Calbi, Andrea Assanelli, Marcella Facchini, Claudia Fossati, Elena Albertazzi, Samantha Scaramuzza, Immacolata Brigida, Serena Scala, Luca Basso‐Ricci, Roberta Pajno, Miriam Casiraghi, Daniele Canarutto, Federica Andrea Salerio, Michael H. Albert, A. Bartoli, Hermann M. Wolf, Rossana Fiori, Paolo Silvani, Salvatore Gattillo, Anna Villa, Luca Biasco, Christopher Dott, Emily J Culme-Seymour, Koenraad van Rossem, Gillian Atkinson, Maria Grazia Valsecchi, Maria Grazia Roncarolo, Fabio Ciceri, Luigi Naldini, Alessandro Aiuti

    Udgivet 2019
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  15. 15
    Targeted NGS Platforms for Genetic Screening and Gene Discovery in Primary Immunodeficiencies

    Targeted NGS Platforms for Genetic Screening and Gene Discovery in Primary Immunodeficiencies af Cristina Cifaldi, Immacolata Brigida, Federica Barzaghi, Matteo Zoccolillo, Valentina Ferradini, Davide Petricone, Maria Pia Cicalese, Dejan Lazarević, Davide Cittaro, Maryam Omrani, Enrico Attardi, Francesca Conti, Alessia Scarselli, Maria Serena Chiriacò, Silvia Di Cesare, Francesco Licciardi, Davide Montin, Francesca Ferrua, Clementina Canessa, Claudio Pignata, Silvia Giliani, Simona Ferrari, Georgia Fousteri, Graziano Barera, Pietro Merli, Paolo Palma, Simone Cesaro, Marco Gattorno, Antonio Trizzino, Viviana Moschese, L Chini, Anna Villa, Chiara Azzari, Andrea Finocchi, Franco Locatelli, Paolo Rossi, Federica Sangiuolo, Alessandro Aiuti, Caterina Cancrini, Gigliola Di Matteo

    Udgivet 2019
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  16. 16
    Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome

    Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome af Alessandro Aiuti, Luca Biasco, Samantha Scaramuzza, Francesca Ferrua, Maria Pia Cicalese, Cristina Baricordi, Francesca Dionisio, Andrea Calabria, Stefania Giannelli, Maria Carmina Castiello, Marita Bosticardo, Costanza Evangelio, Andrea Assanelli, Miriam Casiraghi, Sara Galimberti, Luciano Callegaro, Claudia Benati, Paolo Rizzardi, Danilo Pellin, Clelia Di Serio, Manfred Schmidt, Christof von Kalle, Jason P. Gardner, Nalini Mehta, Victor Neduva, David J. Dow, Anne Galy, R Miniero, Andrea Finocchi, Ayşe Metìn, Pinaki P. Banerjee, Jordan S. Orange, Stefania Galimberti, Maria Grazia Valsecchi, Alessandra Biffi, Eugenio Montini, Anna Villa, Fabio Ciceri, Maria Grazia Roncarolo, Luigi Naldini

    Udgivet 2013
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  17. 17
    Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome

    Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome af Bernhard Gentner, Francesca Tucci, Stefania Galimberti, Francesca Fumagalli, Maurizio De Pellegrin, Paolo Silvani, Chiara Camesasca, Silvia Pontesilli, Silvia Darin, Francesca Ciotti, Marina Sarzana, Giulia Consiglieri, Chiara Filisetti, G Forni, Laura Passerini, Daniela Tomasoni, Daniela Cesana, Andrea Calabria, Giulio Spinozzi, Maria-Pia Cicalese, Valeria Calbi, Maddalena Migliavacca, Federica Barzaghi, Francesca Ferrua, Vera Gallo, Simona Miglietta, Erika Zonari, Patali S. Cheruku, Cristiana Forni, Marcella Facchini, Ambra Corti, Michela Gabaldo, Stefano Zancan, Serena Gasperini, Attilio Rovelli, Jaap Jan Boelens, Simon Jones, Robert Wynn, Cristina Baldoli, Eugenio Montini, Silvia Gregori, Fabio Ciceri, Maria Grazia Valsecchi, Giancarlo la Marca, Rossella Parini, Luigi Naldini, Alessandro Aiuti, Maria-Ester Bernardo

    Udgivet 2021
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  18. 18
    Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

    Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded acc... af Francesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora, Maria Sessa, Cristina Baldoli, Paola M. V. Rancoita, Francesca Ciotti, Marina Sarzana, Maddalena Fraschini, Alberto A. Zambon, Serena Acquati, Daniela Redaelli, Vanessa Attanasio, Simona Miglietta, Fabiola De Mattia, Federica Barzaghi, Francesca Ferrua, Maddalena Migliavacca, Francesca Tucci, Vera Gallo, Ubaldo Del Carro, Sabrina Canale, Ivana Spiga, Laura Lorioli, Salvatore Recupero, Elena Sophia Fratini, Francesco Morena, Paolo Silvani, Maria Rosa Calvi, Marcella Facchini, Sara Locatelli, Ambra Corti, Stefano Zancan, Gigliola Antonioli, Giada Farinelli, Michela Gabaldo, Jesus Garcia‐Segovia, Laetitia Schwab, Gerald Downey, Massimo Filippi, Maria Pia Cicalese, Sabata Martino, Clelia Di Serio, Fabio Ciceri, Maria Ester Bernardo, Luigi Naldini, Alessandra Biffi, Alessandro Aiuti

    Udgivet 2022
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  19. 19
    Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency

    Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency af Maddalena Migliavacca, Federica Barzaghi, Claudia Fossati, Paola M. V. Rancoita, Michela Gabaldo, Francesca Dionisio, Stefania Giannelli, Federica Andrea Salerio, Francesca Ferrua, Francesca Tucci, Valeria Calbi, Vera Gallo, Salvatore Recupero, Giulia Consiglieri, Roberta Pajno, Maria Sambuco, Alessio Priolo, Chiara Ferri, Vittoria Garella, Ilaria Monti, Paolo Silvani, Silvia Darin, Miriam Casiraghi, Ambra Corti, Stefano Zancan, Margherita Levi, Daniela Cesana, Filippo Carlucci, Anna Pituch‐Noworolska, Dalia Abd Elaziz, Ulrich Baumann, Andrea Finocchi, Caterina Cancrini, Saverio Ladogana, Andrea Meinhardt, Isabelle Meyts, Davide Montin, Lucia Dora Notarangelo, Fulvio Porta, Marlène Pasquet, Carsten Speckmann, Polina Stepensky, Alberto Tommasini, Marco Rabusin, Zeynep Karakaş, Miguel Galicchio, Lucia Leonardi, Marzia Duse, Şükrü Nail Güner, Clelia Di Serio, Fabio Ciceri, Maria Ester Bernardo, Alessandro Aiuti, Maria Pia Cicalese

    Udgivet 2024
    Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:
  20. 20
    Hematopoietic cell transplantation in severe combined immunodeficiency: The SCETIDE 2006-2014 European cohort

    Hematopoietic cell transplantation in severe combined immunodeficiency: The SCETIDE 2006-2014 European cohort af Arjan C. Lankester, Bénédicte Neven, Nizar Mahlaoui, Erik G. J. von Asmuth, Virginie Courteille, Mikael Alligon, Michael H. Albert, Isabelle Serra, Peter Bader, Dmitry Balashov, Rita Beier, Yves Bertrand, Stéphane Blanche, Victoria Bordon, Robbert G. M. Bredius, Andrew J. Cant, Marina Cavazzana, Cristina Díaz de Heredia, Figen Doğu, Karoline Ehlert, Natacha Entz‐Werlé, Anders Fasth, Francesca Ferrua, Alina Ferster, Renata Formánková, Wilhelm Friedrich, Marta González‐Vicent, Jolanta Goździk, Tayfun Güngör, Manfred Hoenig, Aydan İkincioğulları, Krzysztof Kałwak, Savaş Kansoy, Alphan Küpesiz, Arnalda Lanfranchi, Caroline A. Lindemans, Roland Meisel, Gérard Michel, Nuno Miranda, José M. Moraleda, Despina Moshous, Herbert Pichler, Kanchan Rao, Petr Sedláček, Mary Slatter, Elena Soncini, Carsten Speckmann, Mikael Sundin, Amos Toren, Kim Vettenranta, Austen Worth, M. Akif Yeşilipek, Marco Zecca, Fulvio Porta, Ansgar Schulz, Paul Veys, Alain Fischer, Andrew R. Gennery

    Udgivet 2021
    Få fuldtekst Få fuldtekst
    Artigo
    Føj til favoritter
    Saved in:

Søgeredskaber: