Search Results - Faith Conroy
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Chemical engineering of therapeutic siRNAs for allele-specific gene silencing in Huntington’s disease models by Faith Conroy, Rachael Miller, Julia F. Alterman, Matthew Hassler, Dimas Echeverria, Bruno M.D.C. Godinho, Emily G. Knox, Ellen Sapp, Jaquelyn Sousa, Ken Yamada, Farah Mahmood, Adel Boudi, Kimberly B. Kegel-Gleason, Marian DiFiglia, Neil Aronin, Anastasia Khvorova, Edith L. Pfister
Published 2022Artigo -
2
Lowering the<i>HTT1a</i>transcript as an effective therapy for Huntingtons disease by Aikaterini S. Papadopoulou, Julia F. Alterman, Christian Landles, Edward J. Smith, Faith Conroy, Jemima Phillips, María Cañibano-Pico, Iulia M Nita, Georgina F Osborne, Arzo Iqbal, Sarah G. Aldous, Marie K. Bondulich, Casandra Gomez-Paredes, Kirupa Sathasivam, Daniel O’Reilly, Dimas Echeverria, Konstantin Bobkov, Jonathan Greene, Neil Aronin, Anastasia Khvorova, Gillian P. Bates
Published 2025Pré-impressão -
3
Artificial miRNAs Reduce Human Mutant Huntingtin Throughout the Striatum in a Transgenic Sheep Model of Huntington's Disease by Edith L. Pfister, Natalie DiNardo, Erica Mondo, Florie Borel, Faith Conroy, Cara K. Fraser, Gwladys Gernoux, Xin Han, Danjing Hu, Emily Johnson, Lori Kennington, Pengpeng Liu, Suzanne J. Reid, Ellen Sapp, Petr Vodička, Tim Kuchel, A. Jennifer Morton, David Howland, Richard P. Moser, Miguel Sena‐Esteves, Guangping Gao, Christian Mueller, Marian DiFiglia, Neil Aronin
Published 2017Artigo -
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A divalent siRNA chemical scaffold for potent and sustained modulation of gene expression throughout the central nervous system by Julia F. Alterman, Bruno M.D.C. Godinho, Matthew Hassler, Chantal Ferguson, Dimas Echeverria, Ellen Sapp, Reka A. Haraszti, Andrew H. Coles, Faith Conroy, Rachael Miller, Loïc Roux, Paul Yan, Emily G. Knox, Anton A. Turanov, R King, Gwladys Gernoux, Christian Mueller, Heather L. Gray‐Edwards, Richard P. Moser, Nina Bishop, Samer M. Jaber, Matthew J. Gounis, Miguel Sena‐Esteves, Athma A. Pai, Marian DiFiglia, Neil Aronin, Anastasia Khvorova
Published 2019Artigo
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Biology
Disease
Gene
Gene silencing
Genetics
Medicine
Huntingtin
Huntington's disease
Internal medicine
Molecular biology
Mutant
RNA
RNA interference
Small interfering RNA
Allele
Cell biology
Dopamine
Gene expression
Genetically modified mouse
Huntingtin Protein
Immunohistochemistry
Immunology
NeuN
Neuroscience
Pathology
RNA silencing
Striatum
Trans-acting siRNA
Transgene