Αποτελέσματα αναζήτησης - David Jacoby
- Εμφανίζονται 1 - 5 Αποτελέσματα από 5
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Study of Intraventricular Cerliponase Alfa for CLN2 Disease από Angela Schulz, Temitayo Ajayi, Nicola Specchio, Emily de los Reyes, Paul Gissen, Douglas Ballon, Jonathan P. Dyke, Heather Cahan, Peter Slasor, David Jacoby, Alfried Kohlschütter
Έκδοση 2018Artigo -
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Regulatory strategies for rare diseases under current global regulatory statutes: a discussion with stakeholders από Andrew E. Mulberg, Christina Bucci‐Rechtweg, Joseph Giuliano, David Jacoby, Franklin K. Johnson, Qing Liu, Deborah Marsden, Scott McGoohan, Robert M. Nelson, Nita Patel, Klaus Romero, Vikram Sinha, Sheela Sitaraman, John Spaltro, Vivian Kessler
Έκδοση 2019Artigo -
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Disease characteristics and progression in patients with late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease: an observational cohort study από Miriam Nickel, Alessandro Simonati, David Jacoby, Susanne Lezius, Dirk Kilian, Benjamin Van de Graaf, Odelya E. Pagovich, Barry E. Kosofsky, Kaleb Yohay, Matthew Downs, Peter Slasor, Temitayo Ajayi, Ronald G. Crystal, Alfried Kohlschütter, Dolan Sondhi, Angela Schulz
Έκδοση 2018Artigo
Εργαλεία αναζήτησης:
Σχετικά θέματα
Biology
Biochemistry
Disease
Gene
Medicine
Internal medicine
Recombinant DNA
Aggression
Amplicon
Batten disease
Bioinformatics
Biopharmaceutical
Biotechnology
Cell culture
Clinical Dementia Rating
Clinical trial
Cognition
Cohort
Cohort study
Computer science
Dementia
Dominance (genetics)
Dominance hierarchy
Drug
Drug development
Ecology
Enzyme replacement therapy
Gene expression
Genetic enhancement
Genetics