نتائج البحث - Catherine Douthwright
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<i>SOD1</i>Suppression with Adeno-Associated Virus and MicroRNA in Familial ALS حسب Christian Mueller, James Berry, Diane McKenna‐Yasek, Gwladys Gernoux, Margaret Owegi, Lindsay Pothier, Catherine Douthwright, Dario Gelevski, Sarah Luppino, Meghan Blackwood, Nicholas Wightman, Derek H. Oakley, Matthew P. Frosch, Terence R. Flotte, Merit Cudkowicz, Robert H. Brown
منشور في 2020Artigo -
2
Poly(GR) and poly(GA) in cerebrospinal fluid as potential biomarkers for C9ORF72-ALS/FTD حسب Gopinath Krishnan, Denitza Raitcheva, Daniel A. Bartlett, Mercedes Prudencio, Diane McKenna‐Yasek, Catherine Douthwright, Björn Oskarsson, Shafeeq Ladha, Oliver D. King, Sami J. Barmada, Timothy M. Miller, Robert Bowser, Jonathan K. Watts, Leonard Petrucelli, Robert H. Brown, Mark W. Kankel, Fen‐Biao Gao
منشور في 2022Artigo -
3
Suppression of mutant C9orf72 expression by a potent mixed backbone antisense oligonucleotide حسب Hélène Tran, Michael P. Moazami, Huiya Yang, Diane McKenna‐Yasek, Catherine Douthwright, Courtney Pinto, Jake Metterville, Minwook Shin, Nitasha Sanil, Craig Dooley, Ajit S Puri, Alexandra Weiss, Nicholas Wightman, Heather L. Gray‐Edwards, Miklós Marosföi, R King, Thomas Kenderdine, Daniele Fabris, Robert Bowser, Jonathan K. Watts, Robert H. Brown
منشور في 2021Artigo -
4
Prospective natural history study of <i>C9orf72</i> ALS clinical characteristics and biomarkers حسب Alexander J. Cammack, Nazem Atassi, Theodore Hyman, Leonard H. van den Berg, Matthew B. Harms, Robert H. Baloh, Robert H. Brown, Michael A. van Es, Jan H. Veldink, Bálint S. de Vries, Jeffrey D. Rothstein, Caroline Drain, Jennifer Jockel‐Balsarotti, Amber Malcolm, Sonia Boodram, Amber Salter, Nicholas Wightman, Hong Yu, Alexander Sherman, Thomas J. Esparza, Diane McKenna‐Yasek, Margaret Owegi, Catherine Douthwright, Alexander McCampbell, Toby A. Ferguson, Carlos Cruchaga, Merit Cudkowicz, Timothy M. Miller
منشور في 2019Artigo -
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AAV gene therapy for Tay-Sachs disease حسب Terence R. Flotte, Oğuz Çataltepe, Ajit S Puri, Ana Rita Batista, Richard P. Moser, Diane McKenna‐Yasek, Catherine Douthwright, Gwladys Gernoux, Meghan Blackwood, Christian Mueller, Phillip W.L. Tai, Xuntian Jiang, Scot T. Bateman, Spiro G. Spanakis, Julia Parzych, Allison M. Keeler, Aly Abayazeed, Saurabh Rohatgi, Laura Gibson, Robert W. Finberg, Bruce Barton, Zeynep Vardar, Mohammed Salman Shazeeb, Matthew J. Gounis, Cynthia J. Tifft, Florian Eichler, Robert H. Brown, Douglas R. Martin, Heather L. Gray‐Edwards, Miguel Sena‐Esteves
منشور في 2022Artigo
أدوات البحث:
موضوعات ذات صلة
Biology
C9orf72
Disease
Gene
Internal medicine
Medicine
Chemistry
Dementia
Frontotemporal dementia
Genetics
Mutant
Adeno-associated virus
Adverse effect
Allele
Biochemistry
Cell biology
Cerebrospinal fluid
Clinical endpoint
Clinical trial
Computational biology
Computer science
Expression (computer science)
Gastroenterology
Genetic enhancement
HEXA
Molecular biology
Natural history
Natural history study
Oligonucleotide
Pediatrics