Rezultaty - Astrid Vallès
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AAV5-miHTT Gene Therapy Demonstrates Sustained Huntingtin Lowering and Functional Improvement in Huntington Disease Mouse Models od Elisabeth A. Spronck, Cynthia Brouwers, Astrid Vallès, Martin de Haan, Harald Petry, S J van Deventer, Pavlina Konstantinova, Melvin M. Evers
Wydane 2019Artigo -
3
AAV5-miHTT Lowers Huntingtin mRNA and Protein without Off-Target Effects in Patient-Derived Neuronal Cultures and Astrocytes od Sonay Keskin, Cynthia Brouwers, Marina Sogorb-González, Raygene Martier, Josse A. Depla, Astrid Vallès, S J van Deventer, Pavlina Konstantinova, Melvin M. Evers
Wydane 2019Artigo -
4
Interneuron hypomyelination is associated with cognitive inflexibility in a rat model of schizophrenia od Dorien A. Maas, Vivian D. Eijsink, Marcia Spoelder, Josephus A. van Hulten, Peter De Weerd, Judith R. Homberg, Astrid Vallès, Brahim Nait‐Oumesmar, Gerard J.M. Martens
Wydane 2020Artigo -
5
Exon 1-targeting miRNA reduces the pathogenic exon 1 HTT protein in Huntington disease models od Marina Sogorb-González, Christian Landles, Nicholas S. Caron, Anouk Stam, Georgina F Osborne, Michael R. Hayden, David Howland, Sander van Deventer, Gillian P. Bates, Astrid Vallès, Melvin M. Evers
Wydane 2024Artigo -
6
Intrastriatal Administration of AAV5-miHTT in Non-Human Primates and Rats Is Well Tolerated and Results in miHTT Transgene Expression in Key Areas of Huntington Disease Pathology od Elisabeth A. Spronck, Astrid Vallès, Margit H. Lampen, Paula S. Montenegro-Miranda, Sonay Keskin, Liesbeth Heijink, Melvin M. Evers, Harald Petry, S. J. H. Van Deventer, Pavlina Konstantinova, Martin de Haan
Wydane 2021Artigo -
7
White matter structure and myelin-related gene expression alterations with experience in adult rats od Cassandra Sampaio‐Baptista, Astrid Vallès, Alexandre A. Khrapitchev, Guus Akkermans, Anderson M. Winkler, Sean Foxley, Nicola R. Sibson, Mark Roberts, Karla L. Miller, Mathew E. Diamond, Gerard J.M. Martens, Peter De Weerd, Heidi Johansen‐Berg
Wydane 2020Artigo -
8
AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model od Melvin M. Evers, Jana Miniarikova, Štefan Juhás, Astrid Vallès, Božena Bohuslavová, Jana Juhásová, Helena Kupcová Skalníková, Petr Vodička, Ivona Valeková, Cynthia Brouwers, Bas Blits, Jacek Lubelski, Hana Kovářová, Zdeňka Ellederová, S J van Deventer, Harald Petry, Jan Motlík, Pavlina Konstantinova
Wydane 2018Artigo -
9
Chromosome 1p21.3 microdeletions comprising DPYD and MIR137 are associated with intellectual disability od Marjolein H. Willemsen, Astrid Vallès, Laurens A. M. H. Kirkels, Mathilde Mastebroek, Nikkie Olde Loohuis, Aron Kos, W.M. Wissink-Lindhout, Arjan P.M. de Brouwer, Willy M. Nillesen, Rolph Pfundt, Muriel Holder‐Espinasse, Louis Vallée, Joris Andrieux, Marjolein C. Coppens‐Hofman, Hanneke Rensen, Ben C.J. Hamel, Hans van Bokhoven, Armaz Aschrafi, Tjitske Kleefstra
Wydane 2011Artigo
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