Résultats de la recherche - Astrid Vallès
- Résultat(s) 1 - 9 résultats de 9
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AAV5-miHTT Gene Therapy Demonstrates Sustained Huntingtin Lowering and Functional Improvement in Huntington Disease Mouse Models par Elisabeth A. Spronck, Cynthia Brouwers, Astrid Vallès, Martin de Haan, Harald Petry, S J van Deventer, Pavlina Konstantinova, Melvin M. Evers
Publié 2019Artigo -
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AAV5-miHTT Lowers Huntingtin mRNA and Protein without Off-Target Effects in Patient-Derived Neuronal Cultures and Astrocytes par Sonay Keskin, Cynthia Brouwers, Marina Sogorb-González, Raygene Martier, Josse A. Depla, Astrid Vallès, S J van Deventer, Pavlina Konstantinova, Melvin M. Evers
Publié 2019Artigo -
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Interneuron hypomyelination is associated with cognitive inflexibility in a rat model of schizophrenia par Dorien A. Maas, Vivian D. Eijsink, Marcia Spoelder, Josephus A. van Hulten, Peter De Weerd, Judith R. Homberg, Astrid Vallès, Brahim Nait‐Oumesmar, Gerard J.M. Martens
Publié 2020Artigo -
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Exon 1-targeting miRNA reduces the pathogenic exon 1 HTT protein in Huntington disease models par Marina Sogorb-González, Christian Landles, Nicholas S. Caron, Anouk Stam, Georgina F Osborne, Michael R. Hayden, David Howland, Sander van Deventer, Gillian P. Bates, Astrid Vallès, Melvin M. Evers
Publié 2024Artigo -
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Intrastriatal Administration of AAV5-miHTT in Non-Human Primates and Rats Is Well Tolerated and Results in miHTT Transgene Expression in Key Areas of Huntington Disease Pathology par Elisabeth A. Spronck, Astrid Vallès, Margit H. Lampen, Paula S. Montenegro-Miranda, Sonay Keskin, Liesbeth Heijink, Melvin M. Evers, Harald Petry, S. J. H. Van Deventer, Pavlina Konstantinova, Martin de Haan
Publié 2021Artigo -
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White matter structure and myelin-related gene expression alterations with experience in adult rats par Cassandra Sampaio‐Baptista, Astrid Vallès, Alexandre A. Khrapitchev, Guus Akkermans, Anderson M. Winkler, Sean Foxley, Nicola R. Sibson, Mark Roberts, Karla L. Miller, Mathew E. Diamond, Gerard J.M. Martens, Peter De Weerd, Heidi Johansen‐Berg
Publié 2020Artigo -
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AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model par Melvin M. Evers, Jana Miniarikova, Štefan Juhás, Astrid Vallès, Božena Bohuslavová, Jana Juhásová, Helena Kupcová Skalníková, Petr Vodička, Ivona Valeková, Cynthia Brouwers, Bas Blits, Jacek Lubelski, Hana Kovářová, Zdeňka Ellederová, S J van Deventer, Harald Petry, Jan Motlík, Pavlina Konstantinova
Publié 2018Artigo -
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Chromosome 1p21.3 microdeletions comprising DPYD and MIR137 are associated with intellectual disability par Marjolein H. Willemsen, Astrid Vallès, Laurens A. M. H. Kirkels, Mathilde Mastebroek, Nikkie Olde Loohuis, Aron Kos, W.M. Wissink-Lindhout, Arjan P.M. de Brouwer, Willy M. Nillesen, Rolph Pfundt, Muriel Holder‐Espinasse, Louis Vallée, Joris Andrieux, Marjolein C. Coppens‐Hofman, Hanneke Rensen, Ben C.J. Hamel, Hans van Bokhoven, Armaz Aschrafi, Tjitske Kleefstra
Publié 2011Artigo
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Sujets similaires
Biology
Gene
Medicine
Neuroscience
Genetics
Huntingtin
Disease
Huntington's disease
Internal medicine
Central nervous system
Myelin
Biochemistry
Cognition
Dopamine
Magnetic resonance imaging
Mutant
Pathology
Pharmacology
Prefrontal cortex
Psychiatry
Psychology
Radiology
Schizophrenia (object-oriented programming)
Striatum
Transgene
White matter
microRNA
Allele
Biotechnology
Cell biology