检索结果 - Anouk Stam
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Exon 1-targeting miRNA reduces the pathogenic exon 1 HTT protein in Huntington disease models 由 Marina Sogorb-González, Christian Landles, Nicholas S. Caron, Anouk Stam, Georgina F Osborne, Michael R. Hayden, David Howland, Sander van Deventer, Gillian P. Bates, Astrid Vallès, Melvin M. Evers
出版 2024Artigo