Rezultati - Anne‐Marie Douar
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Intravenous Administration of Self-complementary AAV9 Enables Transgene Delivery to Adult Motor Neurons od Sandra Duqué, Béatrice Joussemet, Christel Rivière, Thibaut Marais, Laurence Dubreil, Anne‐Marie Douar, John C. Fyfe, Philippe Moullier, M.A. Colle, Martine Barkats
Izdano 2009Artigo -
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AAV-mediated intramuscular delivery of myotubularin corrects the myotubular myopathy phenotype in targeted murine muscle and suggests a function in plasma membrane homeostasis od Anna Buj‐Bello, Françoise Fougerousse, Yannick Schwab, Nadia Messaddeq, Danièle Spehner, Christopher R. Pierson, Muriel Durand, Christine Kretz, Olivier Danos, Anne‐Marie Douar, Alan H. Beggs, Patrick Schultz, Marie Montus, Patrice Denèfle, Jean‐Louis Mandel
Izdano 2008Artigo
Iskalna orodja:
Sorodne teme
Biology
Gene
Biochemistry
Cell biology
Gene delivery
Genetics
Medicine
Recombinant DNA
Transduction (biophysics)
Adeno-associated virus
Biotechnology
Brefeldin A
Cell culture
Central nervous system
Endocrinology
Endoplasmic reticulum
Endosome
Gene expression
Genetic enhancement
Golgi apparatus
Immunology
In vivo
Internal medicine
Internalization
Intracellular
Motor neuron
Muscle disorder
Myocyte
Myopathy
Neuroscience