檢索結果 - Andrea Frassetto
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Risk Factors for Peri-Implantitis: Effect of History of Periodontal Disease and Smoking Habits. A Systematic Review and Meta-Analysis 由 Claudio Stacchi, Federico Berton, Giuseppe Perinetti, Andrea Frassetto, Teresa Lombardi, Aiman Khoury, Francesca Andolsek, Roberto Di Lenarda
出版 2016Revisão -
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Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia 由 An Ding, Andrea Frassetto, Eric Jacquinet, Marianne Eybye, Joseph Milano, Christine DeAntonis, Vi Nguyen, Rodrigo Laureano, Jaclyn Milton, Staci Sabnis, Christine Lukacs, Lin T. Guey
出版 2019Artigo -
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Butyrate and Propionate Protect against Diet-Induced Obesity and Regulate Gut Hormones via Free Fatty Acid Receptor 3-Independent Mechanisms 由 Hua Lin, Andrea Frassetto, Edward J. Kowalik, Andrea R. Nawrocki, Mofei M. Lu, Jennifer Kosinski, James Hubert, Daphne Szeto, Xiaorui Yao, Gail Forrest, Donald J. Marsh
出版 2012Artigo -
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Systemic modified messenger RNA for replacement therapy in alpha 1-antitrypsin deficiency 由 Ahmad Karadagi, Alex Cavedon, Helen Zemack, Greg Nowak, Marianne Eybye, Xuling Zhu, Eleonora Guadagnin, Rebecca White, Lisa Rice, Andrea Frassetto, Stephen C. Strom, Carl Jorns, Paolo G.V. Martini, Ewa Ellis
出版 2020Artigo -
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Characterizing the mechanism of action for mRNA therapeutics for the treatment of propionic acidemia, methylmalonic acidemia, and phenylketonuria 由 Rena Baek, Kimberly A. Coughlan, Lei Jiang, M. Liang, Lei Ci, Harkewal Singh, Hannah Zhang, Neeraj Kaushal, Ivana L. Rajlic, Linh Van, Rain Dimen, Alexander Cavedon, Ling Yin, Lisa Rice, Andrea Frassetto, Lin T. Guey, Patrick F. Finn, Paolo G.V. Martini
出版 2024Artigo -
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Systemic mRNA Therapy for the Treatment of Fabry Disease: Preclinical Studies in Wild-Type Mice, Fabry Mouse Model, and Wild-Type Non-human Primates 由 Xuling Zhu, Ling Yin, Matt Theisen, Jenny Zhuo, Summar Siddiqui, Becca R. Levy, Vladimir Presnyak, Andrea Frassetto, Jaclyn Milton, Timothy Salerno, Kerry E. Benenato, Joe Milano, Andy Lynn, Staci Sabnis, Kristine Burke, Gilles Besin, Christine Lukacs, Lin T. Guey, Patrick F. Finn, Paolo G.V. Martini
出版 2019Artigo -
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Dual mRNA therapy restores metabolic function in long-term studies in mice with propionic acidemia 由 Lei Jiang, Ji-Sun Park, Ling Yin, Rodrigo Laureano, Eric Jacquinet, Jin‐Song Yang, Shi Liang, Andrea Frassetto, Jenny Zhuo, Xinhua Yan, Xuling Zhu, Steven Fortucci, Kara M. Hoar, Cosmin Mihai, Christopher Tunkey, Vladimir Presnyak, Kerry E. Benenato, Christine Lukacs, Paolo G.V. Martini, Lin T. Guey
出版 2020Artigo -
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Synthetic human ABCB4 mRNA therapy rescues severe liver disease phenotype in a BALB/c.Abcb4 mouse model of PFIC3 由 Guangyan Wei, Jingsong Cao, Pinzhu Huang, Ping An, Disha Badlani, Kahini A. Vaid, Shuangshuang Zhao, David Q.‐H. Wang, Jenny Zhuo, Ling Yin, Andrea Frassetto, Arianna Markel, Vladimir Presnyak, Srujan Gandham, Serenus Hua, Christine Lukacs, Patrick F. Finn, Paloma H. Giangrande, Paolo G.V. Martini, Yury Popov
出版 2020Artigo -
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Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia 由 An Ding, Jessica L. Schneller, Andrea Frassetto, Shi Liang, Xuling Zhu, Ji-Sun Park, Matt Theisen, Sue‐Jean Hong, Jenny Zhou, Raj Rajendran, Becca R. Levy, Rebecca Howell, Gilles Besin, Vladimir Presnyak, Staci Sabnis, Kerry E. Murphy-Benenato, E. Sathyajith Kumarasinghe, Timothy Salerno, Cosmin Mihai, Christine Lukacs, Randy J. Chandler, Lin T. Guey, Charles P. Venditti, Paolo G.V. Martini
出版 2017Artigo -
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mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency 由 Jingsong Cao, An Ding, Mikel Galduroz, Jenny Zhuo, Shi Liang, Marianne Eybye, Andrea Frassetto, Eishi Kuroda, Aki Funahashi, Jordan Santana, Cosmin Mihai, Kerry E. Benenato, E. Sathyajith Kumarasinghe, Staci Sabnis, Timothy Salerno, Kimberly A. Coughlan, Edward J. Miracco, Becca R. Levy, Gilles Besin, Joshua R. Schultz, Christine Lukacs, Lin T. Guey, Patrick F. Finn, Tatsuhiko Furukawa, Paloma H. Giangrande, Takeyori Saheki, Paolo G.V. Martini
出版 2019Artigo -
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mRNA therapy corrects defective glutathione metabolism and restores ureagenesis in preclinical argininosuccinic aciduria 由 Sonam Gurung, Oskar Vilhelmsson Timmermand, Dany Perocheau, Ana Luisa Gil-Martínez, Magdalena Minnion, Loukia Touramanidou, Sherry Fang, Martina Messina, Youssef Khalil, Justyna Śpiewak, Abigail R. Barber, Richard S. Edwards, Patrícia Pinto, Patrick F. Finn, Alex Cavedon, Summar Siddiqui, Lisa Rice, Paolo G.V. Martini, Deborah Ridout, Wendy Heywood, I. Hargreaves, Simon Heales, Philippa B. Mills, Simon N. Waddington, Paul Gissen, Simon Eaton, Mina Ryten, Martin Feelisch, Andrea Frassetto, Timothy H. Witney, Julien Baruteau
出版 2024Artigo -
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mRNA therapy restores euglycemia and prevents liver tumors in murine model of glycogen storage disease 由 Jingsong Cao, Minjung Choi, Eleonora Guadagnin, Maud Soty, Marine Silva, Vincent Verzieux, Edward Weisser, Arianna Markel, Jenny Zhuo, Shi Liang, Ling Yin, Andrea Frassetto, Anne-Renee Graham, Kristine Burke, Tatiana Ketova, Cosmin Mihai, Zach Zalinger, Becca R. Levy, Gilles Besin, Meredith Wolfrom, Barbara Tran, Christopher Tunkey, Erik Owen, Joe Sarkis, Athanasios Dousis, Vladimir Presnyak, Christopher S. Pepin, Wei Zheng, Lei Ci, Marjie Hard, Edward J. Miracco, Lisa Rice, Vi Nguyen, Mike Zimmer, Uma Karthika Rajarajacholan, Patrick F. Finn, Gilles Mithieux, Fabienne Rajas, Paolo G.V. Martini, Paloma H. Giangrande
出版 2021Artigo
相關主題
Medicine
Internal medicine
Biology
Biochemistry
Endocrinology
Gene
Messenger RNA
Chemistry
Disease
Enzyme
Enzyme replacement therapy
Genetic enhancement
Methylmalonic acidemia
Pharmacology
Cancer research
Dentistry
Fabry disease
Genetics
Hormone
Hyperammonemia
Immunology
Liver disease
Pathology
Propionic acidemia
Transplantation
Adhesive
Adverse effect
Alpha (finance)
Alpha 1-antitrypsin deficiency
Alpha-galactosidase