检索结果 - Amit Nathwani
- Showing 1 - 16 results of 16
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An ROR1 bi-specific T-cell engager provides effective targeting and cytotoxicity against a range of solid tumors 由 Satyen H. Gohil, Solange Rosa Paredes-Moscosso, Micaela Harrasser, Marzia Vezzalini, Aldo Scarpa, Emma Morris, Andrew M. Davidoff, Claudio Sorio, Amit Nathwani, Marco Della Peruta
出版 2017Artigo -
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Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV... 由 Mei Hong Tan, Alexander J. Smith, Basil S. Pawlyk, Xiaoyun Xu, Xiaoqing Liu, James Bainbridge, Mark Basche, Jenny McIntosh, Hoai Viet Tran, Amit Nathwani, Tiansen Li, Robin R. Ali
出版 2009Artigo -
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The Transcription Factor ZNF683/HOBIT Regulates Human NK-Cell Development 由 Mirte Post, Angélica Cuapio, Markus Osl, Dorit Lehmann, Ulrike Resch, David M. Davies, Martin Bilban, Bernhard Schlechta, Wolfgang Eppel, Amit Nathwani, Dagmar Stoiber, Jan Spanholtz, Emilio Casanova, Erhard Hofer
出版 2017Artigo -
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Improved Intratumoral Oxygenation Through Vascular Normalization Increases Glioma Sensitivity to Ionizing Radiation 由 Mackenzie McGee, John B. Hamner, Regan F. Williams, Shannon F. Rosati, Thomas L. Sims, Catherine Y. Ng, M. Waleed Gaber, Christopher Calabrese, Jianrong Wu, Amit Nathwani, Christopher Duntsch, Thomas E. Merchant, Andrew M. Davidoff
出版 2010Artigo -
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Rituximab Plus Chlorambucil As First-Line Treatment for Chronic Lymphocytic Leukemia: Final Analysis of an Open-Label Phase II Study 由 Peter Hillmen, John G. Gribben, George Follows, Donald Milligan, Hazem A. Sayala, Paul Moreton, David Oscier, Claire Dearden, Daniel B. Kennedy, Andrew R. Pettitt, Amit Nathwani, Abraham Varghese, D. Cohen, Andy C. Rawstron, Stephan Oertel, Christopher Pocock
出版 2014Artigo -
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Preclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry disease 由 Jey M Jeyakumar, Azadeh Kia, Lawrence C. S. Tam, Jenny McIntosh, Justyna Śpiewak, Kevin Mills, Wendy Heywood, Elisa Chisari, Noemi Castaldo, Daniël Verhoef, Paniz Hosseini, Petya Kalcheva, Clément Cocita, Carlos J. Miranda, Miriam Canavese, Jaminder Khinder, Cecilia Rosales, Derralynn Hughes, Rose Sheridan, Romuald Corbau, Amit Nathwani
出版 2023Artigo -
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Adeno-associated virus gene therapy prevents progression of kidney disease in genetic models of nephrotic syndrome 由 Wen Y. Ding, Valeryia Kuzmuk, Sarah Hunter, Abigail C. Lay, Bryony Hayes, Matthew Beesley, Ruth Rollason, Jenny Hurcombe, Fern Barrington, Catrin Masson, William Cathery, Carl May, Jack Tuffin, Timothy K. Roberts, Géraldine Mollet, Colin J. Chu, Jenny McIntosh, Richard J. Coward, Corinne Antignac, Amit Nathwani, Gavin I. Welsh, Moin A. Saleem
出版 2023Artigo -
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Targeting Histone Demethylases in MYC-Driven Neuroblastomas with Ciclopirox 由 Jun Yang, Sandra Milasta, Dongli Hu, Alaa Altahan, Rodrigo B. Interiano, Junfang Zhou, Jesse T. Davidson, Jonathan Low, Wenwei Lin, Ju Bao, Pollyanna Goh, Amit Nathwani, Ruoning Wang, Yingdi Wang, Su Sien Ong, Vincent A. Boyd, Brandon Young, Sourav Das, Anang A. Shelat, Yinan Wu, Zhenmei Li, Jie Zheng, Ashutosh Mishra, Yong Cheng, Chunxu Qu, Junmin Peng, Douglas R. Green, Stephen W. White, R. Kiplin Guy, Taosheng Chen, Andrew M. Davidoff
出版 2017Artigo -
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Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B 由 Amit Nathwani, Ulreke M. Reiss, Edward G. D. Tuddenham, Cecilia Rosales, Pratima Chowdary, Jenny McIntosh, Marco Della Peruta, Elsa Lhériteau, Nishal Patel, Deepak B. Thimiri Govinda Raj, Anne Riddell, Jun Pie, Savita Rangarajan, David Bevan, Michael Recht, Yu‐Min Shen, Kathleen G. Halka, Etiena Basner‐Tschakarjan, Federico Mingozzi, Katherine A. High, James A. Allay, Mark A. Kay, Catherine Y. Ng, Junfang Zhou, Maria Cancio, Christopher L. Morton, John T. Gray, Deo Kumar Srivastava, Arthur W. Nienhuis, Andrew M. Davidoff
出版 2014Artigo -
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A high-throughput sequencing test for diagnosing inherited bleeding, thrombotic, and platelet disorders 由 Ilenia Simeoni, Jonathan Stephens, Fengyuan Hu, Sri V. V. Deevi, Karyn Mégy, Tadbir K. Bariana, Claire Lentaigne, Sol Schulman, Suthesh Sivapalaratnam, Minka J. A. Vries, Sarah K. Westbury, Daniel Greene, Sofia Papadia, Marie‐Christine Alessi, Antony Attwood, Matthias Ballmaier, Gareth Baynam, Emilsé Bermejo, Marta Bértoli, Paul F. Bray, Loredana Bury, Marco Cattaneo, Peter Collins, Louise C. Daugherty, Rémi Favier, Deborah L. French, Bruce Furie, Michael Gattens, Manuela Germeshausen, Cédric Ghevaert, Anne Goodeve, José A. Guerrero, Daniel J. Hampshire, Daniel P. Hart, Johan W. M. Heemskerk, Yvonne Henskens, Marian Hill, Nancy Hogg, Jennifer D. Jolley, Walter H.A. Kahr, Anne M. Kelly, Ron Kerr, Myrto Kostadima, Shinji Kunishima, Michele P. Lambert, Ri Liesner, José A. López, Rutendo Mapeta, Mary Mathias, Carolyn M. Millar, Amit Nathwani, Marguerite Neerman‐Arbez, Alan T. Nurden, Paquita Nurden, Maha Othman, Kathelijne Peerlinck, David J. Perry, Pawan Poudel, Pieter H. Reitsma, Matthew T. Rondina, Peter A. Smethurst, William Stevenson, Artur Szkotak, Salih Tuna, Chris Van Geet, Deborah Whitehorn, David A. Wilcox, Bin Zhang, Shoshana Revel‐Vilk, Paolo Gresele, Daniel B. Bellissimo, Christopher J. Penkett, Michael Laffan, Andrew Mumford, Augusto Rendon, Keith Gomez, Kathleen Freson, Willem H. Ouwehand, Ernest Turro
出版 2016Artigo
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