検索結果 - Amit C. Nathwani
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Gene Therapy for Hemophilia 著者: Arthur W. Nienhuis, Amit C. Nathwani, Andrew M. Davidoff
出版事項 2017Revisão -
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Highly efficient gene transfer into cord blood nonobese diabetic/severe combined immunodeficiency repopulating cells by oncoretroviral vector particles pseudotyped with the feline... 著者: Patrick Kelly, Jody Vandergriff, Amit C. Nathwani, Arthur W. Nienhuis, Elio F. Vanin
出版事項 2000Artigo -
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Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhu... 著者: Andrew M. Davidoff, John T. Gray, Catherine Y. Ng, Youbin Zhang, Junfang Zhou, Yunyu Spence, Yusura Bakar, Amit C. Nathwani
出版事項 2005Artigo -
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Comparison of Various Envelope Proteins for Their Ability to Pseudotype Lentiviral Vectors and Transduce Primitive Hematopoietic Cells from Human Blood 著者: Hideki Hanawa, Patrick Kelly, Amit C. Nathwani, Derek A. Persons, Jody Vandergriff, Phillip W. Hargrove, Elio F. Vanin, Arthur W. Nienhuis
出版事項 2002Artigo -
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Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman prima... 著者: Amit C. Nathwani, John T. Gray, Jenny McIntosh, Catherine Y. Ng, Junfang Zhou, Yunyu Spence, Melanie Cochrane, Elaine Gray, Edward G. D. Tuddenham, Andrew M. Davidoff
出版事項 2006Artigo -
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Good Manufacturing Practice Production of Self-Complementary Serotype 8 Adeno-Associated Viral Vector for a Hemophilia B Clinical Trial 著者: James A. Allay, Susan Sleep, Scott Long, David M. Tillman, Rob Clark, Gael Carney, Paolo Fagone, Jenny H. McIntosh, Arthur W. Nienhuis, Andrew M. Davidoff, Amit C. Nathwani, John T. Gray
出版事項 2011Artigo -
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Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman... 著者: Amit C. Nathwani, John T. Gray, Catherine Y. Ng, Junfang Zhou, Yunyu Spence, Simon N. Waddington, Edward G. D. Tuddenham, Geoffrey Kemball‐Cook, Jenny McIntosh, Mariëtte Boon‐Spijker, Koen Mertens, Andrew M. Davidoff
出版事項 2005Artigo -
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Codon optimization of human factor VIII cDNAs leads to high-level expression 著者: Natalie J Ward, Suzanne M. K. Buckley, Simon N. Waddington, Thierry VandenDriessche, Marinee Chuah, Amit C. Nathwani, Jenny McIntosh, Edward G. D. Tuddenham, Christine Kinnon, Adrian J. Thrasher, John H. McVey
出版事項 2010Artigo -
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In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model 著者: Citra Nurfarah Zaini Mattar, Irene Gil-Fariña, Cecilia Rosales, Nuryanti Johana, Yvonne Tan, Jenny McIntosh, Christine Kaeppel, Simon N. Waddington, Arijit Biswas, Mahesh Choolani, Manfred Schmidt, Amit C. Nathwani, Jerry Kok Yen Chan
出版事項 2017Artigo -
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The cost-effectiveness of gene therapy for severe hemophilia B: a microsimulation study from the United States perspective 著者: Nancy S. Bolous, Yichen Chen, Huiqi Wang, Andrew M. Davidoff, Meenakshi Devidas, Timothy W. Jacobs, Michael M. Meagher, Amit C. Nathwani, Ellis J. Neufeld, Bryan A. Piras, Carlos Rodríguez‐Galindo, Ulrike M. Reiss, Nickhill Bhakta
出版事項 2021Artigo -
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Sustained high-level expression of human factor IX (hFIX) after liver-targeted delivery of recombinant adeno-associated virus encoding the hFIX gene in rhesus macaques 著者: Amit C. Nathwani, Andrew M. Davidoff, Hideki Hanawa, Yunyu Hu, Fredric A. Hoffer, Alexander Y. Nikanorov, Clive A. Slaughter, Catherine Y. Ng, Junfang Zhou, Jay N. Lozier, Timothy D. Mandrell, Elio F. Vanin, Arthur W. Nienhuis
出版事項 2002Artigo -
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GO-8: Preliminary Results of a Phase I/II Dose Escalation Trial of Gene Therapy for Haemophilia a Using a Novel Human Factor VIII Variant 著者: Amit C. Nathwani, Edward G. D. Tuddenham, Pratima Chowdary, Jenny McIntosh, Doyoung Lee, Cecilia Rosales, Mark Phillips, Jun Pie, Junfang Zhou, Michael M. Meagher, Ulrike M. Reiss, Andrew M. Davidoff, Chris L Morton, Anne Riddell
出版事項 2018Artigo -
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The Role of Histone Demethylase KDM4B in Myc Signaling in Neuroblastoma 著者: Jun J. Yang, Alaa Altahan, Dongli Hu, Yingdi Wang, Pei-Hsin Cheng, Christopher L. Morton, Chunxu Qu, Amit C. Nathwani, Jason M. Shohet, Theodore Fotsis, Jan Köster, Rogier Versteeg, Hitoshi Okada, Adrian L. Harris, Andrew M. Davidoff
出版事項 2015Artigo -
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Phase 1–2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B 著者: Pratima Chowdary, Susan Shapiro, Michael Makris, Gillian Evans, Sara Boyce, Kate Talks, Gerard Dolan, Ulrike M. Reiss, Mark Phillips, Anne Riddell, Maria R. Peralta, Michelle Quaye, David Patch, Edward G. D. Tuddenham, Allison Dane, Marie Watissée, Alison Long, Amit C. Nathwani
出版事項 2022Artigo
関連主題
Biology
Gene
Genetics
Recombinant DNA
Genetic enhancement
Vector (molecular biology)
Virology
Adeno-associated virus
Immunology
Medicine
Factor IX
Viral vector
Biochemistry
Internal medicine
Molecular biology
Transgene
Virus
Transduction (biophysics)
Antibody
Capsid
Cell biology
Asymptomatic
Fetus
Genome
Immune system
In vivo
Pregnancy
Adenoviridae
Bioinformatics
CD34