Search Results - Alexander P. Murphy

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  1. 1
    The Classification, Natural History and Treatment of the Limb Girdle Muscular Dystrophies

    The Classification, Natural History and Treatment of the Limb Girdle Muscular Dystrophies by Alexander P. Murphy, Volker Straub

    Published 2015
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  2. 2
    Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy

    Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy by Jerry R. Mendell, Crystal M. Proud, Craig M. Zaidman, Stefanie Mason, Eddie Darton, Shufang Wang, Christoph Wandel, Alexander P. Murphy, Eugenio Mercuri, Francesco Muntoni, Craig M. McDonald

    Published 2024
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  3. 3
    Immunologic investigations into transgene directed immune-mediated myositis following delandistrogene moxeparvovec gene therapy

    Immunologic investigations into transgene directed immune-mediated myositis following delandistrogene moxeparvovec gene therapy by Rachael A. Potter, Ida Moeller, Sohrab Khan, Hélène Haegel, Andreas Hollenstein, Guido Steiner, Christoph Wandel, Alexander P. Murphy, Damon R. Asher, Emanuel Palatinsky, Danielle A. Griffin, Stefanie Mason, Susan T. Iannaccone, Craig M. Zaidman, Louise R. Rodino‐Klapac

    Published 2025
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  4. 4
    Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to &lt;8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study <scp>SRP</scp>‐9001‐103 (<scp>ENDEAVOR</scp>)

    Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to &lt;8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study <scp>SRP</scp>‐9001‐10... by Craig M. Zaidman, Crystal M. Proud, Craig M. McDonald, Kelly J. Lehman, Natalie L. Goedeker, Stefanie Mason, Alexander P. Murphy, Maitea Guridi, Shufang Wang, Carol Reid, Eddie Darton, Christoph Wandel, Sarah Lewis, Jyoti Malhotra, Danielle A. Griffin, Rachael A. Potter, L. Rodino-Klapac, Jerry R. Mendell

    Published 2023
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  5. 5
    229th ENMC international workshop: Limb girdle muscular dystrophies – Nomenclature and reformed classification Naarden, the Netherlands, 17–19 March 2017

    229th ENMC international workshop: Limb girdle muscular dystrophies – Nomenclature and reformed classification Naarden, the Netherlands, 17–19 March 2017 by Volker Straub, Alexander P. Murphy, Bjarne Udd, C. Angelini, Ségolène Aymé, Carsten Bönneman, Marjolein Visser, Ada Hamosh, Laura Jacobs, Nina Khizanishvili, Madelon Kroneman, Pascal Laflorêt, A. St. J. Murphy, Vincenzo Nigro, Laura Rufibach, Anna Sárközy, Shaun Swanepoel, Ivan Torrente, Bjarne Udd, Andoni Urtizberea, John Vissing, Maggie C. Walter

    Published 2018
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  6. 6
    AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial

    AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial by Jerry R. Mendell, Francesco Muntoni, Craig M. McDonald, Eugenio Mercuri, Emma Ciafaloni, Hirofumi Komaki, Carmen Leon‐Astudillo, A. Nascimento, Crystal M. Proud, Ulrike Schara‐Schmidt, Aravindhan Veerapandiyan, Craig M. Zaidman, Maitea Guridi, Alexander P. Murphy, Carol Reid, Christoph Wandel, Damon R. Asher, Eddie Darton, Stefanie Mason, Rachael A. Potter, Teji Singh, Wenfei Zhang, Paulo Fontoura, Jacob Elkins, Louise R. Rodino‐Klapac

    Published 2024
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