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  1. 1
    Achromatopsia

    Achromatopsia by Meredith H. Remmer, Neelesh Rastogi, Milan P. Ranka, Emily Ceisler

    Published 2015
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  2. 2
    Production of lentiviral vectors

    Production of lentiviral vectors by Otto-Wilhelm Merten, Matthias Hebben, Chiara Bovolenta

    Published 2016
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  3. 3
    Adenovirus Strategies for Tissue-Specific Targeting

    Adenovirus Strategies for Tissue-Specific Targeting by Matthew S. Beatty, David T. Curiel

    Published 2012
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  4. 4
    Development of Patient-specific AAV Vectors After Neutralizing Antibody Selection for Enhanced Muscle Gene Transfer

    Development of Patient-specific AAV Vectors After Neutralizing Antibody Selection for Enhanced Muscle Gene Transfer by Chengwen Li, Shuqing Wu, Blake H. Albright, Matthew Hirsch, Wuping Li, Yu-Shan Tseng, Mavis Agbandje‐McKenna, Scott McPhee, Aravind Asokan, R. Jude Samulski

    Published 2015
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  5. 5
    Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1

    Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1 by Fabien Touzot, Despina Moshous, Rita Creidy, Bénédicte Neven, Pierre Frange, Guilhem Cros, Laure Caccavelli, Johanna Blondeau, Alessandra Magnani, Jean-Marc Luby, Brigitte Ternaux, Capucine Pïcard, Stéphane Blanche, Alain Fischer, Salima Hacein‐Bey‐Abina, Marina Cavazzana

    Published 2015
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  6. 6
    Fusions of Elastin-Like Polypeptides to Pharmaceutical Proteins

    Fusions of Elastin-Like Polypeptides to Pharmaceutical Proteins by Wafa Hassouneh, Sarah R. MacEwan, Ashutosh Chilkoti

    Published 2011
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  7. 7
    PEO–PPO–PEO micelles as effective rAAV-mediated gene delivery systems to target human mesenchymal stem cells without altering their differentiation potency

    PEO–PPO–PEO micelles as effective rAAV-mediated gene delivery systems to target human mesenchymal stem cells without altering their differentiation potency by Ana Rey‐Rico, Jagadeesh K. Venkatesan, Janina Frisch, M. Isabel Rial-Hermida, Gertrud Schmitt, Ángel Concheiro, Henning Madry, Carmen Alvarez‐Lorenzo, Magali Cucchiarini

    Published 2015
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  8. 8
    Gene Therapy Restores Hair Cell Stereocilia Morphology in Inner Ears of Deaf Whirler Mice

    Gene Therapy Restores Hair Cell Stereocilia Morphology in Inner Ears of Deaf Whirler Mice by Wade W. Chien, Kevin Isgrig, Soumen Roy, Inna A. Belyantseva, Meghan C. Drummond, Lindsey May, Tracy S. Fitzgerald, Thomas B. Friedman, Lisa L. Cunningham

    Published 2015
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  9. 9
    Optogenetic Control of Cardiomyocytes via Viral Delivery

    Optogenetic Control of Cardiomyocytes via Viral Delivery by Christina M. Ambrosi, Emilia Entcheva

    Published 2014
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  10. 10
    Lentiviral-mediated gene transfer into human lymphocytes: role of HIV-1 accessory proteins

    Lentiviral-mediated gene transfer into human lymphocytes: role of HIV-1 accessory proteins by Dhanalakshmi Chinnasamy, Nachimuthu Chinnasamy, Melissa J. Enriquez, Makoto Otsu, Richard A. Morgan, Fabio Candotti

    Published 2000
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  11. 11
    A Coagulation Factor IX-Deficient Mouse Model for Human Hemophilia B

    A Coagulation Factor IX-Deficient Mouse Model for Human Hemophilia B by Hui-Feng Lin, Nobuyo Maeda, Oliver Smithies, David L. Straight, Darrel W. Stafford

    Published 1997
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  12. 12
    mRNA: Fulfilling the Promise of Gene Therapy

    mRNA: Fulfilling the Promise of Gene Therapy by Drew Weissman, Katalin Karikó

    Published 2015
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    Carta
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  13. 13
    Fibronectin improves transduction of reconstituting hematopoietic stem cells by retroviral vectors: evidence of direct viral binding to chymotryptic carboxy-terminal fragments

    Fibronectin improves transduction of reconstituting hematopoietic stem cells by retroviral vectors: evidence of direct viral binding to chymotryptic carboxy-terminal fragments by Tassilo Moritz, Parmesh Dutt, Xiang Xiao, Dirk Carstanjen, Terry A. Vik, Helmut Hanenberg, DA Williams

    Published 1996
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  14. 14
    Modeling human lymphoid precursor cell gene therapy in the SCID-hu mouse

    Modeling human lymphoid precursor cell gene therapy in the SCID-hu mouse by RK Akkina, Joseph D. Rosenblatt, Andrew G. Campbell, IS Chen, JA Zack

    Published 1994
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  15. 15
    Skipping the co-expression problem: the new 2A "CHYSEL" technology.

    Skipping the co-expression problem: the new 2A "CHYSEL" technology. by Pablo de Felipe

    Published 2004
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    Editorial
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  16. 16
    The Challenge for Gene Therapy: Innate Immune Response to Adenoviruses

    The Challenge for Gene Therapy: Innate Immune Response to Adenoviruses by Bart Thaçi, Ilya V. Ulasov, Derek A. Wainwright, Maciej S. Lesniak

    Published 2011
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  17. 17
    Post-transcriptional restriction of human adenovirus expression in monkey cells

    Post-transcriptional restriction of human adenovirus expression in monkey cells by L J Eron

    Published 1975
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  18. 18
    In vivo genome editing of the albumin locus as a platform for protein replacement therapy

    In vivo genome editing of the albumin locus as a platform for protein replacement therapy by Rajiv P. Sharma, Xavier M. Anguela, Yannick Doyon, Thomas Wechsler, Russell C. DeKelver, Scott Sproul, David E. Paschon, Jeffrey C. Miller, Robert J. Davidson, David A. Shivak, Shangzhen Zhou, Julianne Rieders, Philip D. Gregory, Michael C. Holmes, Edward J. Rebar, Katherine A. High

    Published 2015
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  19. 19
    Inhibition of Human Immunodeficiency Virus-1 (HIV-1) Replication After Transduction of Granulocyte Colony-Stimulating Factor–Mobilized CD34+ Cells From HIV-1–Infected Donors Using Retroviral Vectors Containing Anti–HIV-1 Genes

    Inhibition of Human Immunodeficiency Virus-1 (HIV-1) Replication After Transduction of Granulocyte Colony-Stimulating Factor–Mobilized CD34+ Cells From HIV-1–Infected Donors Using... by Gerhard Bauer, Penelope Valdez, Karen Kearns, Ingrid Bahner, Sui Fang Wen, John A. Zaia, Donald B. Kohn

    Published 1997
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  20. 20
    A preliminary <i>in vitro</i> study into the use of IL‐1Ra gene therapy for the inhibition of intervertebral disc degeneration

    A preliminary <i>in vitro</i> study into the use of IL‐1Ra gene therapy for the inhibition of intervertebral disc degeneration by Christine L. Le Maitre, Anthony J. Freemont, Judith A. Hoyland

    Published 2006
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