Onasemnogene abeparvovec for spinal muscular atrophy: The costlier drug ever

The US Food and Drug Administration (FDA) on May 24, 2019 approved onasemnogene abeparvovec, a drug for the treatment of spinal muscular atrophy (SMA). The drug, developed by the Swiss drugmaker Novartis, has been marketed under the trade name Zolgensma. The drug has been approved to be used in chil...

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主要作者: Rajiv Mahajan
格式: Editorial
语言:英语
出版: 2019
在线阅读:https://doi.org/10.4103/ijabmr.ijabmr_190_19
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