Gene therapy for inherited retinal and optic nerve degenerations

Introduction: The eye is a target for investigational gene therapy due to the monogenic nature of many inherited retinal and optic nerve degenerations (IRD), its accessibility, tight blood-ocular barrier, the ability to non-invasively monitor for functional and anatomic outcomes, as well as its rela...

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Autors principals: Nicholas Moore, Núria Morral, Thomas A. Ciulla, Peter Bracha
Format: Revisão
Idioma:anglès
Publicat: 2017
Accés en línia:https://doi.org/10.1080/14712598.2018.1389886
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