Search Results - Vkl Hung
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1
Challenges in treating Pompe disease: an industry perspective by Vkl Hung, Richie Khanna, Russell Gotschall
Published 2019Revisão -
2
The pharmacological chaperone 1-deoxynojirimycin increases the activity and lysosomal trafficking of multiple mutant forms of acid alpha-glucosidase by John J. Flanagan, Barbara Rossi, Katherine C. Tang, Xiaoyang Wu, Kirsten Mascioli, Francesca Donaudy, Maria Rosaria Tuzzi, Federica Fontana, Maria Vittoria Cubellis, Caterina Porto, Elfrida R. Benjamin, David J. Lockhart, Kenneth J. Valenzano, Generoso Andria, Giancarlo Parenti, Vkl Hung
Published 2009Artigo -
3
Improved efficacy of a next-generation ERT in murine Pompe disease by Su Xu, Yi Lun, Michelle Frascella, Anadina Garcia, Rebecca Soska, Anju Nair, A. S. Ponery, Adriane Schilling, Jessie Feng, Steven Tuske, Maria Cecilia Della Valle, José A. Martina, Evelyn Ralston, Russell Gotschall, Kenneth J. Valenzano, Rosa Puertollano, Vkl Hung, Nina Raben, Richie Khanna
Published 2019Artigo
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