Výsledky vyhledávání - Vkl Hung
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1
Challenges in treating Pompe disease: an industry perspective Autor Vkl Hung, Richie Khanna, Russell Gotschall
Vydáno 2019Revisão -
2
The pharmacological chaperone 1-deoxynojirimycin increases the activity and lysosomal trafficking of multiple mutant forms of acid alpha-glucosidase Autor John J. Flanagan, Barbara Rossi, Katherine C. Tang, Xiaoyang Wu, Kirsten Mascioli, Francesca Donaudy, Maria Rosaria Tuzzi, Federica Fontana, Maria Vittoria Cubellis, Caterina Porto, Elfrida R. Benjamin, David J. Lockhart, Kenneth J. Valenzano, Generoso Andria, Giancarlo Parenti, Vkl Hung
Vydáno 2009Artigo -
3
Improved efficacy of a next-generation ERT in murine Pompe disease Autor Su Xu, Yi Lun, Michelle Frascella, Anadina Garcia, Rebecca Soska, Anju Nair, A. S. Ponery, Adriane Schilling, Jessie Feng, Steven Tuske, Maria Cecilia Della Valle, José A. Martina, Evelyn Ralston, Russell Gotschall, Kenneth J. Valenzano, Rosa Puertollano, Vkl Hung, Nina Raben, Richie Khanna
Vydáno 2019Artigo
Vyhledávací nástroje:
Související témata
Disease
Medicine
Biochemistry
Biology
Enzyme replacement therapy
Internal medicine
Pharmacology
Apoptosis
Autophagy
Bioinformatics
Cell biology
Chaperone (clinical)
Chemical chaperone
Chemistry
Drug
Drug development
Economics
Enzyme
Fabry disease
Gene
Glycogen
Glycogen storage disease type II
HEK 293 cells
Inefficiency
Intensive care medicine
Lysosomal storage disease
Microeconomics
Mutant
Mutant protein
Pathology