Хайлтын үр дүнгүүд - Victoria MacBean
- 3-н 1 - 3 үр дүнгүүдийг харуулж байна
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Safety and efficacy of gene replacement therapy for X-linked myotubular myopathy (ASPIRO): a multinational, open-label, dose-escalation trial -н Perry B. Shieh, Nancy L. Kuntz, James J. Dowling, Wolfgang Müller‐Felber, Carsten G. Bönnemann, A. Seferian, Laurent Servais, Barbara K. Smith, Francesco Muntoni, Astrid Blaschek, A. Reghan Foley, D. Saade, Sarah Neuhaus, Lindsay N. Alfano, Alan H. Beggs, Ana Buj‐Bello, Martin K. Childers, Tina Duong, Robert J. Graham, Minal S. Jain, Julie Coats, Victoria MacBean, Emma James, Jun Lee, Fulvio Mavilio, Weston P. Miller, Fatbardha Varfaj, Michael Murtagh, Cong Han, Mojtaba Noursalehi, Michael W. Lawlor, Suyash Prasad, Salvador Rico
Хэвлэсэн 2023Artigo
Хайх хэрэгслүүд:
Холбогдох сэдвүүд
Internal medicine
Medicine
Acoustics
Adverse effect
Alternative medicine
Anatomy
Anesthesia
Cardiology
Clinical trial
Cochrane Library
Control of respiration
Critical appraisal
Data extraction
Diaphragm (acoustics)
Dosing
Electromyography
Engineering
Hypercapnia
Intercostal muscle
Law
Loudspeaker
MEDLINE
Mechanical engineering
Meta-analysis
Muscle architecture
Parasternal line
Pathology
Pediatrics
Physical medicine and rehabilitation
Physical therapy