Søgeresultater - Stephanie Fradette
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Serious Neurologic Adverse Events in Tofersen Clinical Trials for Amyotrophic Lateral Sclerosis af Alexandra Lovett, Sowmya Chary, Suma Babu, Gaëlle Bruneteau, Jonathan D. Glass, Merete Karlsborg, Shafeeq Ladha, Keith Mayl, Christopher McDermott, Robert C. Bucelli, Adriano Chiò, Toby A. Ferguson, Thos Cochrane, Stephanie Fradette, Karen Smirnakis, Jennifer Inra, Sohail Malek, Laura Fanning
Udgivet 2025Artigo -
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Neurofilament as a potential biomarker for spinal muscular atrophy af Basil T. Darras, Thomas O. Crawford, Richard S. Finkel, Eugenio Mercuri, Darryl C. De Vivo, Maryam Oskoui, Eduardo F. Tizzano, Monique M. Ryan, Francesco Muntoni, Guolin Zhao, John F. Staropoli, Alexander McCampbell, Marco Petrillo, Christopher Stebbins, Stephanie Fradette, Wildon Farwell, Charlotte J. Sumner
Udgivet 2019Artigo -
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Design of a Randomized, Placebo-Controlled, Phase 3 Trial of Tofersen Initiated in Clinically Presymptomatic SOD1 Variant Carriers: the ATLAS Study af Michael Benatar, Joanne Wuu, Peter M. Andersen, Robert C. Bucelli, Jinsy Andrews, Markus Otto, Nita A. Farahany, Elizabeth A. Harrington, Weiping Chen, Adele A. Mitchell, Toby A. Ferguson, Sheena Chew, Liz Gedney, Sue Oakley, Jeong Heo, Sowmya Chary, Laura Fanning, Danielle Graham, Peng Sun, Yingying Liu, Janice Wong, Stephanie Fradette
Udgivet 2022Artigo -
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Trial of Antisense Oligonucleotide Tofersen for <i>SOD1</i> ALS af Jonathan Mill, Merit Cudkowicz, Angela Genge, Pamela J. Shaw, Gen Sobue, Robert C. Bucelli, Adriano Chió, Philip Van Damme, Albert C. Ludolph, Jonathan D. Glass, Jinsy Andrews, Suma Babu, Michael Benatar, Christopher McDermott, Thos Cochrane, Sowmya Chary, Sheena Chew, Han Zhu, Fan Wu, Ivan Nestorov, Danielle Graham, Peng Sun, Manjit McNeill, Laura Fanning, Toby A. Ferguson, Stephanie Fradette
Udgivet 2022Artigo -
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Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study af Darryl C. De Vivo, Enrico Bertini, Kathryn J. Swoboda, Wuh‐Liang Hwu, Thomas O. Crawford, Richard S. Finkel, Janbernd Kirschner, Nancy L. Kuntz, Julie Parsons, Monique M. Ryan, Russell J. Butterfield, Haluk Topaloğlu, Tawfeg Ben‐Omran, Valeria Sansone, Yuh‐Jyh Jong, Francy Shu, John F. Staropoli, Douglas A. Kerr, Alfred Sandrock, Christopher Stebbins, Marco Petrillo, Gabriel Braley, Kristina Johnson, Richard Foster, Sarah Gheuens, Ishir Bhan, Sandra P. Reyna, Stephanie Fradette, Wildon Farwell
Udgivet 2019Artigo -
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Phase 1–2 Trial of Antisense Oligonucleotide Tofersen for <i>SOD1</i> ALS af Jonathan Mill, Merit Cudkowicz, Pamela J. Shaw, Peter M. Andersen, Nazem Atassi, Robert C. Bucelli, Angela Genge, Jonathan D. Glass, Shafeeq Ladha, Albert Ludolph, Nicholas J. Maragakis, Christopher McDermott, Alan Pestronk, John Ravits, François Salachas, Randall Trudell, Philip Van Damme, Lorne Zinman, C. Frank Bennett, Roger Lane, Alfred Sandrock, Heiko Runz, Danielle Graham, Hani Houshyar, Alexander McCampbell, Ivan Nestorov, Ih Chang, Manjit McNeill, Laura Fanning, Stephanie Fradette, Toby A. Ferguson
Udgivet 2020Artigo -
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Preventing amyotrophic lateral sclerosis: insights from pre-symptomatic neurodegenerative diseases af Michael Benatar, Joanne Wuu, Caroline McHutchison, Ronald B. Postuma, Bradley F. Boeve, Ronald C. Petersen, Christopher A. Ross, Howard J. Rosen, Jalayne J. Arias, Stephanie Fradette, Michael McDermott, Jeremy M. Shefner, Christine Stanislaw, Sharon Abrahams, Stephanie Cosentino, Peter M. Andersen, Richard S. Finkel, Volkan Granit, Anne‐Laure Grignon, Jonathan D. Rohrer, Corey T. McMillan, Murray Grossman, Ammar Al‐Chalabi, Martin R. Turner, Ammar Al‐Chalabi, Peter M. Andersen, Jalayne J. Arias, Michael Benatar, Bradley F. Boeve, Stephanie Cosentino, Kuldip D. Dave, Toby A. Ferguson, Mary-Kay Floeter, Jonathan D. Rohrer, Stephanie Fradette, Tania F. Gendron, Volkan Granit, Anne‐Laure Grignon, Murray Grossman, Amelie K. Gubitz, Petra Kaufman, Isabelle Le Ber, Suzee Lee, Andrea Malaspina, Michael McDermott, Caroline McHutchison, Corey T. McMillan, Katie Nicholson, Ronald C. Petersen, Ronald B. Postuma, Richard Robinson, Howard J. Rosen, Christopher A. Ross, Jeremy M. Shefner, Christine Stanislaw, Nadine Tatton, Neil Thakur, Martin R. Turner, Jochen H. Weishaupt, Joanne Wuu
Udgivet 2021Artigo -
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The Miami Framework for ALS and related neurodegenerative disorders: an integrated view of phenotype and biology af Michael Benatar, Joanne Wuu, Edward D. Huey, Corey T. McMillan, Ronald C. Petersen, Ronald B. Postuma, Caroline McHutchison, Laynie Dratch, Jalayne J. Arias, Anita Crawley, Henry Houlden, Michael McDermott, Xueya Cai, Neil Thakur, Adam L. Boxer, Howard J. Rosen, Bradley F. Boeve, Penny A. Dacks, Stephanie Cosentino, Sharon Abrahams, Neil A. Shneider, Paul Lingor, Jeremy M. Shefner, Peter M. Andersen, Ammar Al‐Chalabi, Martin R. Turner, Ronald C. Petersen, Peggy Allred, Stanley H. Appel, David Benatar, James Berry, Meg Bradbury, Lucie Bruijn, Jennifer Buczyner, Nathan Carberry, James B. Caress, Thomas H. Champney, Kuldip D. Dave, Stephanie Fradette, Volkan Granit, Anne‐Laure Grignon, Amelie K. Gubitz, Matthew B. Harms, Terry Heiman‐Patterson, Sharon Hesterlee, Karen A. Lawrence, Travis “Pete” Lewis, Oren Levy, Tahseen Mozaffar, Christine Stanislaw, Alexander G. Thompson, Olga Uspenskaya, Patrick Weydt, Lorne Zinman
Udgivet 2024Revisão
Søgeredskaber:
Relaterede emner
Disease
Medicine
Amyotrophic lateral sclerosis
Biology
Pathology
Genetics
Biomarker
Clinical trial
Gene
Internal medicine
Neuroscience
Psychology
Adverse effect
Atrophy
Bioinformatics
C9orf72
Chemistry
Dementia
Frontotemporal dementia
Gastroenterology
Phenotype
Physical medicine and rehabilitation
SOD1
Spinal muscular atrophy
Alternative medicine
Anesthesia
Biochemistry
Cerebrospinal fluid
Clinical endpoint
Clinical phenotype