Search Results - Simone Thomas

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    Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial by Pedro Machado, Michael McDermott, Thomas Blaettler, Claus Sundgreen, Anthony A. Amato, Emma Ciafaloni, Miriam Freimer, Summer Gibson, Sarah Jones, Todd Levine, Thomas E. Lloyd, Tahseen Mozaffar, Aziz Shaibani, Matthew Wicklund, Anders Rosholm, Tim Dehli Carstensen, Karen Bonefeld, Anders Nørkær Jørgensen, Karina Phonekeo, Andrew Heim, Laura Herbelin, Richard J. Barohn, Michael G. Hanna, Mazen M. Dimachkie, Mazen M. Dimachkie, Jeffrey Statland, Mamatha Pasnoor, Omar Jawdat, Andrew Heim, Ali Ciersdorff, Sandhya Sasidharan, Melissa Currence, Todd Levine, Rebecca Otutoa, Angelina Cooper, Tahseen Mozaffar, Ali A. Habib, Jonathan Cauchi, Shannon Ung, Veena Mathew, Isela Hernandez, Summer Gibson, Mark B. Bromberg, Kyle Mahoney, Crystal Neate, Teresa Janecki, Mike Papadakis, Miriam Freimer, MacKenzie Kaschalk, Sarah Heintzman, Matthew Wicklund, Brenna Baines, Alexa Vareldzis, Emily Hyslop, Brianna Blume, Emma Ciafaloni, Elizabeth Luebbe, Katy Eichinger, William Martens, Stephanie Gregory, Joanne Janciuras, Anthony A. Amato, Christopher Doughty, Kristen Roe, Patricia M. Flynn, Emily Russo, Thomas E. Lloyd, Jemima Albayda, Eleni Tiniakou, Simone Thomas, Sarah Jones, Guillermo Solórzano, Matthew Elliott, Ted M. Burns, Allison Crowell, Deborah Eggleston, Mary Wagoner, Aziz Shaibani, Chantae Oates, Pedro Machado, Michael G. Hanna, Linda Greensmith, Mhoriam Ahmed, Vinojini Vivekanandam, Matthew Appleby, George Ransley, Edwin Eshun, Iwona Skorupinska, Louise Germain, Ana Marie Laxa, Joana Roca Pontes, Anna Bellin, Dolapo Anifowoshe

    Published 2023
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    Artigo
  18. 18

    Sorafenib promotes graft-versus-leukemia activity in mice and humans through IL-15 production in FLT3-ITD-mutant leukemia cells by Nimitha R. Mathew, Francis Baumgartner, Lukas M. Braun, David O’Sullivan, Simone Thomas, Miguel Waterhouse, Tony Andreas Müller, Kathrin Hanke, Sanaz Taromi, Petya Apostolova, Anna Lena Illert, Wolfgang Melchinger, Sandra Duquesne, Annette Schmitt‐Graeff, Lena Oßwald, Kaili Yan, Arnim Weber, Sònia Tugues, Sabine Spath, Dietmar Pfeifer, Marie Follo, Rainer Claus, Michael Lübbert, Christoph Rummelt, Hartmut Bertz, Ralph Wäsch, Johanna Haag, Andrea Schmidts, Michael Schultheiß, Dominik Bettinger, Robert Thimme, Evelyn Ullrich, Yakup Tanriver, Giang Lam Vuong, Renate Arnold, Philipp Hemmati, Dominik Wolf‎, Markus Ditschkowski, Cordula A. Jilg, Konrad Wilhelm, Christian Leiber, Sabine Gerull, Jörg Halter, Claudia Lengerke, Thomas Pabst, Thomas Schroeder, Guido Kobbe, Wolf Rösler, Soroush Doostkam, Stephan Meckel, Kathleen Stabla, Stephan Metzelder, Sebastian Halbach, Tilman Brummer, Zehan Hu, Jörn Dengjel, Björn Hackanson, Christoph Schmid, Udo Holtick, Christof Scheid, Alexandros Spyridonidis, Friedrich Stölzel, Rainer Ordemann, Lutz Müller, Flore Sicre-de-Fontbrune, Gabriele Ihorst, Jürgen Kuball, Jan E. Ehlert, Daniel Feger, Eva-Maria Wagner, Jean‐Yves Cahn, Jacqueline Schnell, Florian Kuchenbauer, Donald Bunjes, Ronjon Chakraverty, Simon Richardson, Saar Gill, Nicolaus Kröger, Francis Ayuk, Luca Vago, Fabio Ciceri, A Müller, Takeshi Kondo, Takanori Teshima, Susan Klaeger, Bernhard Küster, Dennis Dong Hwan Kim, Daniel J. Weisdorf, Walter J. F. M. van der Velden, Daniela Dörfel, Wolfgang Bethge, Inken Hilgendorf, Andreas Hochhaus, Geoffroy Andrieux, Melanie Börries, Hauke Busch, John Magenau, Pavan Reddy, Myriam Labopin, Joseph H. Antin

    Published 2018
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    Artigo
  19. 19

    Biallelic mutations in SORD cause a common and potentially treatable hereditary neuropathy with implications for diabetes by Andrea Cortese, Yi Zhu, Adriana Rebelo, Sara Negri, Steve Courel, Lisa Abreu, Chelsea J. Bacon, Yunhong Bai, Dana M. Bis‐Brewer, Enrico Bugiardini, Elena Buglo, Matt C. Danzi, Shawna Feely, Alkyoni Athanasiou‐Fragkouli, Nourelhoda A. Haridy, Aixa Rodríguez, Alexa Bacha, Ashley Kosikowski, Beth Wood, Brett A. McCray, Brianna Blume, Carly E. Siskind, Charlotte J. Sumner, Daniela Calabrese, David Walk, Dragan Vujović, Eun Hye Park, Francesco Muntoni, Gabrielle Donlevy, Gyula Acsádi, John Day, Joshua Burns, Jun Li, Karen Krajewski, Kate Eichinger, Kayla Cornett, Krista Mullen, Perez Quiros Laura, Laurie Gutmann, Maria Barrett, Mario Saporta, Mariola Skorupinska, Natalie Grant, Paula Bray, Reza Sadjadi, Riccardo Zuccarino, Richard S. Finkel, Richard A. Lewis, Rosemary Shy, Sabrina W. Yum, Sarah Hilbert, Simone Thomas, Steffen Behrens‐Spraggins, Tara Jones, Thomas E. Lloyd, Tiffany Grider, Tim Estilow, Vera Fridman, Rosario Isasi, Alaa Khan, Matilde Laurá, Stefania Magri, Menelaos Pipis, Chiara Pisciotta, Eric Powell, Alexander M. Rossor, Paola Saveri, Janet E. Sowden, Stefano Tozza, Jana Vandrovcová, Julia E. Dallman, Elena Grignani, Enrico Marchioni, Steven S. Scherer, Beisha Tang, Zhiqiang Lin, Abdullah Al‐Ajmi, Rebecca Schüle, Matthis Synofzik, Thierry Maisonobe, Tanya Stojkovic, Michaela Auer‐Grumbach, Mohamed A. Abdelhamed, Sherifa A. Hamed, Ruxu Zhang, Fiore Manganelli, Lucio Santoro, Franco Taroni, Davide Pareyson, Henry Houlden, David N. Herrmann, Mary M. Reilly, Michael E. Shy, R. Grace Zhai, Stephan Züchner

    Published 2020
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    Artigo