检索结果 - Silvia Bader‐Weder
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1
An expanded access program of risdiplam for patients with Type 1 or 2 spinal muscular atrophy 由 Jennifer M. Kwon, Kapil Arya, Nancy L. Kuntz, Han C. Phan, Cory Sieburg, Kathryn J. Swoboda, Aravindhan Veerapandiyan, Beverly Assman, Silvia Bader‐Weder, Travis L. Dickendesher, Jennifer L. Hansen, Helen Lin, Ying Yan, Vamshi K. Rao
出版 2022Artigo -
2
Risdiplam in types 2 and 3 spinal muscular atrophy: A randomised, placebo‐controlled, dose‐finding trial followed by 24 months of treatment 由 Eugenio Mercuri, Giovanni Baranello, Odile Boespflug‐Tanguy, Liesbeth De Waele, Nathalie Goemans, Janbernd Kirschner, Riccardo Masson, Elena Mazzone, Astrid Pechmann, Maria Carmela Pera, Carole Vuillerot, Silvia Bader‐Weder, Marianne Gerber, Ksenija Gorni, Janine Hoffart, Heidemarie Kletzl, Carmen Martín, Tammy McIver, R. Scalco, Wai Yin Yeung, Laurent Servais
出版 2022Artigo