نتائج البحث - Peter Slasor
- يعرض 1 - 9 نتائج من 9
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1
Intramuscular Interferon Beta-1A Therapy Initiated during a First Demyelinating Event in Multiple Sclerosis حسب Lawrence Jacobs, Roy W. Beck, Jack H. Simon, R. Phillip Kinkel, Carol M. Brownscheidle, T. J. Murray, Nancy A. Simonian, Peter Slasor, Alfred Sandrock
منشور في 2000Artigo -
2
Real-world clinical outcomes of patients with CLN2 disease treated with cerliponase alfa حسب Angela Schulz, Christoph Schwering, Eva Wibbeler, Lena Marie Westermann, Luca Hagenah, Susanne Lezius, Ashok Kumar Jha, Abigail Hunt, Peter Slasor, Pascal Reisewitz, Miriam Nickel
منشور في 2025Artigo -
3
Study of Intraventricular Cerliponase Alfa for CLN2 Disease حسب Angela Schulz, Temitayo Ajayi, Nicola Specchio, Emily de los Reyes, Paul Gissen, Douglas Ballon, Jonathan P. Dyke, Heather Cahan, Peter Slasor, David Jacoby, Alfried Kohlschütter
منشور في 2018Artigo -
4
Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo‐controlled study حسب Christian J. Hendriksz, Barbara K. Burton, Thomas R. Fleming, Paul Harmatz, Derralynn Hughes, Simon Jones, Hsiang‐Yu Lin, Eugen Mengel, Maurizio Scarpa, Vassili Valayannopoulos, Roberto Giugliani, Peter Slasor, Debra L. Lounsbury, Wolfgang Dummer
منشور في 2014Artigo -
5
Disease characteristics and progression in patients with late-infantile neuronal ceroid lipofuscinosis type 2 (CLN2) disease: an observational cohort study حسب Miriam Nickel, Alessandro Simonati, David Jacoby, Susanne Lezius, Dirk Kilian, Benjamin Van de Graaf, Odelya E. Pagovich, Barry E. Kosofsky, Kaleb Yohay, Matthew Downs, Peter Slasor, Temitayo Ajayi, Ronald G. Crystal, Alfried Kohlschütter, Dolan Sondhi, Angela Schulz
منشور في 2018Artigo -
6
The Morquio A Clinical Assessment Program: Baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects حسب Paul Harmatz, Eugen Mengel, Roberto Giugliani, Vassili Valayannopoulos, Shuan-Pei Lin, Rossella Parini, Nathalie Guffon, Barbara K. Burton, Christian J. Hendriksz, John J. Mitchell, Ana María Martins, Simon Jones, Norberto Guelbert, Ashok Vellodi, Carla E. M. Hollak, Peter Slasor, Celeste Decker
منشور في 2013Artigo -
7
Safety and efficacy of cerliponase alfa in children with neuronal ceroid lipofuscinosis type 2 (CLN2 disease): an open-label extension study حسب Angela Schulz, Nicola Specchio, Emily de los Reyes, Paul Gissen, Miriam Nickel, Marina Trivisano, Shawn C. Aylward, Anupam Chakrapani, Christoph Schwering, Eva Wibbeler, Lena Marie Westermann, Douglas Ballon, Jonathan P. Dyke, Anu Cherukuri, Shailesh Bondade, Peter Slasor, Jessica Cohen Pfeffer
منشور في 2023Artigo -
8
Longitudinal analysis of endurance and respiratory function from a natural history study of Morquio A syndrome حسب Paul Harmatz, Eugen Mengel, Roberto Giugliani, Vassili Valayannopoulos, Shuan-Pei Lin, Rossella Parini, Nathalie Guffon, Barbara K. Burton, Christian J. Hendriksz, John J. Mitchell, Ana María Martins, Simon Jones, Norberto Guelbert, Ashok Vellodi, Frits A. Wijburg, Kehu Yang, Peter Slasor, Celeste Decker
منشور في 2014Artigo -
9
Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome حسب Christian J. Hendriksz, Rossella Parini, Moeenaldeen AlSayed, Julian Raiman, Roberto Giugliani, Martha Luz Solano Villarreal, John J. Mitchell, Barbara K. Burton, Norberto Guelbert, Fiona Stewart, Derralynn Hughes, Kenneth I. Berger, Peter Slasor, Robert Matousek, Elaina Jurecki, Adam J. Shaywitz, Paul Harmatz
منشور في 2016Artigo
أدوات البحث:
موضوعات ذات صلة
Internal medicine
Medicine
Disease
Enzyme replacement therapy
Pathology
Alternative medicine
Pediatrics
Physical therapy
Placebo
Adverse effect
Clinical endpoint
Clinical trial
Environmental health
Population
Surgery
Batten disease
Biochemistry
Biology
Cardiology
Civil engineering
Clinical Dementia Rating
Clinically isolated syndrome
Cognition
Cohort
Cohort study
Dementia
Diffusing capacity
Discontinuation
Dosing
Engineering