Resultados da pesquisa - Jonas Müntze
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Hot topics in Fabry disease Por Tereza Cairns, Jonas Müntze, Judith Gernert, Lisa Spingler, Peter Nordbeck, Christoph Wanner
Publicado em 2018Revisão -
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Oral Chaperone Therapy Migalastat for Treating Fabry Disease: Enzymatic Response and Serum Biomarker Changes After 1 Year Por Jonas Müntze, Daniel Gensler, Octavian Maniuc, Dan Liu, Tereza Cairns, Daniel Oder, Kai Hu, Kristina Lorenz, Stefan Frantz, Christoph Wanner, Peter Nordbeck
Publicado em 2018Artigo
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Disease
Fabry disease
Medicine
Biochemistry
Bioinformatics
Biology
Biomarker
Cardiology
Chemistry
Creatinine
Enzyme replacement therapy
Gastroenterology
Intensive care medicine
Internal medicine
Law
Lysosomal storage disease
Lysosomal storage disorders
MEDLINE
Pathology
Political science
Renal function
Substrate reduction therapy
Urology