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Antibody-oligonucleotide conjugate achieves CNS delivery in animal models for spinal muscular atrophy por Suzan M. Hammond, Frank Abendroth, Larissa Goli, Jessica Stoodley, Matthew Burrell, George Thom, Ian Gurrell, Nina Ahlskog, Michael J. Gait, Matthew J. A. Wood, Carl I. Webster
Publicado em 2022Artigo
Ferramentas de busca:
Assuntos relacionados
Biochemistry
Biology
Gene
Genetics
In vivo
Medicine
Pharmacology
Antibody
Antisense therapy
Biodistribution
Bioinformatics
Combinatorics
Disease
Genetically modified mouse
Immunology
Internal medicine
Locked nucleic acid
Mathematics
Myotonia
Myotonic dystrophy
Oligonucleotide
Pathology
SMA*
Spinal muscular atrophy
Systemic administration
Transgene