檢索結果 - Hadas Shasha‐Lavsky
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1
Efficacy and safety of lumasiran for infants and young children with primary hyperoxaluria type 1: 12-month analysis of the phase 3 ILLUMINATE-B trial 由 Wesley Hayes, David J. Sas, Daniella Magen, Hadas Shasha‐Lavsky, Mini Michael, Anne‐Laure Sellier‐Leclerc, Julien Hogan, Taylor Ngo, Marianne T. Sweetser, John M. Gansner, Tracy L. McGregor, Yaacov Frishberg
出版 2022Artigo -
2
Lumasiran for Advanced Primary Hyperoxaluria Type 1: Phase 3 ILLUMINATE-C Trial 由 Mini Michael, Jaap W. Groothoff, Hadas Shasha‐Lavsky, John C. Lieske, Yaacov Frishberg, Eva Šimková, Anne‐Laure Sellier‐Leclerc, Arnaud Devresse, Fitsum Guebre‐Egziabher, Sevcan A. Bakkaloğlu, Chebl Mourani, Rola Saqan, Richard Singer, Richard E. Willey, Bahru Habtemariam, John M. Gansner, Ishir Bhan, Tracy L. McGregor, Daniella Magen
出版 2022Artigo -
3
Lumasiran, an RNAi Therapeutic for Primary Hyperoxaluria Type 1 由 Sander F. Garrelfs, Yaacov Frishberg, Sally A. Hulton, Michael J. Koren, William O’Riordan, Pierre Cochat, Georges Deschênes, Hadas Shasha‐Lavsky, Jeffrey M. Saland, William G. van’t Hoff, Daniel G. Fuster, Daniella Magen, Shabbir H. Moochhala, Gesa Schalk, Eva Šimková, Jaap W. Groothoff, David J. Sas, Kristin Meliambro, Jiandong Lu, Marianne T. Sweetser, Pushkal Garg, Akshay Vaishnaw, John M. Gansner, Tracy L. McGregor, John C. Lieske
出版 2021Artigo -
4
Phase 3 trial of lumasiran for primary hyperoxaluria type 1: A new RNAi therapeutic in infants and young children 由 David J. Sas, Daniella Magen, Wesley Hayes, Hadas Shasha‐Lavsky, Mini Michael, Indra Schulte, Anne‐Laure Sellier‐Leclerc, Jiandong Lu, Ali Seddighzadeh, Bahru Habtemariam, Tracy L. McGregor, Kenji P. Fujita, Yaacov Frishberg, Justine Bacchetta, Véronique Baudouin, Rachel Becker‐Cohen, Shimrit Tzvi Behr, Efrat Ben‐Shalom, Maria Berdaguer, Detlef Böckenhauer, Pierre Cochat, Martin Coenen, Carl H. Cramer, Georges Deschênes, Claire Dossier, Emilie Doye, Liat Feraru Feldman, Maximilian Hohenadel, Florentia Kaguelidou, Irina Libinson Zebegret, John C. Lieske, Anne Maisin, Dawn S. Milliner, Moran Plonsky Toder, Shirley Pollack, Aurélie Portefaix, Bruno Ranchin, Choni Rinat, Adnan Safdar, Gesa Schalk, Poyyapakkam Srivaths, Cheryl L. Tran, William van’t Hoff, Jenny Weinbrand-Goichberg, Irith Weissman
出版 2021Artigo -
5
Treatment and long-term outcome in primary distal renal tubular acidosis 由 Sergio Camilo Lopez-Garcia, Francesco Emma, Stephen B. Walsh, Marc Fila, Nakysa Hooman, Marcin Zaniew, Aurélia Bertholet‐Thomas, Giacomo Colussi, Kathrin Burgmaier, Elena Levtchenko, Jyoti Sharma, Jyoti Singhal, Neveen A. Soliman, Gema Ariceta, Biswanath Basu, Luisa Murer, Velibor Tasić, А.Н. Цыгин, Stéphane Decramer, Helena Gil‐Peña, Linda Koster‐Kamphuis, Claudio La Scola, Jutta Gellermann, Martin Konrad, Marc R. Liliën, Telma Francisco, Despoina Tramma, Peter Trnka, Selçuk Yüksel, Rosa Caruso, Milan Chromek, Zelal Ekinci, Giovanni Gambaro, Jameela A. Kari, Jens König, Francesca Taroni, Julia Thumfart, Francesco Trepiccione, Louise Winding, Elke Wühl, Ayşe Ağbaş, А. Г. Белькевич, Rosa Vargas‐Poussou, Anne Blanchard, Giovanni Conti, Olivia Boyer, İsmail Dursun, Ayşe Seda Pınarbaşı, Engin Melek, Marius Miglinas, Robert Novo, Andrew Mallett, Danko Milošević, Maria Szczepańska, Sarah Wente, Hae Il Cheong, Rajiv Sinha, Zoran Gucev, Stephanie Dufek, Daniela Iancu, Amira Peco‐Antić, Amrit Kaur, Antonino Paglialunga, Aude Servais, Branko Lutovac, Ewout J. Hoorn, Hadas Shasha‐Lavsky, Jérôme Harambat, Astrid Godron-Dubrasquet, Kathrin Buder, Lise Allard, Ludwig Patzer, М.В. Шумихина, Matthias Hansen, Nikoleta Printza, Nuran Küçük, Ortraud Beringer, Rajendra Bhimma, Rimantė Čerkauskienė, Thomas J. Neuhaus, Valbona Stavileci, Tim Ulinski, Nida Dinçel, Nilufar Mohebbi, Robert Kleta, Franz Schaefer, Detlef Böckenhauer
出版 2018Artigo
相關主題
Internal medicine
Kidney
Medicine
Primary hyperoxaluria
Chemistry
Gastroenterology
Organic chemistry
Pediatrics
Renal function
Clinical endpoint
Cohort
Creatinine
Kidney disease
Nephrocalcinosis
Oxalate
Surgery
Urinary system
Urology
Adverse effect
Biochemistry
Biology
Clinical trial
Dialysis
Distal renal tubular acidosis
Dosing
Gene
Hemodialysis
Interquartile range
Kidney stones
Metabolic acidosis