检索结果 - Gihan Tennekoon
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Phase 1 Study of Edasalonexent (CAT-1004), an Oral NF-κB Inhibitor, in Pediatric Patients with Duchenne Muscular Dystrophy 由 Erika Finanger, Krista Vandenborne, Richard S. Finkel, H. Lee Sweeney, Gihan Tennekoon, Sabrina W. Yum, Maria Mancini, Pradeep Bista, Andrew J. Nichols, Hanlan Liu, Angelika Fretzen, Joanne M. Donovan
出版 2018Artigo -
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Sildenafil does not improve cardiomyopathy in <scp>D</scp>uchenne/<scp>B</scp>ecker muscular dystrophy 由 Doris G. Leung, Daniel A. Herzka, William Thompson, Bing He, Genila Bibat, Gihan Tennekoon, Stuart D. Russell, Karl H. Schuleri, Albert C. Lardo, David A. Kass, Richard E. Thompson, Daniel P. Judge, Kathryn R. Wagner
出版 2014Artigo -
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Longitudinal timed function tests in Duchenne muscular dystrophy: ImagingDMD cohort natural history 由 Harneet Arora, Rebecca J. Willcocks, Donovan J. Lott, Ann T. Harrington, Claudia Senesac, Kirsten L. Zilke, Michael J. Daniels, Dandan Xu, Gihan Tennekoon, Erika Finanger, Barry S. Russman, Richard S. Finkel, William Triplett, Barry J. Byrne, Glenn A. Walter, H. Lee Sweeney, Krista Vandenborne
出版 2018Artigo -
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Examination of effects of corticosteroids on skeletal muscles of boys with DMD using MRI and MRS 由 Ishu Arpan, Rebecca J. Willcocks, Sean C. Forbes, Richard S. Finkel, Donovan J. Lott, William D. Rooney, William Triplett, Claudia Senesac, Michael J. Daniels, Barry J. Byrne, Erika Finanger, Barry S. Russman, Dah-Jyuu Wang, Gihan Tennekoon, Glenn A. Walter, H. Lee Sweeney, Krista Vandenborne
出版 2014Artigo -
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Magnetic Resonance Imaging and Spectroscopy Assessment of Lower Extremity Skeletal Muscles in Boys with Duchenne Muscular Dystrophy: A Multicenter Cross Sectional Study 由 Sean C. Forbes, Rebecca J. Willcocks, William Triplett, William D. Rooney, Donovan J. Lott, Dah-Jyuu Wang, Jim Pollaro, Claudia Senesac, Michael J. Daniels, Richard S. Finkel, Barry S. Russman, Barry J. Byrne, Erika Finanger, Gihan Tennekoon, Glenn A. Walter, H. Lee Sweeney, Krista Vandenborne
出版 2014Artigo -
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Multicenter prospective longitudinal study of magnetic resonance biomarkers in a large duchenne muscular dystrophy cohort 由 Rebecca J. Willcocks, William D. Rooney, William Triplett, Sean C. Forbes, Donovan J. Lott, Claudia Senesac, Michael J. Daniels, Dah‐Jyuu Wang, Ann T. Harrington, Gihan Tennekoon, Barry S. Russman, Erika Finanger, Barry J. Byrne, Richard S. Finkel, Glenn A. Walter, H. Lee Sweeney, Krista Vandenborne
出版 2016Artigo -
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MR biomarkers predict clinical function in Duchenne muscular dystrophy 由 Alison M. Barnard, Rebecca J. Willcocks, William Triplett, Sean C. Forbes, Michael J. Daniels, Saptarshi Chakraborty, Donovan J. Lott, Claudia Senesac, Erika Finanger, Ann T. Harrington, Gihan Tennekoon, Harneet Arora, Dah-Jyuu Wang, H. Lee Sweeney, William D. Rooney, Glenn A. Walter, Krista Vandenborne
出版 2020Artigo -
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Evaluator Training and Reliability for SMA Global Nusinersen Trials1 由 Allan M. Glanzman, Elena Mazzone, Sally Dunaway Young, Richard Gee, Kristy Rose, Anna Mayhew, Leslie Nelson, Chris Yun, K. Alexander, Basil T. Darras, Zarazuela Zolkipli‐Cunningham, Gihan Tennekoon, John Day, Richard S. Finkel, Eugenio Mercuri, Darryl C. De Vivo, Ron Baldwin, Kathie M. Bishop, Jacqueline Montes
出版 2018Artigo -
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Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambulatory Patients with Spinal Muscular Atrophy: Phase I Ascending-Dose Study (STRONG) 由 Richard S. Finkel, Basil T. Darras, Jerry R. Mendell, John Day, Nancy L. Kuntz, Anne M. Connolly, Craig M. Zaidman, Thomas O. Crawford, Russell J. Butterfield, Perry B. Shieh, Gihan Tennekoon, John F. Brandsema, Susan T. Iannaccone, John M. Shoffner, Sarah Kavanagh, Thomas A. Macek, Sitra Tauscher‐Wisniewski
出版 2023Artigo -
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Skeletal muscle magnetic resonance biomarkers correlate with function and sentinel events in Duchenne muscular dystrophy 由 Alison M. Barnard, Rebecca J. Willcocks, Erika Finanger, Michael J. Daniels, William Triplett, William D. Rooney, Donovan J. Lott, Sean C. Forbes, Dah-Jyuu Wang, Claudia Senesac, Ann T. Harrington, Richard S. Finkel, Barry S. Russman, Barry J. Byrne, Gihan Tennekoon, Glenn A. Walter, H. Lee Sweeney, Krista Vandenborne
出版 2018Artigo -
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Modeling disease trajectory in Duchenne muscular dystrophy 由 William D. Rooney, Yosef A. Berlow, William Triplett, Sean C. Forbes, Rebecca J. Willcocks, Dah-Jyuu Wang, Ishu Arpan, Harneet Arora, Claudia Senesac, Donovan J. Lott, Gihan Tennekoon, Richard S. Finkel, Barry S. Russman, Erika Finanger, Saptarshi Chakraborty, Elliott O’Brien, Brendan Moloney, Alison M. Barnard, H. Lee Sweeney, Michael J. Daniels, Glenn A. Walter, Krista Vandenborne
出版 2020Artigo -
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Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool 由 Danielle Ramsey, Mariacristina Scoto, Anna Mayhew, Marion Main, Elena Mazzone, Jacqueline Montes, Roberto De Sanctis, Sally Dunaway Young, Rachel Salazar, Allan M. Glanzman, Amy Pasternak, Janet Quigley, Elizabeth Mirek, Tina Duong, Richard Gee, Matthew Civitello, Gihan Tennekoon, Marika Pane, Maria Carmela Pera, Kate Bushby, John Day, Basil T. Darras, Darryl C. De Vivo, Richard S. Finkel, Eugenio Mercuri, Francesco Muntoni
出版 2017Artigo -
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Ambulatory function in spinal muscular atrophy: Age-related patterns of progression 由 Jacqueline Montes, Michael McDermott, Elizabeth Mirek, Elena Mazzone, Marion Main, Allan M. Glanzman, Tina Duong, Sally Dunaway Young, Rachel Salazar, Amy Pasternak, Richard Gee, Roberto De Sanctis, Giorgia Coratti, Nicola Forcina, Lavinia Fanelli, Danielle Ramsey, Evelin Milev, Matthew Civitello, Marika Pane, Maria Carmela Pera, Mariacristina Scoto, John Day, Gihan Tennekoon, Richard S. Finkel, Basil T. Darras, Francesco Muntoni, Darryl C. De Vivo, Eugenio Mercuri
出版 2018Artigo -
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Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial 由 Craig M. McDonald, Craig Campbell, Ricardo Erazo Torricelli, Richard S. Finkel, Kevin M. Flanigan, Nathalie Goemans, Peter Heydemann, Anna Kamińska, Janbernd Kirschner, Francesco Muntoni, A. Nascimento Osorio, Ulrike Schara, Thomas Sejersen, Perry B. Shieh, H. Lee Sweeney, Haluk Topaloğlu, M. Tulinius, Juan J. Vílchez, Thomas Voït, Brenda Wong, Gary Elfring, Hans Kröger, Xiaohui Luo, Joseph McIntosh, Tuyen Ong, Peter Riebling, Marcio Ferreira de Souza, Robert J. Spiegel, Stuart W. Peltz, Eugenio Mercuri, Lindsay N. Alfano, Michelle Eagle, M. James, Linda Lowes, Anna Mayhew, Elena Mazzone, Leslie Nelson, Kristy Rose, Hoda Abdel‐Hamid, Susan Apkon, Richard J. Barohn, Enrico Bertini, Clemens Bloetzer, Lausanne Canton de Vaud, Russell J. Butterfield, B. Chabrol, Jong‐Hee Chae, Daehak-ro Jongno-gu, Giacomi Pietro Comi, Basil T. Darras, Jahannaz Dastgir, Isabelle Desguerre, Raúl G. Escobar, Erika Finanger, Michela Guglieri, Imelda Hughes, Susan T. Iannaccone, Kristi Jones, Peter Karachunski, Martin Kudr, Timothy Lotze, Jean K. Mah, Katherine D. Mathews, Yoram Nevo, Julie Parsons, Yann Péréon, Alexandra Prufer de Queiroz Campos Araújo, J. Ben Renfroe, Maria Bernadete Dutra de Resende, Monique M. Ryan, Kathryn Selby, Gihan Tennekoon, Giuseppe Vita
出版 2017Artigo
相关主题
Medicine
Internal medicine
Duchenne muscular dystrophy
Physical medicine and rehabilitation
Physical therapy
Biology
Muscular dystrophy
Biochemistry
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Ambulatory
Disease
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Magnetic resonance imaging
Radiology
SMA*
Spinal muscular atrophy
Anatomy
Cardiology
Cell biology
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Genetics
Prospective cohort study
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Biceps
Central nervous system
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Environmental health