Resultados de procura - Dragosky, Marta
- Mostrando 1 - 6 Resultados de 6
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Outcomes after 8 years of eliglustat therapy for Gaucher disease type 1: Final results from the Phase 2 trial por Lukina, Elena, Watman, Nora, Dragosky, Marta, Lau, Heather, Avila Arreguin, Elsa, Rosenbaum, Hanna, Zimran, Ari, Foster, Meredith C., Gaemers, Sebastiaan J. M., Peterschmitt, M. Judith
Publicado 2018Text -
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The road to biosimilars in rare diseases ‐ ongoing lessons from Gaucher disease por Drelichman, Guillermo, Castañeda‐Hernández, Gilberto, Cem Ar, Muhlis, Dragosky, Marta, Garcia, Ricardo, Lee, Howard, Moiseev, Sergey, Naderi, Majid, Rosenbaum, Hanna, Žnidar, Irena, Zuluaga, Andrés Felipe, Freisens, Selena, Mistry, Pramod K.
Publicado 2019Text -
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Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat por Kamath, Ravi S., Lukina, Elena, Watman, Nora, Dragosky, Marta, Pastores, Gregory M., Arreguin, Elsa Avila, Rosenbaum, Hanna, Zimran, Ari, Aguzzi, Rasha, Puga, Ana Cristina, Norfleet, Andrea M., Peterschmitt, M. Judith, Rosenthal, Daniel I.
Publicado 2014Text -
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Improvement in hematological, visceral, and skeletal manifestations of Gaucher disease type 1 with oral eliglustat tartrate (Genz-112638) treatment: 2-year results of a phase 2 stu... por Lukina, Elena, Watman, Nora, Arreguin, Elsa Avila, Dragosky, Marta, Iastrebner, Marcelo, Rosenbaum, Hanna, Phillips, Mici, Pastores, Gregory M., Kamath, Ravi S., Rosenthal, Daniel I., Kaper, Mathilde, Singh, Tejdip, Puga, Ana Cristina, Peterschmitt, M. Judith
Publicado 2010Text -
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A phase 2 study of eliglustat tartrate (Genz-112638), an oral substrate reduction therapy for Gaucher disease type 1 por Lukina, Elena, Watman, Nora, Arreguin, Elsa Avila, Banikazemi, Maryam, Dragosky, Marta, Iastrebner, Marcelo, Rosenbaum, Hanna, Phillips, Mici, Pastores, Gregory M., Rosenthal, Daniel I., Kaper, Mathilde, Singh, Tejdip, Puga, Ana Cristina, Bonate, Peter L., Peterschmitt, M. Judith
Publicado 2010Text