Search Results - Chivukula, Padmanabh
- Showing 1 - 7 results of 7
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1
Development of an mRNA replacement therapy for phenylketonuria by Perez-Garcia, Carlos G., Diaz-Trelles, Ramon, Vega, Jerel Boyd, Bao, Yanjie, Sablad, Marciano, Limphong, Patty, Chikamatsu, Simon, Yu, Hailong, Taylor, Wendy, Karmali, Priya P., Tachikawa, Kiyoshi, Chivukula, Padmanabh
Published 2022Text -
2
Lipid nanoparticle delivers phenylalanine ammonia lyase mRNA to the liver leading to catabolism and clearance of phenylalanine in a phenylketonuria mouse model by Diaz-Trelles, Ramon, Lee, Sharon, Kuakini, Kristen, Park, Jenny, Dukanovic, Adrian, Gonzalez, Jose A., Dam, Thanhchau, Kim, Jae Heon, Vega, Jerel Boyd, Sablad, Marciano, Karmali, Priya P., Tachikawa, Kiyoshi, Chivukula, Padmanabh
Published 2022Text -
3
Selective suppression of polyglutamine-expanded protein by lipid nanoparticle-delivered siRNA targeting CAG expansions in the mouse CNS by Hirunagi, Tomoki, Sahashi, Kentaro, Tachikawa, Kiyoshi, Leu, Angel I., Nguyen, Michelle, Mukthavaram, Rajesh, Karmali, Priya P., Chivukula, Padmanabh, Tohnai, Genki, Iida, Madoka, Onodera, Kazunari, Ohyama, Manabu, Okada, Yohei, Okano, Hideyuki, Katsuno, Masahisa
Published 2021Text -
4
Anti-HFRS Human IgG Produced in Transchromosomic Bovines Has Potent Hantavirus Neutralizing Activity and Is Protective in Animal Models by Perley, Casey C., Brocato, Rebecca L., Wu, Hua, Bausch, Christoph, Karmali, Priya P., Vega, Jerel B., Cohen, Melanie V., Somerville, Brandon, Kwilas, Steven A., Principe, Lucia M., Shamblin, Joshua, Chivukula, Padmanabh, Sullivan, Eddie, Hooper, Jay W.
Published 2020Text -
5
CD8(+) T cells mediate protection against Zika virus induced by an NS3-based vaccine by Elong Ngono, Annie, Syed, Thasneem, Nguyen, Anh-Viet, Regla-Nava, Jose Angel, Susantono, Mercylia, Spasova, Darina, Aguilar, Allison, West, Melissa, Sparks, Jessica, Gonzalez, Andrew, Branche, Emilie, DeHart, Jason L., Vega, Jerel Boyd, Karmali, Priya Prakash, Chivukula, Padmanabh, Kamrud, Kurt, Aliahmad, Parinaz, Wang, Nathaniel, Shresta, Sujan
Published 2020Text -
6
Immune modulatory nanoparticle therapeutics for intracerebral glioma by Yaghi, Nasser K., Wei, Jun, Hashimoto, Yuuri, Kong, Ling-Yuan, Gabrusiewicz, Konrad, Nduom, Edjah K., Ling, Xiaoyang, Huang, Neal, Zhou, Shouhao, Kerrigan, Brittany C. Parker, Levine, Jonathan M., Fajt, Virginia R., Levine, Gwendolyn, Porter, Brian F., Marcusson, Eric G., Tachikawa, Kiyoshi, Chivukula, Padmanabh, Webb, David C., Payne, Joseph E., Heimberger, Amy B.
Published 2017Text -
7
Hepatocyte-specific activity of TSC22D4 triggers progressive NAFLD by impairing mitochondrial function by Wolff, Gretchen, Sakurai, Minako, Mhamane, Amit, Troullinaki, Maria, Maida, Adriano, Deligiannis, Ioannis K., Yin, Kelvin, Weber, Peter, Morgenstern, Jakob, Wieder, Annika, Kwon, Yun, Sekar, Revathi, Zeigerer, Anja, Roden, Michael, Blüher, Matthias, Volk, Nadine, Poth, Tanja, Hackert, Thilo, Wiedmann, Lena, De Angelis Rigotti, Francesca, Rodriguez-Vita, Juan, Fischer, Andreas, Mukthavaram, Rajesh, Limphong, Pattraranee, Tachikawa, Kiyoshi, Karmali, Priya, Payne, Joseph, Chivukula, Padmanabh, Ekim-Üstünel, Bilgen, Martinez-Jimenez, Celia P., Szendrödi, Julia, Nawroth, Peter, Herzig, Stephan
Published 2022Text