检索结果 - Cheryl Wong Po Foo
- Showing 1 - 6 results of 6
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First-in-human in vivo genome editing via AAV-zinc-finger nucleases for mucopolysaccharidosis I/II and hemophilia B 由 Paul Harmatz, Carlos E. Prada, Barbara K. Burton, Heather Lau, Craig M. Kessler, Liching Cao, Marina Falaleeva, Andres G. Villegas, Jennifer Zeitler, Kathleen Meyer, Weston P. Miller, Cheryl Wong Po Foo, Sagar A. Vaidya, Wendy Swenson, Lisa H. Shiue, Didier Rouy, Joseph Muenzer
出版 2022Artigo -
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P142: Efficacy, safety and tolerability of chenodeoxycholic acid in adult patients with cerebrotendinous xanthomatosis (RESTORE): A randomized, placebo-controlled phase 3 study* 由 Andrea E. DeBarber, Yaz Y. Kisanuki, Paulo Ribeiro Nóbrega, Ryan Himes, Suman Jayadev, John Bernat, Vikram Prakash, James B. Gibson, Austin Larson, Paulo Victor Sgobbi de Souza, Edward Murphy, Brian Fedor, Cheryl Wong Po Foo, Rana Dutta, Michael J. Imperiale, Jolan Terner-Rosenthal, Will Garner, Pamela Vig, P. Barton Duell, Sarah Perez, Ritesh Ramdhani, Jonas Alex Morales Saute
出版 2024Artigo -
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Efficacy, safety, and tolerability of chenodeoxycholic acid (CDCA) in adult patients with cerebrotendinous xanthomatosis (RESTORE): a randomized withdrawal, double-blind, placebo-c... 由 Yaz Y. Kisanuki, Paulo Ribeiro Nóbrega, Ryan Himes, Suman Jayadev, John Bernat, Vikram Prakash, James B. Gibson, Austin Larson, Paulo Victor Sgobbi de Souza, Andrea E. DeBarber, Edward Murphy, Brian Fedor, Cheryl Wong Po Foo, Rana Dutta, Michael J. Imperiale, Will Garner, Joanne Quan, Pamela Vig, P. Barton Duell, Sarah Perez, Ritesh Ramdhani, Jonas Alex Morales Saute
出版 2025Artigo -
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Comparison of Allogeneic vs Autologous Bone Marrow–Derived Mesenchymal Stem Cells Delivered by Transendocardial Injection in Patients With Ischemic Cardiomyopathy 由 Joshua M. Hare, Joel E. Fishman, Gary Gerstenblith, Darcy L. Velazquez, Juan P. Zambrano, Viky Y. Suncion, Melissa Tracy, Eduard Ghersin, Peter V. Johnston, Jeffrey Brinker, Elayne Breton, Janice Davis‐Sproul, John Byrnes, Richard T. De George, Albert C. Lardo, Ivonne Hernandez Schulman, Adam Mendizabal, Maureen H. Lowery, Didier Rouy, Peter Altman, Cheryl Wong Po Foo, Phillip Ruiz, Alexandra Amador, Jose Da Silva, Ian McNiece, Alan W. Heldman
出版 2012Artigo -
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Transendocardial Mesenchymal Stem Cells and Mononuclear Bone Marrow Cells for Ischemic Cardiomyopathy 由 Alan W. Heldman, Darcy L. DiFede, Joel E. Fishman, Juan P. Zambrano, Barry Trachtenberg, Vasileios Karantalis, Muzammil Mushtaq, Adam Williams, Viky Y. Suncion, Ian McNiece, Eduard Ghersin, Victor Soto, Gustavo Lopera, Roberto Miki, Howard J. Willens, Robert C. Hendel, Raul D. Mitrani, Pradip M. Pattany, Gary Feigenbaum, Behzad N. Oskouei, John Byrnes, Maureen H. Lowery, Julio Sierra, M Pujol, Cindy Delgado, Phillip Gonzalez, Jose Rodriguez, Luiza Bagno, Didier Rouy, Peter Altman, Cheryl Wong Po Foo, Jose Da Silva, Erica Anderson, Richard P. Schwarz, Adam Mendizabal, Joshua M. Hare
出版 2013Artigo
相关主题
Medicine
Internal medicine
Pathology
Adverse effect
Alternative medicine
Biology
Placebo
Surgery
Cardiology
Cerebrotendinous Xanthomatosis
Chenodeoxycholic acid
Cholesterol
Ejection fraction
Heart failure
Ischemic cardiomyopathy
Mesenchymal stem cell
Tolerability
Transplantation
Biochemistry
Biomaterial
Biomedical engineering
Bone marrow
Cardiomyopathy
Cell biology
Context (archaeology)
Crossover study
Double blind
Gene
Genetics
Genome