Որոնման արդյունքները - Cagin, Umut
- Ցուցադրվում են 1 - 5 արդյունքները 5
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1
Unkempt Is Negatively Regulated by mTOR and Uncouples Neuronal Differentiation from Growth Control Avet-Rochex, Amélie, Carvajal, Nancy, Christoforou, Christina P., Yeung, Kelvin, Maierbrugger, Katja T., Hobbs, Carl, Lalli, Giovanna, Cagin, Umut, Plachot, Cedric, McNeill, Helen, Bateman, Joseph M.
Հրապարակվել է 2014Տեքստ -
2
Rescue of Advanced Pompe Disease in Mice with Hepatic Expression of Secretable Acid α-Glucosidase Cagin, Umut, Puzzo, Francesco, Gomez, Manuel Jose, Moya-Nilges, Maryse, Sellier, Pauline, Abad, Catalina, Van Wittenberghe, Laetitia, Daniele, Nathalie, Guerchet, Nicolas, Gjata, Bernard, Collaud, Fanny, Charles, Severine, Sola, Marcelo Simon, Boyer, Olivier, Krijnse-Locker, Jacomina, Ronzitti, Giuseppe, Colella, Pasqualina, Mingozzi, Federico
Հրապարակվել է 2020Տեքստ -
3
Gene therapy with secreted acid alpha-glucosidase rescues Pompe disease in a novel mouse model with early-onset spinal cord and respiratory defects Colella, Pasqualina, Sellier, Pauline, Gomez, Manuel J., Biferi, Maria G., Tanniou, Guillaume, Guerchet, Nicolas, Cohen-Tannoudji, Mathilde, Moya-Nilges, Maryse, van Wittenberghe, Laetitia, Daniele, Natalie, Gjata, Bernard, Krijnse-Locker, Jacomina, Collaud, Fanny, Simon-Sola, Marcelo, Charles, Severine, Cagin, Umut, Mingozzi, Federico
Հրապարակվել է 2020Տեքստ -
4
Deep morphological analysis of muscle biopsies from type III glycogenesis (GSDIII), debranching enzyme deficiency, revealed stereotyped vacuolar myopathy and autophagy impairment Laforêt, Pascal, Inoue, Michio, Goillot, Evelyne, Lefeuvre, Claire, Cagin, Umut, Streichenberger, Nathalie, Leonard-Louis, Sarah, Brochier, Guy, Madelaine, Angeline, Labasse, Clemence, Hedberg-Oldfors, Carola, Krag, Thomas, Jauze, Louisa, Fabregue, Julien, Labrune, Philippe, Milisenda, Jose, Nadaj-Pakleza, Aleksandra, Sacconi, Sabrina, Mingozzi, Federico, Ronzitti, Giuseppe, Petit, François, Schoser, Benedikt, Oldfors, Anders, Vissing, John, Romero, Norma B., Nishino, Ichizo, Malfatti, Edoardo
Հրապարակվել է 2019Տեքստ -
5
Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates Costa-Verdera, Helena, Collaud, Fanny, Riling, Christopher R., Sellier, Pauline, Nordin, Jayme M. L., Preston, G. Michael, Cagin, Umut, Fabregue, Julien, Barral, Simon, Moya-Nilges, Maryse, Krijnse-Locker, Jacomina, van Wittenberghe, Laetitia, Daniele, Natalie, Gjata, Bernard, Cosette, Jeremie, Abad, Catalina, Simon-Sola, Marcelo, Charles, Severine, Li, Mathew, Crosariol, Marco, Antrilli, Tom, Quinn, William J., Gross, David A., Boyer, Olivier, Anguela, Xavier M., Armour, Sean M., Colella, Pasqualina, Ronzitti, Giuseppe, Mingozzi, Federico
Հրապարակվել է 2021Տեքստ