檢索結果 - Bartholomae, Cynthia

Linear Amplification Mediated PCR – Localization of Genetic Elements and Characterization of Unknown Flanking DNA 由 Gabriel, Richard, Kutschera, Ina, Bartholomae, Cynthia C, von Kalle, Christof, Schmidt, Manfred

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Analyzing the Number of Common Integration Sites of Viral Vectors – New Methods and Computer Programs 由 Abel, Ulrich, Deichmann, Annette, Nowrouzi, Ali, Gabriel, Richard, Bartholomae, Cynthia C., Glimm, Hanno, von Kalle, Christof, Schmidt, Manfred

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Integration-deficient Lentiviral Vectors Expressing Codon-optimized R338L Human FIX Restore Normal Hemostasis in Hemophilia B Mice 由 Suwanmanee, Thipparat, Hu, Genlin, Gui, Tong, Bartholomae, Cynthia C, Kutschera, Ina, von Kalle, Christof, Schmidt, Manfred, Monahan, Paul E, Kafri, Tal

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Transgenic Expression of Human Glial Cell Line-Derived Neurotrophic Factor from Integration-Deficient Lentiviral Vectors is Neuroprotective in a Rodent Model of Parkinson's Disease 由 Lu-Nguyen, Ngoc B., Broadstock, Martin, Schliesser, Maximilian G., Bartholomae, Cynthia C., von Kalle, Christof, Schmidt, Manfred, Yáñez-Muñoz, Rafael J.

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Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell 由 Biasco, Luca, Ambrosi, Alessandro, Pellin, Danilo, Bartholomae, Cynthia, Brigida, Immacolata, Roncarolo, Maria Grazia, Di Serio, Clelia, von Kalle, Christof, Schmidt, Manfred, Aiuti, Alessandro

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Bioinformatic Clonality Analysis of Next-Generation Sequencing-Derived Viral Vector Integration Sites 由 Arens, Anne, Appelt, Jens-Uwe, Bartholomae, Cynthia C., Gabriel, Richard, Paruzynski, Anna, Gustafson, Derek, Cartier, Nathalie, Aubourg, Patrick, Deichmann, Annette, Glimm, Hanno, von Kalle, Christof, Schmidt, Manfred

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Real-Time Definition of Non-Randomness in the Distribution of Genomic Events 由 Abel, Ulrich, Deichmann, Annette, Bartholomae, Cynthia, Schwarzwaelder, Kerstin, Glimm, Hanno, Howe, Steven, Thrasher, Adrian, Garrigue, Alexandrine, Hacein-Bey-Abina, Salima, Cavazzana-Calvo, Marina, Fischer, Alain, Jaeger, Dirk, von Kalle, Christof, Schmidt, Manfred

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The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy 由 Montini, Eugenio, Cesana, Daniela, Schmidt, Manfred, Sanvito, Francesca, Bartholomae, Cynthia C., Ranzani, Marco, Benedicenti, Fabrizio, Sergi, Lucia Sergi, Ambrosi, Alessandro, Ponzoni, Maurilio, Doglioni, Claudio, Di Serio, Clelia, von Kalle, Christof, Naldini, Luigi

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High-Definition Mapping of Retroviral Integration Sites Defines the Fate of Allogeneic T Cells After Donor Lymphocyte Infusion 由 Cattoglio, Claudia, Maruggi, Giulietta, Bartholomae, Cynthia, Malani, Nirav, Pellin, Danilo, Cocchiarella, Fabienne, Magnani, Zulma, Ciceri, Fabio, Ambrosi, Alessandro, von Kalle, Christof, Bushman, Frederic D., Bonini, Chiara, Schmidt, Manfred, Mavilio, Fulvio, Recchia, Alessandra

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Lentiviral vector-based insertional mutagenesis identifies genes associated with liver cancer 由 Ranzani, Marco, Cesana, Daniela, Bartholomae, Cynthia C., Sanvito, Francesca, Pala, Mauro, Benedicenti, Fabrizio, Gallina, Pierangela, Sergi, Lucia Sergi, Merella, Stefania, Bulfone, Alessandro, Doglioni, Claudio, von Kalle, Christof, Kim, Yoon Jun, Schmidt, Manfred, Tonon, Giovanni, Naldini, Luigi, Montini, Eugenio

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Retroviral Gene Therapy for X-linked Chronic Granulomatous Disease: Results From Phase I/II Trial 由 Kang, Hyoung Jin, Bartholomae, Cynthia C, Paruzynski, Anna, Arens, Anne, Kim, Sujeong, Yu, Seung Shin, Hong, Youngtae, Joo, Chang-Wan, Yoon, Nam-Kyung, Rhim, Jung-Woo, Kim, Joong Gon, Von Kalle, Christof, Schmidt, Manfred, Kim, Sunyoung, Ahn, Hyo Seop

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Uncovering and Dissecting the Genotoxicity of Self-inactivating Lentiviral Vectors In Vivo 由 Cesana, Daniela, Ranzani, Marco, Volpin, Monica, Bartholomae, Cynthia, Duros, Caroline, Artus, Alexandre, Merella, Stefania, Benedicenti, Fabrizio, Sergi Sergi, Lucia, Sanvito, Francesca, Brombin, Chiara, Nonis, Alessandro, Serio, Clelia Di, Doglioni, Claudio, von Kalle, Christof, Schmidt, Manfred, Cohen-Haguenauer, Odile, Naldini, Luigi, Montini, Eugenio

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Lentiviral Vector Integration Profiles Differ in Rodent Postmitotic Tissues 由 Bartholomae, Cynthia C, Arens, Anne, Balaggan, Kamaljit S, Yáñez-Muñoz, Rafael J, Montini, Eugenio, Howe, Steven J, Paruzynski, Anna, Korn, Bernhard, Appelt, Jens Uwe, MacNeil, Angus, Cesana, Daniela, Abel, Ulrich, Glimm, Hanno, Naldini, Luigi, Ali, Robin R, Thrasher, Adrian J, von Kalle, Christof, Schmidt, Manfred

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Hepatocyte-Targeted Expression by Integrase-Defective Lentiviral Vectors Induces Antigen-Specific Tolerance in Mice with Low Genotoxic Risk 由 Mátrai, Janka, Cantore, Alessio, Bartholomae, Cynthia C, Annoni, Andrea, Wang, Wei, Acosta-Sanchez, Abel, Samara-Kuko, Ermira, De Waele, Liesbeth, Ma, Ling, Genovese, Pietro, Damo, Martina, Arens, Anne, Goudy, Kevin, Nichols, Timothy C, von Kalle, Christof, Chuah, Marinee K L, Roncarolo, Maria Grazia, Schmidt, Manfred, VandenDriessche, Thierry, Naldini, Luigi

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Liver-Directed Lentiviral Gene Therapy in a Dog Model of Hemophilia B 由 Cantore, Alessio, Ranzani, Marco, Bartholomae, Cynthia C., Volpin, Monica, Della Valle, Patrizia, Sanvito, Francesca, Sergi Sergi, Lucia, Gallina, Pierangela, Benedicenti, Fabrizio, Bellinger, Dwight, Raymer, Robin, Merricks, Elizabeth, Bellintani, Francesca, Martin, Samia, Doglioni, Claudio, D’Angelo, Armando, VandenDriessche, Thierry, Chuah, Marinee K., Schmidt, Manfred, Nichols, Timothy, Montini, Eugenio, Naldini, Luigi

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Preclinical Safety and Efficacy of Human CD34(+) Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome 由 Scaramuzza, Samantha, Biasco, Luca, Ripamonti, Anna, Castiello, Maria C, Loperfido, Mariana, Draghici, Elena, Hernandez, Raisa J, Benedicenti, Fabrizio, Radrizzani, Marina, Salomoni, Monica, Ranzani, Marco, Bartholomae, Cynthia C, Vicenzi, Elisa, Finocchi, Andrea, Bredius, Robbert, Bosticardo, Marita, Schmidt, Manfred, von Kalle, Christof, Montini, Eugenio, Biffi, Alessandra, Roncarolo, Maria G, Naldini, Luigi, Villa, Anna, Aiuti, Alessandro

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Preclinical Evaluation of Efficacy and Safety of an Improved Lentiviral Vector for the Treatment of β-Thalassemia and Sickle Cell Disease 由 Negre, Olivier, Bartholomae, Cynthia, Beuzard, Yves, Cavazzana, Marina, Christiansen, Lauryn, Courne, Céline, Deichmann, Annette, Denaro, Maria, de Dreuzy, Edouard, Finer, Mitchell, Fronza, Raffaele, Gillet-Legrand, Béatrix, Joubert, Christophe, Kutner, Robert, Leboulch, Philippe, Maouche, Leïla, Paulard, Anaïs, Pierciey, Francis J., Rothe, Michael, Ryu, Byoung, Schmidt, Manfred, von Kalle, Christof, Payen, Emmanuel, Veres, Gabor

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Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group Meeting 由 Tolar, Jakub, Adair, Jennifer E, Antoniou, Michael, Bartholomae, Cynthia C, Becker, Pamela S, Blazar, Bruce R, Bueren, Juan, Carroll, Thomas, Cavazzana-Calvo, Marina, Clapp, D Wade, Dalgleish, Robert, Galy, Anne, Gaspar, H Bobby, Hanenberg, Helmut, Von Kalle, Christof, Kiem, Hans-Peter, Lindeman, Dirk, Naldini, Luigi, Navarro, Susana, Renella, Raffaele, Rio, Paula, Sevilla, Julián, Schmidt, Manfred, Verhoeyen, Els, Wagner, John E, Williams, David A, Thrasher, Adrian J

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Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients 由 Howe, Steven J., Mansour, Marc R., Schwarzwaelder, Kerstin, Bartholomae, Cynthia, Hubank, Michael, Kempski, Helena, Brugman, Martijn H., Pike-Overzet, Karin, Chatters, Stephen J., de Ridder, Dick, Gilmour, Kimberly C., Adams, Stuart, Thornhill, Susannah I., Parsley, Kathryn L., Staal, Frank J.T., Gale, Rosemary E., Linch, David C., Bayford, Jinhua, Brown, Lucie, Quaye, Michelle, Kinnon, Christine, Ancliff, Philip, Webb, David K., Schmidt, Manfred, von Kalle, Christof, Gaspar, H. Bobby, Thrasher, Adrian J.

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Insertion Sites in Engrafted Cells Cluster Within a Limited Repertoire of Genomic Areas After Gammaretroviral Vector Gene Therapy 由 Deichmann, Annette, Brugman, Martijn H, Bartholomae, Cynthia C, Schwarzwaelder, Kerstin, Verstegen, Monique MA, Howe, Steven J, Arens, Anne, Ott, Marion G, Hoelzer, Dieter, Seger, Reinhard, Grez, Manuel, Hacein-Bey-Abina, Salima, Cavazzana-Calvo, Marina, Fischer, Alain, Paruzynski, Anna, Gabriel, Richard, Glimm, Hanno, Abel, Ulrich, Cattoglio, Claudia, Mavilio, Fulvio, Cassani, Barbara, Aiuti, Alessandro, Dunbar, Cynthia E, Baum, Christopher, Gaspar, H Bobby, Thrasher, Adrian J, von Kalle, Christof, Schmidt, Manfred, Wagemaker, Gerard

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