檢索結果 - Angela Genge
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Reliability and validity of speech & pause measures during passage reading in ALS 由 Carolina Barnett, Jordan R. Green, Reeman Marzouqah, Kaila L. Stipancic, James Berry, Lawrence Korngut, Angela Genge, Christen Shoesmith, Hannah Briemberg, Agessandro Abrahão, Sanjay Kalra, Lorne Zinman, Yana Yunusova
出版 2019Artigo -
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Pompe Disease: Diagnosis and Management. Evidence-Based Guidelines from a Canadian Expert Panel 由 Mark A. Tarnopolsky, Hans Katzberg, Basil J. Petrof, Sandra Sirrs, Harvey B. Sarnat, Kimberley Myers, Nicolas Dupré, Dubravka Dodig, Angela Genge, Shannon L. Venance, Lawrence Korngut, Julian Raiman, Anzalee Khan
出版 2016Revisão -
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Addressing heterogeneity in amyotrophic lateral sclerosis CLINICAL TRIALS 由 Namita Goyal, James Berry, Anthony J. Windebank, Nathan P. Staff, Nicholas J. Maragakis, Leonard H. van den Berg, Angela Genge, Robert G. Miller, Robert H. Baloh, R. Kern, Yaël Gothelf, Chaim Lebovits, Merit Cudkowicz
出版 2020Revisão -
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Understanding the use of NIV in ALS: results of an international ALS specialist survey 由 Terry Heiman‐Patterson, Merit Cudkowicz, Mamede de Carvalho, Angela Genge, Orla Hardiman, Carlayne E. Jackson, Noah Lechtzin, Hiroshi Mitsumoto, Vincenzo Silani, Jinsy Andrews, Dafeng Chen, Sarah Kulke, Stacy A. Rudnicki, Leonard H. van den Berg
出版 2018Artigo -
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Efficacy and Safety of Once Daily Dosing vs. Approved On/Off Dosing of Edaravone Oral Suspension Up to 48 Weeks in Patients With Amyotrophic Lateral Sclerosis (Study <scp>MT</scp>‐... 由 Jeffrey D. Rothstein, Angela Genge, Amélia M. Silva, Lorne Zinman, Marvin Chum, Adriano Chiò, Gen Sobue, Masashi Aoki, Hiide Yoshino, Manabu Doyu, Daniel Selness, Vesna Todorović, Noah J. Sasson, Manabu Hirai, Fumihiro Takahashi, Alejandro Salah, Art Wamil, Stephen Apple
出版 2025Artigo -
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Safety Extension Study of Edaravone Oral Suspension in Patients With Amyotrophic Lateral Sclerosis for up to an Additional 96 Weeks of Treatment 由 Angela Genge, Gary L. Pattee, Gen Sobue, Masashi Aoki, Hiide Yoshino, Philippe Couratier, Christian Lunetta, Susanne Petri, Daniel Selness, Vesna Todorović, Noah J. Sasson, Manabu Hirai, Fumihiro Takahashi, Alejandro Salah, Stephen Apple, Art Wamil, Alexander Kalin, Carlayne E. Jackson
出版 2025Artigo -
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Defining cognitive impairment in amyotrophic lateral sclerosis: an evaluation of empirical approaches 由 Corey T. McMillan, Joanne Wuu, Katya Rascovsky, Stephanie Cosentino, Murray Grossman, Lauren Elman, Colin Quinn, Luis Rosario, Jessica Stark, Volkan Granit, Hannah Briemberg, Sneha Chenji, Annie Dionne, Angela Genge, Wendy Johnston, Lawrence Korngut, Christen Shoesmith, Lorne Zinman, Sanjay Kalra, Michael Benatar
出版 2022Artigo -
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Masitinib as an add-on therapy to riluzole in patients with amyotrophic lateral sclerosis: a randomized clinical trial 由 Jesús S. Mora, Angela Genge, Adriano Chió, Conrado J. Estol, Delia Chaverri, Mariluz Hernández, Saúl Marín, Javier Mascías, Gabriel Rodríguez, Mònica Povedano, Andrés Paipa, Raúl Domínguez, Josep Gámez, María Salvadó, Christian Lunetta, Carlos Ballario, Nilo Riva, Jessica Mandrioli, Alain Moussy, Jean‐Pierre Kinet, Christian Auclair, Patrice Dubreuil, Vincent Arnold, Colin D. Mansfield, Olivier Hermine
出版 2019Artigo -
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Revised Airlie House consensus guidelines for design and implementation of ALS clinical trials 由 Leonard H. van den Berg, Eric J. Sorenson, Gary Gronseth, Eric A. Macklin, Jinsy Andrews, Robert H. Baloh, Michael Benatar, James Berry, Adriano Chió, Philippe Corcia, Angela Genge, Amelie K. Gubitz, Catherine Lomen‐Hoerth, Christopher McDermott, Erik P. Pioro, Jeffrey Rosenfeld, Vincenzo Silani, Martin R. Turner, Markus Weber, Benjamin Rix Brooks, Robert G. Miller, Hiroshi Mitsumoto
出版 2019Artigo -
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Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study 由 Stacy A. Rudnicki, Jinsy Andrews, Tina Duong, Bettina M. Cockroft, Fady I. Malik, Lisa Meng, Jenny Wei, Andrew A. Wolff, Angela Genge, Nicholas E. Johnson, Carolina Tesi Rocha, Anne M. Connolly, Basil T. Darras, Kevin J. Felice, Richard S. Finkel, Perry B. Shieh, Jean K. Mah, Jeffrey Statland, Craig Campbell, Ali A. Habib, Nancy L. Kuntz, Maryam Oskoui, John Day
出版 2021Artigo -
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A Phase 1 study of <scp>GDC</scp>‐0134, a dual leucine zipper kinase inhibitor, in <scp>ALS</scp> 由 Jonathan Katz, Jeffrey D. Rothstein, Merit Cudkowicz, Angela Genge, Björn Oskarsson, Avis B. Hains, Chen Chen, Joshua Galanter, Braydon L. Burgess, Yong‐Yeon Cho, Geoffrey A. Kerchner, Felix L. Yeh, Arundhati Sengupta Ghosh, Sravanthi Cheeti, Logan Brooks, Lee Honigberg, Jessica A. Couch, Michael E. Rothenberg, Flávia Brunstein, Khema R. Sharma, Leonard van den Berg, James Berry, Jonathan D. Glass
出版 2022Artigo -
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The ALSFRS-R Summit: a global call to action on the use of the ALSFRS-R in ALS clinical trials 由 Angela Genge, Jesse M. Cedarbaum, Jeremy M. Shefner, Adriano Chiò, Ammar Al‐Chalabi, Philip Van Damme, Christopher McDermott, Jonathan D. Glass, James Berry, Ruben P.A. van Eijk, Christina N. Fournier, Julian Großkreutz, Jinsy Andrews, Vanessa Bertone, Tommy M. Bunte, Mathias Couillard, Cathy Cummings, Gale Kittle, John Polzer, Kristiana Salmon, Corey Straub, Leonard H. van den Berg
出版 2024Artigo -
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Trial of Antisense Oligonucleotide Tofersen for <i>SOD1</i> ALS 由 Jonathan Mill, Merit Cudkowicz, Angela Genge, Pamela J. Shaw, Gen Sobue, Robert C. Bucelli, Adriano Chió, Philip Van Damme, Albert C. Ludolph, Jonathan D. Glass, Jinsy Andrews, Suma Babu, Michael Benatar, Christopher McDermott, Thos Cochrane, Sowmya Chary, Sheena Chew, Han Zhu, Fan Wu, Ivan Nestorov, Danielle Graham, Peng Sun, Manjit McNeill, Laura Fanning, Toby A. Ferguson, Stephanie Fradette
出版 2022Artigo
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